Simultaneous Reprogramming and Gene Correction of Patient Fibroblasts

Stem Cell Reports

Volumn 5, Issue 6, 2015, Pages 1109-1118

  Howden, Sara E ^a   Maufort, John P ^a   Duffin, Bret M ^a   Elefanty, Andrew G ^d,e   Stanley, Edouard G ^d,e   Thomson, James A ^a,b,c  

^a MORGRIDGE INSTITUTE FOR RESEARCH   (United States)

^b UNIVERSITY OF WISCONSIN SCHOOL OF MEDICINE AND PUBLIC HEALTH   (United States)

^c UNIVERSITY OF CALIFORNIA   (United States)

^d MONASH UNIVERSITY   (Australia)

^e UNIVERSITY OF MELBOURNE   (Australia)

Author keywords

[No Author keywords available]

Indexed keywords

DNA METHYLTRANSFERASE 3B; MESSENGER RNA; OCTAMER TRANSCRIPTION FACTOR 4; PLASMID DNA; DNA (CYTOSINE 5) METHYLTRANSFERASE; POU5F1 PROTEIN, HUMAN;

ADULT; ARTICLE; CELL CLONE; CONTROLLED STUDY; CRISPR CAS SYSTEM; DNA END JOINING REPAIR; EMBRYONIC STEM CELL; FIBROBLAST; GENE TARGETING; GENETIC ENGINEERING; HIGH PERFORMANCE LIQUID CHROMATOGRAPHY; HOMOLOGOUS RECOMBINATION; HUMAN; HUMAN CELL; INFANT; NUCLEAR REPROGRAMMING; PLURIPOTENT STEM CELL; PRIORITY JOURNAL; RETINITIS PIGMENTOSA; SEVERE COMBINED IMMUNODEFICIENCY; SOMATIC MUTATION; CELL CULTURE; CELL LINE; CYTOLOGY; ELECTROPORATION; GENE VECTOR; GENETICS; INDUCED PLURIPOTENT STEM CELL; METABOLISM; MOLECULAR GENETICS; NUCLEOTIDE SEQUENCE; PROCEDURES;

ADULT; BASE SEQUENCE; CELL LINE; CELLS, CULTURED; CELLULAR REPROGRAMMING; CRISPR-CAS SYSTEMS; DNA (CYTOSINE-5-)-METHYLTRANSFERASE; ELECTROPORATION; FIBROBLASTS; GENE TARGETING; GENETIC VECTORS; HUMANS; INDUCED PLURIPOTENT STEM CELLS; MOLECULAR SEQUENCE DATA; OCTAMER TRANSCRIPTION FACTOR-3;

EID: 84949534786     PISSN: 22136711     EISSN: None     Source Type: Journal    
DOI: 10.1016/j.stemcr.2015.10.009     Document Type: Article

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