Correction of hyperbilirubinemia in gunn rats by surgical delivery of low doses of helper-dependent adenoviral vectors

Human Gene Therapy Methods

Volumn 25, Issue 3, 2014, Pages 181-186

  Schmitt, Françoise ^a,b   Pastore, Nunzia ^c   Abarrategui Pontes, Cecilia ^a   Flageul, Maude ^a   Myara, Anne ^d   Laplanche, Sophie ^d   Labrune, Philippe ^e   Podevin, Guillaume ^b,f   Nguyen, Tuan Huy ^a   Brunetti Pierri, Nicola ^c,g  

^a NANTES UNIVERSITY HOSPITAL   (France)

^b Pediatric Hepatogastroenterology HIFIH Laboratory UPRES 3859 SFR 4038   (France)

^c TELETHON INSTITUTE OF GENETICS AND MEDICINE TIGEM   (Italy)

^d SAINT JOSEPH HOSPITAL   (France)

^e HÔPITAL ANTOINE BÉCLÈRE   (France)

^f INSERM   (France)

^g UNIVERSITY OF NAPLES FEDERICO II   (Italy)

Author keywords

[No Author keywords available]

Indexed keywords

BILIRUBIN; GLUCURONOSYLTRANSFERASE; UGT1A1 ENZYME;

ANIMAL EXPERIMENT; ANIMAL MODEL; ARTICLE; BILIRUBIN BLOOD LEVEL; CONTROLLED STUDY; GUNN RAT; HELPER DEPENDENT ADENOVIRUS; HYPERBILIRUBINEMIA; INSTRUMENTAL DELIVERY; ISOLATED LIVER; MALE; NONHUMAN; PRIORITY JOURNAL; RAT; VIRUS GENOME; ADENOVIRIDAE; ANIMAL; BLOOD; CRIGLER-NAJJAR SYNDROME; GENE THERAPY; GENE VECTOR; GENETIC TRANSDUCTION; GENETICS; HUMAN; LIVER; METABOLISM; PROMOTER REGION; SURGERY;

ADENOVIRIDAE; ANIMALS; BILIRUBIN; CRIGLER-NAJJAR SYNDROME; GENETIC THERAPY; GENETIC VECTORS; GLUCURONOSYLTRANSFERASE; HUMANS; HYPERBILIRUBINEMIA; LIVER; PROMOTER REGIONS, GENETIC; RATS; RATS, GUNN; TRANSDUCTION, GENETIC;

EID: 84902602382     PISSN: 19466536     EISSN: 19466544     Source Type: Journal    
DOI: 10.1089/hgtb.2013.236     Document Type: Article

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