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Volumn 24, Issue 6, 2013, Pages 584-594

Long-term robust myocardial transduction of the dog heart from a peripheral vein by adeno-associated virus serotype-8

Author keywords

[No Author keywords available]

Indexed keywords

ALKALINE PHOSPHATASE PLACENTA ISOENZYME; PARVOVIRUS VECTOR;

EID: 84879182056     PISSN: 10430342     EISSN: 15577422     Source Type: Journal    
DOI: 10.1089/hum.2013.044     Document Type: Article
Times cited : (26)

References (32)
  • 1
    • 56749102970 scopus 로고    scopus 로고
    • Percutaneous transendocardial delivery of self-complementary adenoassociated virus 6 achieves global cardiac gene transfer in canines
    • Bish, L.T., Sleeper, M.M., Brainard, B., et al. (2008). Percutaneous transendocardial delivery of self-complementary adenoassociated virus 6 achieves global cardiac gene transfer in canines. Mol. Ther. 16, 1953-1959.
    • (2008) Mol. Ther. , vol.16 , pp. 1953-1959
    • Bish, L.T.1    Sleeper, M.M.2    Brainard, B.3
  • 2
    • 35848961457 scopus 로고    scopus 로고
    • Systemic AAV-9 transduction in mice is influenced by animal age but not by the route of administration
    • Bostick, B., Ghosh, A., Yue, Y., et al. (2007). Systemic AAV-9 transduction in mice is influenced by animal age but not by the route of administration. Gene Ther. 14, 1605-1609.
    • (2007) Gene Ther. , vol.14 , pp. 1605-1609
    • Bostick, B.1    Ghosh, A.2    Yue, Y.3
  • 3
    • 67651087321 scopus 로고    scopus 로고
    • Exploiting and antagonizing microrna regulation for therapeutic and experimental applications
    • Brown, B.D., and Naldini, L. (2009). Exploiting and antagonizing microrna regulation for therapeutic and experimental applications. Nat. Rev. Genet. 10, 578-585.
    • (2009) Nat. Rev. Genet. , vol.10 , pp. 578-585
    • Brown, B.D.1    Naldini, L.2
  • 4
    • 84864008603 scopus 로고    scopus 로고
    • Human galectin 3 binding protein interacts with recombinant adeno-associated virus type 6
    • Denard, J., Beley, C., Kotin, R., et al. (2012). Human galectin 3 binding protein interacts with recombinant adeno-associated virus type 6. J. Virol. 86, 6620-6631.
    • (2012) J. Virol. , vol.86 , pp. 6620-6631
    • Denard, J.1    Beley, C.2    Kotin, R.3
  • 5
    • 84862018387 scopus 로고    scopus 로고
    • Duchenne muscular dystrophy gene therapy: Lost in translation? Res
    • Duan, D. (2011a). Duchenne muscular dystrophy gene therapy: lost in translation? Res. Rep. Biol. 2, 31-42.
    • (2011) Rep. Biol. , vol.2 , pp. 31-42
    • Duan, D.1
  • 6
    • 80054946993 scopus 로고    scopus 로고
    • Gene delivery to the heart: An updated review on vectors and methods
    • Duan, D. (2011b). Gene delivery to the heart: an updated review on vectors and methods. J. Gene Med. 13, 556.
    • (2011) J. Gene Med. , vol.13 , pp. 556
    • Duan, D.1
  • 7
    • 79960089426 scopus 로고    scopus 로고
    • Age-matched comparison reveals early electrocardiography and echocardiography changes in dystrophin-deficient dogs
    • Fine, D.M., Shin, J.H., Yue, Y., et al. (2011). Age-matched comparison reveals early electrocardiography and echocardiography changes in dystrophin-deficient dogs. Neuromuscul. Disord. 21, 453-461.
    • (2011) Neuromuscul. Disord. , vol.21 , pp. 453-461
    • Fine, D.M.1    Shin, J.H.2    Yue, Y.3
  • 8
    • 4043092073 scopus 로고    scopus 로고
    • Systemic delivery of genes to striated muscles using adenoassociated viral vectors
    • Gregorevic, P., Blankinship, M.J., Allen, J.M., et al. (2004). Systemic delivery of genes to striated muscles using adenoassociated viral vectors. Nat. Med. 10, 828-834.
    • (2004) Nat. Med. , vol.10 , pp. 828-834
    • Gregorevic, P.1    Blankinship, M.J.2    Allen, J.M.3
  • 9
    • 33745143956 scopus 로고    scopus 로고
    • Robust systemic transduction with AAV9 vectors in mice: Efficient global cardiac gene transfer superior to that of AAV8
    • Inagaki, K., Fuess, S., Storm, T.A., et al. (2006). Robust systemic transduction with AAV9 vectors in mice: efficient global cardiac gene transfer superior to that of AAV8. Mol. Ther. 14, 45-53.
    • (2006) Mol. Ther. , vol.14 , pp. 45-53
    • Inagaki, K.1    Fuess, S.2    Storm, T.A.3
  • 10
    • 80054955037 scopus 로고    scopus 로고
    • Gene delivery methods in cardiac gene therapy
    • Ishikawa, K., Tilemann, L., Fish, K., and Hajjar, R.J. (2011). Gene delivery methods in cardiac gene therapy. J. Gene Med. 13, 566-572.
    • (2011) J. Gene Med. , vol.13 , pp. 566-572
    • Ishikawa, K.1    Tilemann, L.2    Fish, K.3    Hajjar, R.J.4
  • 11
    • 62649133817 scopus 로고    scopus 로고
    • Calcium upregulation by percutaneous administration of gene therapy in cardiac disease (Cupid Trial), a first-in-human phase 1/2 clinical trial
    • Jaski, B.E., Jessup, M.L., Mancini, D.M., et al. (2009). Calcium upregulation by percutaneous administration of gene therapy in cardiac disease (Cupid Trial), a first-in-human phase 1/2 clinical trial. J. Card. Fail. 15, 171-181.
    • (2009) J. Card. Fail. , vol.15 , pp. 171-181
    • Jaski, B.E.1    Jessup, M.L.2    Mancini, D.M.3
  • 12
    • 79961032369 scopus 로고    scopus 로고
    • Calcium Upregulation by Percutaneous Administration of Gene Therapy in Cardiac Disease (CUPID): A phase 2 trial of intracoronary gene therapy of sarcoplasmic reticulum Ca2 +-ATPase in patients with advanced heart failure
    • Jessup, M., Greenberg, B., Mancini, D., et al. (2011). Calcium Upregulation by Percutaneous Administration of Gene Therapy in Cardiac Disease (CUPID): a phase 2 trial of intracoronary gene therapy of sarcoplasmic reticulum Ca2 +-ATPase in patients with advanced heart failure. Circulation 124, 304-313.
    • (2011) Circulation , vol.124 , pp. 304-313
    • Jessup, M.1    Greenberg, B.2    Mancini, D.3
  • 13
    • 80054946146 scopus 로고    scopus 로고
    • Modelspecific selection of molecular targets for heart failure gene therapy
    • Katz, M.G., Fargnoli, A.S., Tomasulo, C.E., et al. (2011). Modelspecific selection of molecular targets for heart failure gene therapy. J. Gene Med. 13, 573-586.
    • (2011) J. Gene Med. , vol.13 , pp. 573-586
    • Katz, M.G.1    Fargnoli, A.S.2    Tomasulo, C.E.3
  • 14
    • 61649088631 scopus 로고    scopus 로고
    • MicroRNAs and the regulation of vector tropism
    • Kelly, E.J., and Russell, S.J. (2009). MicroRNAs and the regulation of vector tropism. Mol. Ther. 17, 409-416.
    • (2009) Mol. Ther. , vol.17 , pp. 409-416
    • Kelly, E.J.1    Russell, S.J.2
  • 15
    • 41149109650 scopus 로고    scopus 로고
    • Aav vectormediated reversal of hypoglycemia in canine and murine glycogen storage disease type Ia
    • Koeberl, D.D., Pinto, C., Sun, B., et al. (2008). Aav vectormediated reversal of hypoglycemia in canine and murine glycogen storage disease type Ia. Mol. Ther. 16, 665-672.
    • (2008) Mol. Ther. , vol.16 , pp. 665-672
    • Koeberl, D.D.1    Pinto, C.2    Sun, B.3
  • 16
    • 84862848384 scopus 로고    scopus 로고
    • Cardiac gene therapy: From concept to reality
    • Kratlian, R.G., and Hajjar, R.J. (2012). Cardiac gene therapy: from concept to reality. Curr. Heart Fail. Rep. 9, 33-39.
    • (2012) Curr. Heart Fail. Rep. , vol.9 , pp. 33-39
    • Kratlian, R.G.1    Hajjar, R.J.2
  • 17
    • 84862026502 scopus 로고    scopus 로고
    • Progress in gene therapy of dystrophic heart disease
    • Lai, Y., and Duan, D. (2012). Progress in gene therapy of dystrophic heart disease. Gene Ther. 19, 678-685.
    • (2012) Gene Ther. , vol.19 , pp. 678-685
    • Lai, Y.1    Duan, D.2
  • 18
    • 0033066691 scopus 로고    scopus 로고
    • Synthetic muscle promoters: Activities exceeding naturally occurring regulatory sequences
    • Li, X., Eastman, E.M., Schwartz, R.J., and Draghia-Akli, R. (1999). Synthetic muscle promoters: activities exceeding naturally occurring regulatory sequences. Nat. Biotechnol. 17, 241-245.
    • (1999) Nat. Biotechnol. , vol.17 , pp. 241-245
    • Li, X.1    Eastman, E.M.2    Schwartz, R.J.3    Draghia-Akli, R.4
  • 20
    • 33747518710 scopus 로고    scopus 로고
    • Recombinant adeno-associated virus serotype 9 leads to preferential cardiac transduction in vivo
    • Pacak, C.A., Mah, C.S., Thattaliyath, B.D., et al. (2006). Recombinant adeno-associated virus serotype 9 leads to preferential cardiac transduction in vivo. Circ. Res. 99, e3-9.
    • (2006) Circ. Res. , vol.99
    • Pacak, C.A.1    Mah, C.S.2    Thattaliyath, B.D.3
  • 21
    • 84856958590 scopus 로고    scopus 로고
    • Neutralizing antibodies against AAV serotypes 1, 2, 6, and 9 in sera of commonly used animal models
    • Rapti, K., Louis-Jeune, V., Kohlbrenner, E., et al. (2012). Neutralizing antibodies against AAV serotypes 1, 2, 6, and 9 in sera of commonly used animal models. Mol. Ther. 20, 73-83.
    • (2012) Mol. Ther. , vol.20 , pp. 73-83
    • Rapti, K.1    Louis-Jeune, V.2    Kohlbrenner, E.3
  • 22
    • 33645908797 scopus 로고    scopus 로고
    • Long-term efficacy of adeno-associated virus serotypes 8 and 9 in hemophilia a dogs and mice
    • Sarkar, R., Mucci, M., Addya, S., et al. (2006). Long-term efficacy of adeno-associated virus serotypes 8 and 9 in hemophilia a dogs and mice. Hum. Gene Ther. 17, 427-439.
    • (2006) Hum. Gene Ther. , vol.17 , pp. 427-439
    • Sarkar, R.1    Mucci, M.2    Addya, S.3
  • 23
    • 84555191581 scopus 로고    scopus 로고
    • Recombinant adenoassociated viral vector production and purification
    • Shin, J.H., Yue, Y., and Duan, D. (2012a). Recombinant adenoassociated viral vector production and purification. Methods Mol. Biol. 798, 267-284.
    • (2012) Methods Mol. Biol. , vol.798 , pp. 267-284
    • Shin, J.H.1    Yue, Y.2    Duan, D.3
  • 24
    • 84863419418 scopus 로고    scopus 로고
    • Humoral immunity to AAV-6, 8, and 9 in normal and dystrophic dogs
    • Shin, J.H., Yue, Y., Smith, B., and Duan, D. (2012b). Humoral immunity to AAV-6, 8, and 9 in normal and dystrophic dogs. Hum. Gene Ther. 23, 287-294.
    • (2012) Hum. Gene Ther. , vol.23 , pp. 287-294
    • Shin, J.H.1    Yue, Y.2    Smith, B.3    Duan, D.4
  • 25
    • 84863393197 scopus 로고    scopus 로고
    • A simplified immune suppression scheme leads to persistent microdystrophin expression in Duchenne muscular dystrophy dogs
    • Shin, J.H., Yue, Y., Srivastava, A., et al. (2012c). A simplified immune suppression scheme leads to persistent microdystrophin expression in Duchenne muscular dystrophy dogs. Hum. Gene Ther. 23, 202-209.
    • (2012) Hum. Gene Ther. , vol.23 , pp. 202-209
    • Shin, J.H.1    Yue, Y.2    Srivastava, A.3
  • 26
    • 79551596262 scopus 로고    scopus 로고
    • An intronic LINE-1 element insertion in the dystrophin gene aborts dystrophin expression and results in Duchenne-like muscular dystrophy in the corgi breed
    • Smith, B.F., Yue, Y., Woods, P.R., et al. (2011). An intronic LINE-1 element insertion in the dystrophin gene aborts dystrophin expression and results in Duchenne-like muscular dystrophy in the corgi breed. Lab. Invest. 91, 216-231.
    • (2011) Lab. Invest. , vol.91 , pp. 216-231
    • Smith, B.F.1    Yue, Y.2    Woods, P.R.3
  • 27
    • 19644378907 scopus 로고    scopus 로고
    • Adeno-associated virus serotype 8 efficiently delivers genes to muscle and heart
    • Wang, Z., Zhu, T., Qiao, C., et al. (2005). Adeno-associated virus serotype 8 efficiently delivers genes to muscle and heart. Nat. Biotechnol. 23, 321-328.
    • (2005) Nat. Biotechnol. , vol.23 , pp. 321-328
    • Wang, Z.1    Zhu, T.2    Qiao, C.3
  • 28
    • 80054949849 scopus 로고    scopus 로고
    • The evolution of heart gene delivery vectors
    • Wasala, N.B., Shin, J.H., and Duan, D. (2011). The evolution of heart gene delivery vectors. J. Gene Med. 13, 557-565.
    • (2011) J. Gene Med. , vol.13 , pp. 557-565
    • Wasala, N.B.1    Shin, J.H.2    Duan, D.3
  • 29
    • 56749104321 scopus 로고    scopus 로고
    • A single intravenous injection of adeno-associated virus serotype-9 leads to whole body skeletal muscle transduction in dogs
    • Yue, Y., Ghosh, A., Long, C., et al. (2008). A single intravenous injection of adeno-associated virus serotype-9 leads to whole body skeletal muscle transduction in dogs. Mol. Ther. 16, 1944-1952.
    • (2008) Mol. Ther. , vol.16 , pp. 1944-1952
    • Yue, Y.1    Ghosh, A.2    Long, C.3
  • 30
    • 79960066008 scopus 로고    scopus 로고
    • Whole body skeletal muscle transduction in neonatal dogs with AAV-9
    • Yue, Y., Shin, J.-H., and Duan, D. (2011). Whole body skeletal muscle transduction in neonatal dogs with AAV-9. Methods Mol. Biol. 709, 313-329.
    • (2011) Methods Mol. Biol. , vol.709 , pp. 313-329
    • Yue, Y.1    Shin, J.-H.2    Duan, D.3
  • 31
    • 84864375254 scopus 로고    scopus 로고
    • Immunosuppression decreases inflammation and increases AAV6-hSERCA2a-mediated SERCA2a expression
    • Zhu, X., McTiernan, C.F., Rajagopalan, N., et al. (2012). Immunosuppression decreases inflammation and increases AAV6-hSERCA2a-mediated SERCA2a expression. Hum. Gene Ther. 23, 722-732.
    • (2012) Hum. Gene Ther. , vol.23 , pp. 722-732
    • Zhu, X.1    McTiernan, C.F.2    Rajagopalan, N.3
  • 32
    • 44349170706 scopus 로고    scopus 로고
    • Analysis of AAV serotypes 1-9 mediated gene expression and tropism in mice after systemic injection
    • Zincarelli, C., Soltys, S., Rengo, G., and Rabinowitz, J.E. (2008). Analysis of AAV serotypes 1-9 mediated gene expression and tropism in mice after systemic injection. Mol. Ther. 16, 1073-1080.
    • (2008) Mol. Ther. , vol.16 , pp. 1073-1080
    • Zincarelli, C.1    Soltys, S.2    Rengo, G.3    Rabinowitz, J.E.4


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