-
1
-
-
0024332294
-
Randomized, double-blind six-month trial of prednisone in Duchenne's muscular dystrophy
-
Mendell, JR, Moxley, RT, Griggs, RC, Brooke, MH, Fenichel, GM, Miller, JP et al. (1989). Randomized, double-blind six-month trial of prednisone in Duchenne's muscular dystrophy. N Engl J Med 320: 1592-1597. (Pubitemid 19154573)
-
(1989)
New England Journal of Medicine
, vol.320
, Issue.24
, pp. 1592-1597
-
-
Mendell, J.R.1
Moxley, R.T.2
Griggs, R.C.3
Brooke, M.H.4
Fenichel, G.M.5
Miller, J.P.6
King, W.7
Signore, L.8
Pandya, S.9
Florence, J.10
Schierbecker, J.11
Robison, J.12
Kaiser, K.13
Mandel, S.14
Arfken, C.15
Gilder, B.16
-
2
-
-
0034050904
-
Evidence for gene transfer and expression of factor IX in haemophilia B patients treated with an AAV vector
-
DOI 10.1038/73464
-
Kay, MA, Manno, CS, Ragni, MV, Larson, PJ, Couto, LB, McClelland, A et al. (2000). Evidence for gene transfer and expression of factor IX in haemophilia B patients treated with an AAV vector. Nat Genet 24: 257-261. (Pubitemid 30132193)
-
(2000)
Nature Genetics
, vol.24
, Issue.3
, pp. 257-261
-
-
Kay, M.A.1
Manno, C.S.2
Ragni, M.V.3
Larson, P.J.4
Couto, L.B.5
McClelland, A.6
Glader, B.7
Chew, A.J.8
Tai, S.J.9
Herzog, R.W.10
Arruda, V.11
Johnson, F.12
Scallan, C.13
Skarsgard, E.14
Flake, A.W.15
High, K.A.16
-
3
-
-
70350067897
-
Limb-girdle muscular dystrophy type 2D gene therapy restores alphasarcoglycan and associated proteins
-
Mendell, JR, Rodino-Klapac, LR, Rosales-Quintero, X, Kota, J, Coley, BD, Galloway, G et al. (2009). Limb-girdle muscular dystrophy type 2D gene therapy restores alphasarcoglycan and associated proteins. Ann Neurol 66: 290-297.
-
(2009)
Ann Neurol
, vol.66
, pp. 290-297
-
-
Mendell, J.R.1
Rodino-Klapac, L.R.2
Rosales-Quintero, X.3
Kota, J.4
Coley, B.D.5
Galloway, G.6
-
4
-
-
0034689207
-
Phase I clinical trial utilizing gene therapy for limb girdle muscular dystrophy: α-, β-, γ-, or Δ-Sarcoglycan gene delivered with intramuscular instillations of adeno-associated vectors
-
DOI 10.1089/10430340050015671
-
Stedman, H, Wilson, JM, Finke, R, Kleckner, AL and Mendell, J (2000). Phase I clinical trial utilizing gene therapy for limb girdle muscular dystrophy: alpha-, beta-, gamma-, or delta-sarcoglycan gene delivered with intramuscular instillations of adenoassociated vectors. Hum Gene Ther 11: 777-790. (Pubitemid 30180282)
-
(2000)
Human Gene Therapy
, vol.11
, Issue.5
, pp. 777-790
-
-
Stedman, H.1
Wilson, J.M.2
Finke, R.3
Kleckner, A.-L.4
Mendell, J.5
-
5
-
-
4344715026
-
A facile nonviral method for delivering genes and siRNAs to skeletal muscle of mammalian limbs
-
DOI 10.1016/j.ymthe.2004.05.004, PII S1525001604001704
-
Hagstrom, JE, Hegge, J, Zhang, G, Noble, M, Budker, V, Lewis, DL et al. (2004). A facile nonviral method for delivering genes and siRNAs to skeletal muscle of mammalian limbs. Mol Ther 10: 386-398. (Pubitemid 39117883)
-
(2004)
Molecular Therapy
, vol.10
, Issue.2
, pp. 386-398
-
-
Hagstrom, J.E.1
Hegge, J.2
Zhang, G.3
Noble, M.4
Budker, V.5
Lewis, D.L.6
Herweijer, H.7
Wolff, J.A.8
-
6
-
-
0027713222
-
Plasmid DNA is superior to viral vectors for direct gene transfer into adult mouse skeletal muscle
-
Davis, HL, Demeneix, BA, Quantin, B, Coulombe, J and Whalen, RG (1993). Plasmid DNA is superior to viral vectors for direct gene transfer into adult mouse skeletal muscle. Hum Gene Ther 4: 733-740. (Pubitemid 24305767)
-
(1993)
Human Gene Therapy
, vol.4
, Issue.6
, pp. 733-740
-
-
Davis, H.L.1
Demeneix, B.A.2
Quantin, B.3
Coulombe, J.4
Whalen, R.G.5
-
7
-
-
0030451214
-
Gene delivery to skeletal muscle results in sustained expression and systemic delivery of a therapeutic protein
-
DOI 10.1073/pnas.93.24.14082
-
Kessler, PD, Podsakoff, GM, Chen, X, McQuiston, SA, Colosi, PC, Matelis, LA et al. (1996). Gene delivery to skeletal muscle results in sustained expression and systemic delivery of a therapeutic protein. Proc Natl Acad Sci USA 93: 14082-14087. (Pubitemid 26424249)
-
(1996)
Proceedings of the National Academy of Sciences of the United States of America
, vol.93
, Issue.24
, pp. 14082-14087
-
-
Kessler, P.D.1
Podsakoff, G.M.2
Chen, X.3
McQuiston, S.A.4
Colosi, P.C.5
Matelis, L.A.6
Kurtzman, G.J.7
Byrne, B.J.8
-
8
-
-
0027408847
-
Efficient adenovirus-mediated transfer of a human minidystrophin gene to skeletal muscle of mdx mice
-
DOI 10.1038/361647a0
-
Ragot, T, Vincent, N, Chafey, P, Vigne, E, Gilgenkrantz, H, Couton, D et al. (1993). Efficient adenovirus-mediated transfer of a human minidystrophin gene to skeletal muscle of mdx mice. Nature 361: 647-650. (Pubitemid 23062399)
-
(1993)
Nature
, vol.361
, Issue.6413
, pp. 647-650
-
-
Ragot, T.1
Vincent, N.2
Chafey, P.3
Vigne, E.4
Gilgenkrantz, H.5
Couton, D.6
Cartaud, J.7
Briand, P.8
Kaplan, J.-C.9
Perricaudet, M.10
Kahn, A.11
-
9
-
-
74149089250
-
Image-guided, intravascular hydrodynamic gene delivery to skeletal muscle in pigs
-
Kamimura, K, Zhang, G and Liu, D (2010). Image-guided, intravascular hydrodynamic gene delivery to skeletal muscle in pigs. Mol Ther 18: 93-100.
-
(2010)
Mol Ther
, vol.18
, pp. 93-100
-
-
Kamimura, K.1
Zhang, G.2
Liu, D.3
-
10
-
-
77952012209
-
Expression of dog microdystrophin in mouse and dog muscles by gene therapy
-
Pichavant, C, Chapdelaine, P, Cerri, DG, Dominique, JC, Quenneville, SP, Skuk, D et al. (2010). Expression of dog microdystrophin in mouse and dog muscles by gene therapy. Mol Ther 18: 1002-1009.
-
(2010)
Mol Ther
, vol.18
, pp. 1002-1009
-
-
Pichavant, C.1
Chapdelaine, P.2
Cerri, D.G.3
Dominique, J.C.4
Quenneville, S.P.5
Skuk, D.6
-
11
-
-
47549101040
-
A canine minidystrophin is functional and therapeutic in mdx mice
-
DOI 10.1038/gt.2008.70, PII GT200870
-
Wang, B, Li, J, Qiao, C, Chen, C, Hu, P, Zhu, X et al. (2008). A canine minidystrophin is functional and therapeutic in mdx mice. Gene Ther 15: 1099-1106. (Pubitemid 352006080)
-
(2008)
Gene Therapy
, vol.15
, Issue.15
, pp. 1099-1106
-
-
Wang, B.1
Li, J.2
Qiao, C.3
Chen, C.4
Hu, P.5
Zhu, X.6
Zhou, L.7
Bogan, J.8
Kornegay, J.9
Xiao, X.10
-
12
-
-
0021848735
-
Activity creatine kinase, and myoglobin in Duchenne muscular dystrophy: A clue to etiology?
-
Florence, JM, Fox, PT, Planer, GJ and Brooke, MH (1985). Activity, creatine kinase, and myoglobin in Duchenne muscular dystrophy: a clue to etiology? Neurology 35: 758-761. (Pubitemid 15067040)
-
(1985)
Neurology
, vol.35
, Issue.5
, pp. 758-761
-
-
Florence, J.M.1
Fox, P.T.2
Planer, J.3
Brooke, M.H.4
-
13
-
-
0023150536
-
An examination of some factors influencing creatine kinase in the blood of patients with muscular dystrophy
-
Jackson, MJ, Round, JM, Newham, DJ and Edwards, RH (1987). An examination of some factors influencing creatine kinase in the blood of patients with muscular dystrophy. Muscle Nerve 10: 15-21. (Pubitemid 17223305)
-
(1987)
Muscle and Nerve
, vol.10
, Issue.1
, pp. 15-21
-
-
Jackson, M.J.1
Round, J.M.2
Newham, D.J.3
Edwards, R.H.T.4
-
15
-
-
74049135356
-
Repeatability of nerve conduction measurements derived entirely by computer methods
-
Kong, X, Lesser, EA and Gozani, SN (2009). Repeatability of nerve conduction measurements derived entirely by computer methods. Biomed Eng Online 8: 33.
-
(2009)
Biomed Eng Online
, vol.8
, pp. 33
-
-
Kong, X.1
Lesser, E.A.2
Gozani, S.N.3
-
16
-
-
77957935853
-
Evaluation of hydrodynamic limb vein injections in nonhuman primates
-
Hegge, JO, Wooddell, CI, Zhang, G, Hagstrom, JE, Braun, S, Huss, T et al. (2010). Evaluation of hydrodynamic limb vein injections in nonhuman primates. Hum Gene Ther 21: 829-842.
-
(2010)
Hum Gene Ther
, vol.21
, pp. 829-842
-
-
Hegge, J.O.1
Wooddell, C.I.2
Zhang, G.3
Hagstrom, J.E.4
Braun, S.5
Huss, T.6
-
17
-
-
33749657688
-
Intravenous regional anesthesia (Bier block)
-
DOI 10.1053/j.trap.2006.07.005, PII S1084208X06000462, Peripheral Nerve Blocks: A View from Argentinia, I
-
Barry, LA, Balliana, BS, Galeppi AC. Intravenous regional anesthesia (Bier block). Techniques in Regional Anesthesia and Pain Management, Volume 10, Issue 3, 2006, pp 123-131. (Pubitemid 44557117)
-
(2006)
Techniques in Regional Anesthesia and Pain Management
, vol.10
, Issue.3
, pp. 123-131
-
-
Barry, L.A.1
Balliana, S.A.2
Galeppi, A.C.3
-
18
-
-
34247235162
-
Magnetic resonance imaging-monitored plasmid DNA delivery in primate limb muscle
-
DOI 10.1089/hum.2006.115
-
Vigen, KK, Hegge, JO, Zhang, G, Mukherjee, R, Braun, S, Grist, TM et al. (2007). Magnetic resonance imaging-monitored plasmid DNA delivery in primate limb muscle. Hum Gene Ther 18: 257-268. (Pubitemid 46626464)
-
(2007)
Human Gene Therapy
, vol.18
, Issue.3
, pp. 257-268
-
-
Vigen, K.K.1
Hegge, J.O.2
Zhang, G.3
Mukherjee, R.4
Braun, S.5
Grist, T.M.6
Wolff, J.A.7
-
19
-
-
77955177089
-
Widespread muscle expression of an AAV9 human mini-dystrophin vector after intravenous injection in neonatal dystrophin-deficient dogs
-
Kornegay, JN, Li, J, Bogan, JR, Bogan, DJ, Chen, C, Zheng, H et al. (2010). Widespread muscle expression of an AAV9 human mini-dystrophin vector after intravenous injection in neonatal dystrophin-deficient dogs. Mol Ther 18: 1501-1508.
-
(2010)
Mol Ther
, vol.18
, pp. 1501-1508
-
-
Kornegay, J.N.1
Li, J.2
Bogan, J.R.3
Bogan, D.J.4
Chen, C.5
Zheng, H.6
-
20
-
-
58849124144
-
Hydrodynamic limb vein injection of adeno-associated virus serotype 8 vector carrying canine myostatin propeptide gene into normal dogs enhances muscle growth
-
Qiao, C, Li, J, Zheng, H, Bogan, J, Li, J, Yuan, Z et al. (2009). Hydrodynamic limb vein injection of adeno-associated virus serotype 8 vector carrying canine myostatin propeptide gene into normal dogs enhances muscle growth. Hum Gene Ther 20: 1-10.
-
(2009)
Hum Gene Ther
, vol.20
, pp. 1-10
-
-
Qiao, C.1
Li, J.2
Zheng, H.3
Bogan, J.4
Li, J.5
Yuan, Z.6
-
21
-
-
79960039072
-
AAVmediated gene therapy to the isolated limb in rhesus macaques
-
Rodino-Klapac, LR, Montgomery, CL, Mendell, JR and Chicoine, LG (2011). AAVmediated gene therapy to the isolated limb in rhesus macaques. Methods Mol Biol 709: 287-298.
-
(2011)
Methods Mol Biol
, vol.709
, pp. 287-298
-
-
Rodino-Klapac, L.R.1
Montgomery, C.L.2
Mendell, J.R.3
Chicoine, L.G.4
-
22
-
-
79960074647
-
Gene transfer to muscle from the isolated regional circulation
-
Petrov, M, Malik, A, Mead, A, Bridges, CR and Stedman, HH (2011). Gene transfer to muscle from the isolated regional circulation. Methods Mol Biol 709: 277-286.
-
(2011)
Methods Mol Biol
, vol.709
, pp. 277-286
-
-
Petrov, M.1
Malik, A.2
Mead, A.3
Bridges, C.R.4
Stedman, H.H.5
-
23
-
-
0030463485
-
Consequences of alteration in capillary permeability
-
DOI 10.1139/cjpp-74-7-824
-
Plante, GE, Chakir, M, Ettaouil, K, Lehoux, S and Sirois, P (1996). Consequences of alteration in capillary permeability. Can J Physiol Pharmacol 74: 824-833. (Pubitemid 26426572)
-
(1996)
Canadian Journal of Physiology and Pharmacology
, vol.74
, Issue.7
, pp. 824-833
-
-
Plante, G.E.1
Chakir, M.2
Ettaouil, K.3
Lehoux, S.4
Sirois, P.5
-
24
-
-
0141919796
-
Definition of venous reflux in lower-extremity veins
-
DOI 10.1016/S0741-5214(03)00424-5
-
Labropoulos, N, Tiongson, J, Pryor, L, Tassiopoulos, AK, Kang, SS, Ashraf Mansour, M et al. (2003). Definition of venous reflux in lower-extremity veins. J Vasc Surg 38: 793-798. (Pubitemid 37254810)
-
(2003)
Journal of Vascular Surgery
, vol.38
, Issue.4
, pp. 793-798
-
-
Labropoulos, N.1
Tiongson, J.2
Pryor, L.3
Tassiopoulos, A.K.4
Kang, S.S.5
Mansour, M.A.6
Baker, W.H.7
-
25
-
-
0036644465
-
ATS statement: Guidelines for the six-minute walk test
-
ATS Committee on Proficiency Standards for Clinical Pulmonary Function Laboratories
-
ATS Committee on Proficiency Standards for Clinical Pulmonary Function Laboratories (2002). ATS statement: guidelines for the six-minute walk test. Am J Respir Crit Care Med 166:111-117.
-
(2002)
Am J Respir Crit Care Med
, vol.166
, pp. 111-117
-
-
-
26
-
-
17844379455
-
The diagnotis value of intracompartmental pressure measurement, magnetic resonance imaging, and near-infrared spectroscopy in chronic exertional compartment syndrome: A prospective study in 50 patients
-
DOI 10.1177/0363546504270565
-
van den Brand, JG, Nelson, T, Verleisdonk, EJ and van der Werken, C (2005). The diagnostic value of intracompartmental pressure measurement, magnetic resonance imaging, and near-infrared spectroscopy in chronic exertional compartment syndrome: a prospective study in 50 patients. Am J Sports Med 33: 699-704. (Pubitemid 40593766)
-
(2005)
American Journal of Sports Medicine
, vol.33
, Issue.5
, pp. 699-704
-
-
Van Den Brand, J.G.H.1
Nelson, T.2
Verleisdonk, E.J.M.M.3
Van Der Werken, C.4
-
27
-
-
2442651754
-
0.5.% versus 1.0% 2-chloroprocaine for intravenous regional anesthesia: A prospective, randomized, double-blind trial
-
Marsch, SC, Sluga, M, Studer, W, Barandun, J, Scharplatz, D and Ummenhofer, W (2004). 0.5% versus 1.0% 2-chloroprocaine for intravenous regional anesthesia: a prospective, randomized, double-blind trial. Anesth Analg 98: 1789-93, table of contents. (Pubitemid 38668935)
-
(2004)
Anesthesia and Analgesia
, vol.98
, Issue.6
, pp. 1789-1793
-
-
Marsch, S.C.1
Sluga, M.2
Studer, W.3
Barandun, J.4
Scharplatz, D.5
Ummenhofer, W.6
-
28
-
-
0141681158
-
A laboratory evaluation of the Level 1 rapid infuser (H1025) and the Belmont instrument fluid management system (FMS 2000) for rapid transfusion
-
Comunale, ME (2003). A laboratory evaluation of the level 1 rapid infuser (H1025) and the Belmont instrument fluid management system (FMS 2000) for rapid transfusion. Anesth Analg. 97:1064-1069, table of contents. (Pubitemid 37158690)
-
(2003)
Anesthesia and Analgesia
, vol.97
, Issue.4
, pp. 1064-1069
-
-
Comunale, M.E.1
-
29
-
-
33744930583
-
User-guided 3D active contour segmentation of anatomical structures: Significantly improved efficiency and reliability
-
DOI 10.1016/j.neuroimage.2006.01.015, PII S1053811906000632
-
Yushkevich, PA, Piven, J, Hazlett, HC, Smith, RG, Ho, S, Gee, JC et al. (2006). User-guided 3D active contour segmentation of anatomical structures: significantly improved efficiency and reliability. Neuroimage 31: 1116-1128. (Pubitemid 43851334)
-
(2006)
NeuroImage
, vol.31
, Issue.3
, pp. 1116-1128
-
-
Yushkevich, P.A.1
Piven, J.2
Hazlett, H.C.3
Smith, R.G.4
Ho, S.5
Gee, J.C.6
Gerig, G.7
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