Therapy of Genetic Disorders: Novel Therapies for Duchenne Muscular Dystrophy

Current Pediatrics Reports

Volumn 2, Issue 2, 2014, Pages 102-112

  Seto, Jane T ^a   Bengtsson, Niclas E ^a   Chamberlain, Jeffrey S ^a  

^a UNIVERSITY OF WASHINGTON   (United States)

Author keywords

Adeno associated viral vectors; Antisense oligonucleotide; Duchenne muscular dystrophy; Dystrophin; Gene therapy; Inducible pluripotent stem cell; Mesoangioblast; Myoblast; Satellite cell

Indexed keywords

EID: 84919951141     PISSN: None     EISSN: 21674841     Source Type: Journal    
DOI: 10.1007/s40124-014-0044-x     Document Type: Article

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