Critical assessment of lifelong phenotype correction in hyperbilirubinemic Gunn rats after retroviral mediated gene transfer

Gene Therapy

Volumn 14, Issue 17, 2007, Pages 1270-1277

  Nguyen, T H ^a   Aubert, D ^a   Bellodi Privato, M ^a   Flageul, M ^a   Pichard, V ^a   Jaidane Abdelghani, Z ^b   Myara, A ^b   Ferry, N ^a  

^a HÔTEL DIEU   (France)

^b SAINT JOSEPH HOSPITAL   (France)

Author keywords

[No Author keywords available]

Indexed keywords

BILIRUBIN GLUCURONIDE; COMPLEMENTARY DNA; GLUCURONOSYLTRANSFERASE; LENTIVIRUS VECTOR; RETROVIRUS VECTOR;

ANIMAL EXPERIMENT; ANIMAL MODEL; ANIMAL TISSUE; ARTICLE; BILE; CONTROLLED STUDY; CRIGLER NAJJAR SYNDROME; ENZYME ACTIVITY; ENZYME DEFICIENCY; FEMALE; GENE TRANSFER; GENETIC TRANSDUCTION; GUNN RAT; HAPLOIDY; HEPATITIS; HUMAN; HYPERBILIRUBINEMIA; IMMUNE RESPONSE; LIVER CELL; LIVER HISTOLOGY; MALE; NONHUMAN; PHENOTYPE; POLYMERASE CHAIN REACTION; PRIORITY JOURNAL; PROMOTER REGION; TISSUE DISTRIBUTION; VIRAL GENE THERAPY;

ANIMALS; ANIMALS, NEWBORN; BILIRUBIN; CONCANAVALIN A; CRIGLER-NAJJAR SYNDROME; FEMALE; GENE EXPRESSION; GENE THERAPY; GENETIC ENGINEERING; GENETIC VECTORS; GLUCURONOSYLTRANSFERASE; GREEN FLUORESCENT PROTEINS; HEPATOCYTES; HUMANS; INJECTIONS, INTRAVENOUS; LENTIVIRUS; LEUKEMIA VIRUS, MURINE; LIVER; LIVER FUNCTION TESTS; MALE; MODELS, ANIMAL; PHENOTYPE; RATS; RATS, GUNN; RETROVIRIDAE; TIME FACTORS; TRANSDUCTION, GENETIC; TRANSGENES;

RATTUS NORVEGICUS;

EID: 34548118717     PISSN: 09697128     EISSN: 14765462     Source Type: Journal    
DOI: 10.1038/sj.gt.3302993     Document Type: Article

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