Special issue: Gene therapy with emphasis on RNA interference

Viruses

Volumn 7, Issue 8, 2015, Pages 4482-4487

  Lundstrom, Kenneth ^a  

^a Pan Therapeutics   (Switzerland)

Author keywords

Gene therapy; Non viral delivery; RNA interference; Viral vectors

Indexed keywords

BACULOVIRUS VECTOR; CLAUDIN 1; LENTIVIRUS VECTOR; RECOMBINANT PROTEIN; SHORT HAIRPIN RNA;

ALPHAVIRUS; BREAST CANCER; CYTOMEGALOVIRUS INFECTION; EDITORIAL; EPITHELIAL MESENCHYMAL TRANSITION; GENE DELIVERY SYSTEM; GENE THERAPY; HUMAN; METASTASIS; NONHUMAN; POSTTRANSCRIPTIONAL GENE SILENCING; RIBOZYME THERAPY; RNA INTERFERENCE; SEMLIKI FOREST VIRUS; VIRAL GENE DELIVERY SYSTEM; VIRAL GENE THERAPY; VIRUS CAPSID; ANIMAL; PROCEDURES;

ANIMALS; GENETIC THERAPY; HUMANS; RNA INTERFERENCE;

EID: 84941079088     PISSN: None     EISSN: 19994915     Source Type: Journal    
DOI: 10.3390/v7082830     Document Type: Editorial

References (22)

1. Raper, S.E.; Chirmule, N.; Lee, F.S.; Wivel, N.A.; Bagg, A.; Gao, P.; Wilson, J.M.; Batshaw, M.L. Fatal systemic inflammatory response syndrome in a ornithine transcarbamylase deficient patient following adenoviral gene transfer. Mol. Genet. Metab. 2003, 80, 148-158. [CrossRef] [PubMed]
2. McCormack, M.P.; Rabbitts, T.H. Activation of the T-cell oncogene LMO2 after gene therapy for X-linked severe combined immunodeficiency. New Engl. J. Med. 2004, 350, 913-922. [CrossRef] [PubMed]
3. Ginn, S.L.; Alexander, I.E.; Edelstein, M.L.; Abedi, M.R.; Wixon, J. Gene therapy clinical trials worldwide-An update. J. Gene Med. 2013, 15, 65-77. [CrossRef] [PubMed]
4. Reinhart, B.J.; Slack, F.J.; Basson, M.; Pasquinelli, A.E.; Bettinger, J.C.; Rougvie, A.E.; Horvitz, H.R.; Ruvkun, G. The 21-nucleotide let-7 RNA regulates developmental timing in Caenorrhabdatis elegans. Nature 2000, 403, 901-906. [PubMed]
5. Shah, P.P.; Hutchinson, L.E.; Kakar, S.S. Emerging roles of miRNAs in diagnosis and treatment of various diseases including ovarian cancer. J. Ovarian Res. 2009, 2, e11. [CrossRef] [PubMed]
6. Sandig, V.; Hofmann, C.; Steinert, S.; Jennings, G.; Schlag, P.; Strauss, M. Gene transfer into hepatocytes and human liver tissue by baculovirus vectors. Hum. Gene Ther. 1996, 7, 1937-1945. [CrossRef] [PubMed]
7. Valdes, V.J.; Sampieri, A.; Sepulveda, J.; Vaca, L. Using double-stranded RNA to prevent in vitro and in vivo viral infections by recombinant baculovirus. J. Biol. Chem. 2003, 278, 19317-19324. [CrossRef] [PubMed]
8. Hebert, C.G.; Valdes, J.J.; Bentley, W.E. In vitro and in vivo RNA interference mediated suppression of Tn-caspase-1 for improved recombinant protein production in High Five cell culture with the baculovirus expression vector system. Biotechnol. Bioeng. 2009, 104, 390-399. [CrossRef] [PubMed]
9. Nicholson, L.J.; Philippe, M.; Paine, A.J.; Mann, D.A.; Dolphin, C.T. RNA interference mediated in human primary cells via recombinant baculoviral vectors. Mol. Ther. 2005, 11, 638-644. [CrossRef] [PubMed]
10. Ong, S.T.; Li, F.; Du, J.; Tan, Y.W.; Wang, S. Hybrid cytomegalovirus enhancer-h1 promoter-based plasmid and baculovirus vectors mediate effective RNA interference. Hum. Gene Ther. 2005, 16, 1404-1412. [CrossRef] [PubMed]
11. Chen, C.-L.; Tseng, Y.-W.; Wu, J.-C.; Chen, G.-Y.; Lin, K.-C.; Hwang, S.-M.; Hu, Y.-C. Suppression of hepatocellular carcinoma by baculovirus-mediated expression of long non-coding RNA PTENP1 and MicroRNA regulation. Biomaterials 2015, 44, 71-81. [CrossRef] [PubMed]
12. Lin, J.; Teo, S.; Lam, D.H.; Jeyaseelan, K.; Wang, S. MicroRNA-10b pleiotropically regulates invasion, angiogenicity and apoptosis of tumor cells resembling mesenchymal subtype of glioblastoma multiforme. Cell Death Dis. 2012, 3, e398. [CrossRef] [PubMed]
13. Suzuki, H.; Tamai, N.; Habu, Y.; Chang, M.O.O.; Takaku, H. Suppression of hepatitis C virus replication by baculovirus vector-mediated short-hairpin RNA expression. FEBS Lett. 2008, 582, 3085-3089. [CrossRef] [PubMed]
14. Lundstrom, K. Biology and application of alphaviruses in gene therapy. Gene Ther. 2005, 12 (Suppl. 1), S92-S97. [CrossRef] [PubMed]
15. Lundstrom, K. Alphavirus-based vaccines. Viruses 2014, 6, 2392-2415. [CrossRef] [PubMed]
16. Ylösmäki, E.; Martikainen, M.; Hinkkanen, A.; Saksela, K. Attenuation of Semliki Forest virus neurovirulence by micro-RNA detargeting. J. Virol. 2013, 87, 335-344. [CrossRef] [PubMed]
17. Bobbin, M.L.; Burnett, J.C.; Rossi, J.J. RNA interference approaches for treatment of HIV infection. Genome Med. 2015, 7, e50. [CrossRef] [PubMed]
18. Chung, J.; Scherer, L.J.; Gu, A.; Gardner, A.M.; Torres-Coronado, M.; Epps, E.W.; Digiusto, D.L.; Rossi, J.J. Optimized lentiviral vectors for HIV gene therapy: Multiplexed expression of small RNAs and inclusion of MGMT(P140K) drug resistance gene. Mol. Ther. 2014, 22, 952-963. [CrossRef] [PubMed]
19. Habib, R.; Akhtar, J.; Taqi, M.; Yu, C.; Zhang, C. Lentiviral vector-mdeiated survivin shRNA delivery in gastric cancer cell lines significantly inhibits cell proliferation and tumor growth. Oncol. Rep. 2015, 34, 859-867. [PubMed]
20. Pozzuto, T.; Röger, C.; Kurreck, J.; Fechner, H. Enhanced suppression of adenovirus replication by triple combination of anti-adenoviral siRNAs, soluble adenovirus receptor trap sCAR-Fc and cidofovir. Antivir. Res. 2015, 120, 72-78. [CrossRef] [PubMed]
21. Bisset, D.R.; Stepniak-Konieczna, E.A.; Zavaljevski, M.; Wei, J.; Carter, G.T.; Weiss, M.D.; Chamberlain, J.R. Therapeutic impact of systemic AAV-mediated RNA interference in a mouse model of myotonic dystrophy. Hum. Mol. Genet. 2015. [CrossRef] [PubMed]
22. Zhu, Z.; Chen, W.; Hao, L.; Zhu, G.; Lu, Y.; Li, S.; Wang, L.; Li, Y.P. Ac45 silencing mediated by AAV-sh-Ac45-RNAi prevents both bone loss and inflammation caused by periodontitis. J. Clin. Periodontol. 2015. [CrossRef] [PubMed]