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Volumn 39, Issue 16, 2011, Pages

A novel screening system improves genetic correction by internal exon replacement

Author keywords

[No Author keywords available]

Indexed keywords

GREEN FLUORESCENT PROTEIN;

EID: 80052498191     PISSN: 03051048     EISSN: 13624962     Source Type: Journal    
DOI: 10.1093/nar/gkr465     Document Type: Article
Times cited : (25)

References (18)
  • 1
    • 27144477400 scopus 로고    scopus 로고
    • Gene therapy progress and prospects: Reprograming gene expression by trans-splicing
    • DOI 10.1038/sj.gt.3302596, PII 3302596
    • Mitchell, L.G. and McGarrity, G.J. (2005) Gene therapy progress and prospects: reprograming gene expression by trans-splicing. Gene Ther., 12, 1477-1485. (Pubitemid 41508672)
    • (2005) Gene Therapy , vol.12 , Issue.20 , pp. 1477-1485
    • Mitchell, L.G.1    McGarrity, G.J.2
  • 3
    • 0141743742 scopus 로고    scopus 로고
    • 5′ Exon replacement and repair by spliceosome-mediated RNA trans-splicing
    • DOI 10.1261/rna.5101903
    • Mansfield, S.G., Clark, R.H., Puttaraju, M., Kole, J., Cohn, J.A., Mitchell, L.G. and Garcia-Blanco, M.A. (2003) 50 exon replacement and repair by spliceosome-mediated RNA trans-splicing. RNA, 9, 1290-1297. (Pubitemid 37151683)
    • (2003) RNA , vol.9 , Issue.10 , pp. 1290-1297
    • Mansfield, S.G.1    Clark, R.H.2    Puttaraju, M.3    Kole, J.4    Cohn, J.A.5    Mitchell, L.G.6    Garcia-Blanco, M.A.7
  • 4
    • 0034889309 scopus 로고    scopus 로고
    • Messenger RNA repair and restoration of protein function by spliceosome-mediated RNa trans-splicing
    • DOI 10.1006/mthe.2001.0426
    • Puttaraju, M., DiPasquale, J., Baker, C.C., Mitchell, L.G. and Garcia-Blanco, M.A. (2001) Messenger RNA repair and restoration of protein function by spliceosome-mediated RNA trans-splicing. Mol. Ther., 4, 105-114. (Pubitemid 32776501)
    • (2001) Molecular Therapy , vol.4 , Issue.2 , pp. 105-114
    • Puttaraju, M.1    DiPasquale, J.2    Baker, C.C.3    Mitchell, L.G.4    Garcia-Blanco, M.A.5
  • 5
    • 47949120992 scopus 로고    scopus 로고
    • Conserved RNA secondary structures promote alternative splicing
    • Shepard, P.J. and Hertel, K.J. (2008) Conserved RNA secondary structures promote alternative splicing. RNA, 14, 1463-1469.
    • (2008) RNA , vol.14 , pp. 1463-1469
    • Shepard, P.J.1    Hertel, K.J.2
  • 9
    • 4043179784 scopus 로고    scopus 로고
    • Trans-splicing repair of CD40 ligand deficiency results in naturally regulated correction of a mouse model of hyper-IgM X-linked immunodeficiency
    • DOI 10.1038/nm1086
    • Tahara, M., Pergolizzi, R.G., Kobayashi, H., Krause, A., Luettich, K., Lesser, M.L. and Crystal, R.G. (2004) Trans-splicing repair of CD40 ligand deficiency results in naturally regulated correction of a mouse model of hyper-IgM X-linked immunodeficiency. Nat. Med., 10, 835-841. (Pubitemid 39070857)
    • (2004) Nature Medicine , vol.10 , Issue.8 , pp. 835-841
    • Tahara, M.1    Pergolizzi, R.G.2    Kobayashi, H.3    Krause, A.4    Luettich, K.5    Lesser, M.L.6    Crystal, R.G.7
  • 10
    • 34447542621 scopus 로고    scopus 로고
    • Using 5′-PTMs to repair mutant β-globin transcripts
    • DOI 10.1261/rna.525607
    • Kierlin-Duncan, M.N. and Sullenger, B.A. (2007) Using 50-PTMs to repair mutant beta-globin transcripts. RNA, 13, 1317-1327. (Pubitemid 47080476)
    • (2007) RNA , vol.13 , Issue.8 , pp. 1317-1327
    • Kierlin-Duncan, M.N.1    Sullenger, B.A.2
  • 14
    • 77956509696 scopus 로고    scopus 로고
    • Exon exchange approach to repair duchenne dystrophin transcripts
    • Lorain, S., Peccate, C., Le Hir, M. and Garcia, L. (2010) Exon exchange approach to repair duchenne dystrophin transcripts. PloS One, 5, e10894.
    • (2010) PloS One , vol.5
    • Lorain, S.1    Peccate, C.2    Le Hir, M.3    Garcia, L.4
  • 15
    • 0037272530 scopus 로고    scopus 로고
    • Type XVII collagen gene mutations in junctional epidermolysis bullosa and prospects for gene therapy
    • DOI 10.1046/j.1365-2230.2003.01192.x
    • Bauer, J.W. and Lanschuetzer, C. (2003) Type XVII collagen gene mutations in junctional epidermolysis bullosa and prospects for gene therapy. Clin. Exp. Dermatol., 28, 53-60. (Pubitemid 36197565)
    • (2003) Clinical and Experimental Dermatology , vol.28 , Issue.1 , pp. 53-60
    • Bauer, J.W.1    Lanschuetzer, C.2
  • 18
    • 0043175257 scopus 로고    scopus 로고
    • Development of spliceosome-mediated RNA trans-splicing (SMaRT™) for the correction of inherited skin diseases
    • DOI 10.1034/j.1600-0625.2003.120105.x
    • Dallinger, G., Puttaraju, M., Mitchell, L.G., Yancey, K.B., Yee, C., Klausegger, A., Hintner, H. and Bauer, J.W. (2003) Development of spliceosome-mediated RNA trans-splicing (SMaRT) for the correction of inherited skin diseases. Exp. Dermatol., 12, 37-46. (Pubitemid 36934688)
    • (2003) Experimental Dermatology , vol.12 , Issue.1 , pp. 37-46
    • Dallinger, G.1    Puttaraju, M.2    Mitchell, L.G.3    Yancey, K.B.4    Yee, C.5    Klausegger, A.6    Hintner, H.7    Bauer, J.W.8


* 이 정보는 Elsevier사의 SCOPUS DB에서 KISTI가 분석하여 추출한 것입니다.