Gene therapy for stargardt disease associated with ABCA4 gene

Advances in Experimental Medicine and Biology

Volumn 801, Issue , 2014, Pages 719-724

  Han, Zongchao ^a   Conley, Shannon M ^a   Naash, Muna I ^a  

^a UNIVERSITY OF OKLAHOMA COLLEGE OF MEDICINE   (United States)

Author keywords

ABCA4; Gene therapy; Lentivirus; Nanoparticles; Non viral; STGD1; Viral

Indexed keywords

ABC TRANSPORTER; COMPLEMENTARY DNA; DNA; LENTIVIRUS VECTOR; MACROGOL; NANOPARTICLE; PARVOVIRUS VECTOR; POLYLYSINE; PROTEIN ABCA4; UNCLASSIFIED DRUG; ABCA4 PROTEIN, MOUSE;

ABCA4 GENE; ARTICLE; CELL THERAPY; DRUG EFFICACY; DRUG SAFETY; EMBRYONIC STEM CELL; GENE; GENE THERAPY; GENE TRANSFER; GENETIC ASSOCIATION; HUMAN; NONHUMAN; NONVIRAL GENE DELIVERY SYSTEM; PHASE 1 CLINICAL TRIAL (TOPIC); PHASE 2 CLINICAL TRIAL (TOPIC); PIGMENT EPITHELIUM; PRIORITY JOURNAL; STARGARDT DISEASE; UNSPECIFIED SIDE EFFECT; VIRAL GENE DELIVERY SYSTEM; ANIMAL; DISEASE MODEL; GENETICS; KNOCKOUT MOUSE; LENTIVIRINAE; METHODOLOGY; MOUSE; RETINA MACULA DEGENERATION; REVIEW;

LENTIVIRUS; MURINAE;

ANIMALS; ATP-BINDING CASSETTE TRANSPORTERS; DISEASE MODELS, ANIMAL; GENETIC THERAPY; HUMANS; LENTIVIRUS; MACULAR DEGENERATION; MICE; MICE, KNOCKOUT; NANOPARTICLES;

EID: 84904792543     PISSN: 00652598     EISSN: 22148019     Source Type: Book Series    
DOI: 10.1007/978-1-4614-3209-8_90     Document Type: Article

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