A novel screening system improves genetic correction by internal exon replacement

Nucleic Acids Research

Volumn 39, Issue 16, 2011, Pages

  Koller, Ulrich ^a   Wally, Verena ^a   Mitchell, Lloyd G ^b   Klausegger, Alfred ^a   Murauer, Eva M ^a   Mayr, Elisabeth ^a   Gruber, Christina ^a   Hainzl, Stefan ^a   Hintner, Helmut ^a   Bauer, Johann W ^a  

^a PARACELSUS MEDICAL UNIVERSITY   (Austria)

^b Retro Therapy   (United States)

Author keywords

[No Author keywords available]

Indexed keywords

GREEN FLUORESCENT PROTEIN;

ARTICLE; COL17A1 GENE; CONTROLLED STUDY; EPIDERMOLYSIS BULLOSA; EXON; FLUORESCENCE ANALYSIS; GENE; GENE EXPRESSION; GENE IDENTIFICATION; GENE MUTATION; GENE SEQUENCE; GENE TARGETING; GENETIC ENGINEERING; GENETIC SCREENING; GENETIC TRANSFECTION; HUMAN; HUMAN CELL; INTERNAL EXON REPLACEMENT; INTRON; MOLECULAR CLONING; NUCLEIC ACID BASE SUBSTITUTION; PRIORITY JOURNAL; TRANS SPLICING;

AUTOANTIGENS; BLOTTING, WESTERN; CELL LINE; EXONS; FLOW CYTOMETRY; FLUORESCENT DYES; GENES, REPORTER; GENETIC TECHNIQUES; GREEN FLUORESCENT PROTEINS; HEK293 CELLS; HUMANS; NON-FIBRILLAR COLLAGENS; RNA, MESSENGER; TRANS-SPLICING;

EID: 80052498191     PISSN: 03051048     EISSN: 13624962     Source Type: Journal    
DOI: 10.1093/nar/gkr465     Document Type: Article

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