A canine minidystrophin is functional and therapeutic in mdx mice

Gene Therapy

Volumn 15, Issue 15, 2008, Pages 1099-1106

  Wang, B ^a   Li, J ^b   Qiao, C ^b   Chen, C ^b   Hu, P ^b   Zhu, X ^c   Zhou, L ^a   Bogan, J ^d   Kornegay, J ^d   Xiao, X ^b  

^a UNIVERSITY OF PITTSBURGH SCHOOL OF MEDICINE   (United States)

^b UNIVERSITY OF NORTH CAROLINA   (United States)

^c UNIVERSITY OF PITTSBURGH   (United States)

^d UNIVERSITY OF NORTH CAROLINA SCHOOL OF MEDICINE   (United States)

Author keywords

[No Author keywords available]

Indexed keywords

ALPHA SYNUCLEIN; DYSTROBREVIN; DYSTROPHIN; MINIDYSTROPHIN; NEURONAL NITRIC OXIDE SYNTHASE; PARVOVIRUS VECTOR; SARCOGLYCAN;

ANIMAL EXPERIMENT; ANIMAL MODEL; ANIMAL TISSUE; ARTICLE; CELL MEMBRANE; CELLULAR IMMUNITY; COMPLEX FORMATION; CONTROLLED STUDY; GENE EXPRESSION; GENE THERAPY; IN VIVO STUDY; MOLECULAR CLONING; MOUSE; MUSCLE FIBER MEMBRANE; MUSCULAR DYSTROPHY; MYOFIBROSIS; NONHUMAN; NUCLEOTIDE SEQUENCE; PRIORITY JOURNAL; SARCOLEMMA; VIRAL GENE DELIVERY SYSTEM;

ANIMALS; BASE SEQUENCE; DEPENDOVIRUS; DOGS; DYSTROPHIN; DYSTROPHIN-ASSOCIATED PROTEIN COMPLEX; FLUORESCENT ANTIBODY TECHNIQUE; GENE EXPRESSION; GENE THERAPY; GENETIC VECTORS; MICE; MICE, INBRED MDX; MOLECULAR SEQUENCE DATA; MUSCLE FIBERS; MUSCLE, SKELETAL; MUSCULAR DYSTROPHY, ANIMAL; SARCOLEMMA; STAINING AND LABELING; TRANSGENES;

ADENO-ASSOCIATED VIRUS; CANIS FAMILIARIS; MUS;

EID: 47549101040     PISSN: 09697128     EISSN: 14765462     Source Type: Journal    
DOI: 10.1038/gt.2008.70     Document Type: Article

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