Pressurized transvenous-retrograde extremity perfusion

Gene and Cell Therapy: Therapeutic Mechanisms and Strategies, Fourth Edition

Volumn , Issue , 2015, Pages 439-449

  Fan, Zheng ^a   Power, William ^a   Kornegay, Joe ^b   Xiao, Xiao ^c  

^a UNIVERSITY OF NORTH CAROLINA SCHOOL OF MEDICINE   (United States)

^b TEXAS A AND M UNIVERSITY   (United States)

^c UNC Hamner Institute for Drug Safety Sciences   (United States)

Author keywords

[No Author keywords available]

Indexed keywords

EID: 84941286563     PISSN: None     EISSN: None     Source Type: Book    
DOI: 10.1201/b18002     Document Type: Chapter

References (33)

1. KayMA, MannoCS, RagniMVet al.Evidence for gene transfer and expression of factor IX in haemophilia B patients treated with an AAV vector. Nat Genet2000;24:257-261.
2. MendellJr., Rodino-KlapacLR, Rosales-QuinteroXet al.Limb-girdle muscular dystrophy type 2D gene therapy restores alpha-sarcoglycan and associated proteins. Ann Neurol2009;66:290-297.
3. Stedman H, Wilson JM, Finke R, Kleckner AL, Mendell J. Phase I clinical trial utilizing gene therapy for limb girdle muscular dystrophy: Alpha-, beta-, gamma-, or delta-sarcoglycan gene delivered with intramuscular instillations of adeno-associated vectors. Hum Gene Ther2000;11:777-790.
4. HaldaneJS.On being the right size. Possible Worlds and Other Essays. D’Arcy W. Thompson (ed.)1927; Chatto & Windus: London, U.K.
5. ArrudaVR, StedmanHH, NicholsTCet al.Regional intravascular delivery of AAV-2-F.IX to skeletal muscle achieves long-term correction of hemophilia B in a large animal model. Blood2005;105:3458-3464.
6. SuLT, GopalK, WangZet al.Uniform scale-independent gene transfer to striated muscle after transvenular extravasation of vector. Circulation2005;112:1780-1788.
7. HeggeJO, WooddellCI, ZhangGet al.Evaluation of hydrodynamic limb vein injections in nonhuman primates. Hum Gene Ther2010;21:829-842.
8. FanZ, KocisK, ValleyRet al.Safety and feasibility of high-pressure transvenous limb perfusion with 0.9% saline in human muscular dystrophy. Mol Ther: J Am Soc Gene Ther2012;20:456-461.
9. HagstromJE, HeggeJ, ZhangGet al.A facile nonviral method for delivering genes and siRNAs to skeletal muscle of mammalian limbs. Mol Ther: J Am Soc Gene Ther2004;10:386-398.
10. DavisHL, DemeneixBA, QuantinB, CoulombeJ, WhalenRG.Plasmid DNA is superior to viral vectors for direct gene transfer into adult mouse skeletal muscle. Hum Gene Ther1993;4:733-740.
11. KesslerPD, PodsakoffGM, ChenXet al.Gene delivery to skeletal muscle results in sustained expression and systemic delivery of a therapeutic protein. Proc Natl Acad Sci USA1996;93:14082-14087.
12. RagotT, VincentN, ChafeyPet al.Efficient adenovirusmediated transfer of a human minidystrophin gene to skeletal muscle of mdx mice. Nature1993;361:647-650.
13. KamimuraK, ZhangG, LiuD.Image-guided, intravascular hydrodynamic gene delivery to skeletal muscle in pigs. Mol Ther: J Am Soc Gene Ther2010;18:93-100.
14. PichavantC, ChapdelaineP, CerriDGet al.Expression of dog microdystrophin in mouse and dog muscles by gene therapy. Mol Ther: J Am Soc Gene Ther2010;18:1002-1009.
15. WangB, LiJ, QiaoCet al.A canine minidystrophin is functional and therapeutic in mdx mice. Gene Ther2008;15:1099-1106.
16. HerweijerH, Wolff JA. Gene therapyprogress and prospects: Hydrodynamic gene delivery. Gene Ther2007;14:99-107.
17. PetrovM, MalikA, MeadA, BridgesCR, StedmanHH.Gene transfer to muscle from the isolated regional circulation. Methods Mol Biol2011;709:277-286.
18. QiaoC, LiJ, ZhengHet al.Hydrodynamic limb vein injection of adeno-associated virus serotype 8 vector carrying canine myostatin propeptide gene into normal dogs enhances muscle growth. Hum Gene Ther2009;20:1-10.
19. ToromanoffA, CherelY, GuilbaudMet al.Safety and efficacy of regional intravenous (r.i.) versus intramuscular (i.m.) delivery of rAAV1 and rAAV8 to nonhuman primate skeletal muscle. Mol Ther: J Am Soc Gene Ther2008;16:1291-1299.
20. van den BrandJG, NelsonT, VerleisdonkEJ, van der WerkenC.The diagnostic value of intracompartmental pressure measurement, magnetic resonance imaging, and near-infrared spectroscopy in chronic exertional compartment syndrome: A prospective study in 50 patients. Am J Sports Med2005;33:699-704.
21. Marsch SC, Sluga M, Studer W, Barandun J, Scharplatz D, Ummenhofer W. 0.5% versus 1.0% 2-chloroprocaine for intravenous regional anesthesia: A prospective, randomized, double-blind trial. AnesthAnalg 2004;98:1789-1793, table of contents.
22. Comunale ME. A laboratory evaluation of the level 1 rapid infuser (H1025) and the Belmont instrument fluid management system (FMS 2000) for rapid transfusion. Anesth Analg 2003;97:1064-1069, table of contents.
23. LabropoulosN, TiongsonJ, PryorLet al.Definition of venous reflux in lower-extremity veins. J Vasc Surg2003;38:793-798.
24. ATS Committee on Proficiency Standards for Clinical Pulmonary Function Laboratories. ATS statement: Guidelines for the six-minute walk test. Am Jr.espir Crit Care Med2002;166:111-117.
25. YushkevichPA, PivenJ, HazlettHCet al.User-guided 3D active contour segmentation of anatomical structures: Significantly improved efficiency and reliability. Neuroimage2006;31:1116-1128.
26. FlorenceJM, FoxPT, PlanerGJ, Brooke MH.Activity, creatinekinase, and myoglobin in Duchenne muscular dystrophy: A clue to etiology?Neurology1985;35:758-761.
27. JacksonMJ, RoundJM, NewhamDJ, EdwardsRH.An examination of some factors influencing creatine kinase in the blood of patients with muscular dystrophy. Muscle Nerve1987;10:15-21.
28. BrombergMB, SpiegelbergT.The influence of active electrode placement on CMAP amplitude. Electroencephalogr Clin Neurophysiol1997;105:385-389.
29. KongX, LesserEA, GozaniSN.Repeatability of nerve conduction measurements derived entirely by computer methods. Biomed Eng Online2009;8:33.
30. BarryLA, BallianaSA, and GaleppiAC, Intravenous regional anesthesia (Bier block)., Techn Reg Anesth Pain Manag2006;10:123-131.
31. Rodino-KlapacLR, MontgomeryCL, MendellJr., ChicoineLG.AAV-mediated gene therapy to the isolated limb in rhesus macaques. Methods Mol Biol2011;709:287-298.
32. VigenKK, HeggeJO, ZhangGet al.Magnetic resonance imaging-monitored plasmid DNA delivery in primate limb muscle. Hum Gene Ther2007;18:257-268.
33. PlanteGE, ChakirM, EttaouilK, LehouxS, SiroisP.Consequences of alteration in capillary permeability. Can J Physiol Pharmacol1996;74:824-833.