메뉴 건너뛰기




Volumn 35, Issue 6, 2013, Pages 419-423

International cooperation for the cure and prevention of severe hemoglobinopathies

Author keywords

bone marrow transplantation; international cooperation; thalassemia

Indexed keywords

ACUTE LYMPHOBLASTIC LEUKEMIA; ALPHA THALASSEMIA; APLASTIC ANEMIA; BONE MARROW TRANSPLANTATION; CONTROLLED STUDY; DEVELOPING COUNTRY; DISEASE FREE SURVIVAL; DISEASE SEVERITY; FANCONI ANEMIA; FEASIBILITY STUDY; FETUS HYDROPS; HEALTH CARE COST; HEALTH CARE ORGANIZATION; HEALTH SERVICE; HEMOGLOBINOPATHY; HISTOCOMPATIBILITY; HUMAN; INDIA; INTERNATIONAL COOPERATION; LOW RISK POPULATION; MAJOR CLINICAL STUDY; MEDICAL SOCIETY; OUTCOME ASSESSMENT; PAKISTAN; PRIORITY JOURNAL; PUBLIC-PRIVATE PARTNERSHIP; REVIEW; SICKLE CELL ANEMIA; SICKLE CELL BETA THALASSEMIA; THALASSEMIA; THALASSEMIA MAJOR;

EID: 84881480318     PISSN: 10774114     EISSN: 15363678     Source Type: Journal    
DOI: 10.1097/MPH.0b013e31829cd920     Document Type: Review
Times cited : (18)

References (34)
  • 2
    • 77953952024 scopus 로고    scopus 로고
    • The inherited diseases of hemoglobin are an emerging global health burden
    • Weatherall DJ. The inherited diseases of hemoglobin are an emerging global health burden. Blood. 2010;115:4331-4336.
    • (2010) Blood , vol.115 , pp. 4331-4336
    • Weatherall, D.J.1
  • 3
    • 0037057643 scopus 로고    scopus 로고
    • Screening extended families for genetic hemoglobin disorders in Pakistan
    • Ahmed S, Saleem M, Modell B, et al. Screening extended families for genetic hemoglobin disorders in Pakistan. N Engl J Med. 2002;347:1162-1168.
    • (2002) N Engl J Med , vol.347 , pp. 1162-1168
    • Ahmed, S.1    Saleem, M.2    Modell, B.3
  • 4
    • 24944465060 scopus 로고    scopus 로고
    • Rachmilewitz E. b-Thalassemia
    • Rund D, Rachmilewitz E. b-Thalassemia. N Engl J Med. 2005; 353:1135-1146.
    • (2005) N Engl J Med , vol.353 , pp. 1135-1146
    • Rund, D.1
  • 5
    • 84881481529 scopus 로고    scopus 로고
    • Available at Accessed June 11, 2013
    • Worldmapper: population under 15 years. Available at: http://sasi.group.shef.ac.uk/worldmapper/display.php?selected=5. Accessed June 11, 2013.
    • Worldmapper: Population under 15 Years
  • 6
    • 80053364446 scopus 로고    scopus 로고
    • How i treat thalassemia
    • Rachmilewitz EA, Giardina PJ. How I treat thalassemia. Blood. 2011;118:3479-3488.
    • (2011) Blood , vol.118 , pp. 3479-3488
    • Rachmilewitz, E.A.1    Giardina, P.J.2
  • 7
    • 77958177906 scopus 로고    scopus 로고
    • Management of chronic viral hepatitis in patients with thalassemia: Recommendations from an international panel
    • Di Marco V, Capra M, Angelucci E, et al. Management of chronic viral hepatitis in patients with thalassemia: recommendations from an international panel. Blood. 2010;116: 2875-2883.
    • (2010) Blood , vol.116 , pp. 2875-2883
    • Di Marco, V.1    Capra, M.2    Angelucci, E.3
  • 8
    • 84871903577 scopus 로고    scopus 로고
    • Hematopoietic cell transplantation for thalassemia: A global perspective
    • Mehta PA, Faulkner LB. Hematopoietic cell transplantation for thalassemia: a global perspective. Biol Blood Marrow Transplant. 2013;19(suppl):S70-S73.
    • (2013) Biol Blood Marrow Transplant , vol.19 , Issue.SUPPL.
    • Mehta, P.A.1    Faulkner, L.B.2
  • 10
    • 52149111377 scopus 로고    scopus 로고
    • Quality of life in patients with transfusion-dependent thalassemia after hematopoietic SCT
    • Cheuk DKL, Mok ASP, Lee ACW, et al. Quality of life in patients with transfusion-dependent thalassemia after hematopoietic SCT. Bone Marrow Transplant. 2008;42:319-327.
    • (2008) Bone Marrow Transplant , vol.42 , pp. 319-327
    • Cheuk, D.K.L.1    Mok, A.S.P.2    Lee, A.C.W.3
  • 11
    • 77955333676 scopus 로고    scopus 로고
    • A costutility and budget impact analysis of allogeneic hematopoietic stem cell transplantation for severe thalassemic patients in Thailand
    • Leelahavarong P, Chaikledkaew U, Hongeng S, et al. A costutility and budget impact analysis of allogeneic hematopoietic stem cell transplantation for severe thalassemic patients in Thailand. BMC Health Serv Res. 2010;10:209-221.
    • (2010) BMC Health Serv Res , vol.10 , pp. 209-221
    • Leelahavarong, P.1    Chaikledkaew, U.2    Hongeng, S.3
  • 13
    • 79956038028 scopus 로고    scopus 로고
    • Prospective assessment of health-related quality of life in pediatric patients with betathalassemia following hematopoietic stem cell transplantation
    • Caocci G, Efficace F, Ciotti F, et al. Prospective assessment of health-related quality of life in pediatric patients with betathalassemia following hematopoietic stem cell transplantation. Biol Blood Marrow Transplant. 2011;17:861-866.
    • (2011) Biol Blood Marrow Transplant , vol.17 , pp. 861-866
    • Caocci, G.1    Efficace, F.2    Ciotti, F.3
  • 14
    • 80051666676 scopus 로고    scopus 로고
    • Umbilical cord blood transplantation for children with thalassemia and sickle cell disease
    • Ruggeri A, Eapen M, Scaravadou A, et al. Umbilical cord blood transplantation for children with thalassemia and sickle cell disease. Biol Blood Marrow Transplant. 2011;17:1375-1382.
    • (2011) Biol Blood Marrow Transplant , vol.17 , pp. 1375-1382
    • Ruggeri, A.1    Eapen, M.2    Scaravadou, A.3
  • 15
    • 84876089274 scopus 로고    scopus 로고
    • T-cell-replete HLAhaploidentical hematopoietic transplantation for hematologic malignancies using post-transplantation cyclophosphamide results in outcomes equivalent to those of contemporaneous HLA-matched related and unrelated donor transplantation
    • Bashey A, Zhang Xu, Sizemore CA, et al. T-cell-replete HLAhaploidentical hematopoietic transplantation for hematologic malignancies using post-transplantation cyclophosphamide results in outcomes equivalent to those of contemporaneous HLA-matched related and unrelated donor transplantation. J Clin Oncol. 2013;31:1310-1316.
    • (2013) J Clin Oncol , vol.31 , pp. 1310-1316
    • Bashey, A.1    Xu, Z.2    Sizemore, C.A.3
  • 16
    • 77949532641 scopus 로고    scopus 로고
    • Purified T-depleted CD34+ peripheral blood and bone marrow cell transplantation from haploidentical mother to child with thalassemia
    • Sodani P, Isgrò A, Gaziev J, et al. Purified T-depleted, CD34+ peripheral blood and bone marrow cell transplantation from haploidentical mother to child with thalassemia. Blood. 2010;115:1296-1302.
    • (2010) Blood , vol.115 , pp. 1296-1302
    • Sodani, P.1    Isgrò, A.2    Gaziev, J.3
  • 17
    • 84869813639 scopus 로고    scopus 로고
    • HLA-haploidentical bone marrow transplantation with post-transplant cyclophosphamide expands the donor pool for patients with sickle cell disease
    • Bolañ os-Meade J, Fuchs EJ, Luznik L, et al. HLA-haploidentical bone marrow transplantation with post-transplant cyclophosphamide expands the donor pool for patients with sickle cell disease. Blood. 2012;120:4285-4291.
    • (2012) Blood , vol.120 , pp. 4285-4291
    • Bolaños-Meade, J.1    Fuchs, E.J.2    Luznik, L.3
  • 18
    • 84871907955 scopus 로고    scopus 로고
    • Hematopoietic stem cell transplantation in thalassemia and sickle cell disease: Experience of Mediterranean Institute of Hematology in a multiethnic population
    • Marziali M, Isgrò A, Gaziev J, et al. Hematopoietic stem cell transplantation in thalassemia and sickle cell disease: experience of Mediterranean Institute of Hematology in a multiethnic population. Mediterr J Hematol Infect Dis. 2009;1: e2009027.
    • (2009) Mediterr J Hematol Infect Dis , vol.1
    • Marziali, M.1    Isgrò, A.2    Gaziev, J.3
  • 20
    • 80051562984 scopus 로고    scopus 로고
    • Allogeneic hematopoietic stem cell transplant for sickle cell disease: The time is now
    • Hsieh MM, Fitzhugh CD, Tisdale JF. Allogeneic hematopoietic stem cell transplant for sickle cell disease: the time is now. Blood. 2011;118:1197-1207.
    • (2011) Blood , vol.118 , pp. 1197-1207
    • Hsieh, M.M.1    Fitzhugh, C.D.2    Tisdale, J.F.3
  • 22
    • 79959830632 scopus 로고    scopus 로고
    • Efficacy of hydroxyurea in providing transfusion independence in b-thalassemia
    • Ansari SH, Shamsi TS, Ashraf M, et al. Efficacy of hydroxyurea in providing transfusion independence in b-thalassemia. J Pediatr Hematol Oncol. 2011;33:339-343.
    • (2011) J Pediatr Hematol Oncol , vol.33 , pp. 339-343
    • Ansari, S.H.1    Shamsi, T.S.2    Ashraf, M.3
  • 23
    • 69149106268 scopus 로고    scopus 로고
    • Hydroxyurea therapy in 49 patients with major beta-thalassemia
    • Zamani F, Shakeri R, Eslami S-M, et al. Hydroxyurea therapy in 49 patients with major beta-thalassemia. Arch Iran Med. 2009;12:295-297.
    • (2009) Arch Iran Med , vol.12 , pp. 295-297
    • Zamani, F.1    Shakeri, R.2    Eslami, S.-M.3
  • 24
    • 0042237715 scopus 로고    scopus 로고
    • Hydroxyurea can eliminate transfusion requirements in children with severe betathalassemia
    • Bradai M, Abad MT, Pissard S, et al. Hydroxyurea can eliminate transfusion requirements in children with severe betathalassemia. Blood. 2003;102:1529-1530.
    • (2003) Blood , vol.102 , pp. 1529-1530
    • Bradai, M.1    Abad, M.T.2    Pissard, S.3
  • 25
    • 13344259315 scopus 로고    scopus 로고
    • Hydroxyurea increases hemoglobin F levels and improves the effectiveness of erythropoiesis in beta-thalassemia/hemoglobin e disease
    • Fucharoen S, Siritanaratkul N, Winichagoon P, et al. Hydroxyurea increases hemoglobin F levels and improves the effectiveness of erythropoiesis in beta-thalassemia/hemoglobin E disease. Blood. 1996;87:887-892.
    • (1996) Blood , vol.87 , pp. 887-892
    • Fucharoen, S.1    Siritanaratkul, N.2    Winichagoon, P.3
  • 26
    • 33645961286 scopus 로고    scopus 로고
    • Infections in children undergoing allogeneic bone marrow transplantation in India
    • George B, Mathews V, Viswabandya A, et al. Infections in children undergoing allogeneic bone marrow transplantation in India. Pediatr Transplant. 2006;10:48-54.
    • (2006) Pediatr Transplant , vol.10 , pp. 48-54
    • George, B.1    Mathews, V.2    Viswabandya, A.3
  • 27
    • 59549106857 scopus 로고    scopus 로고
    • Allogeneic hematopoietic SCT performed in non-HEPA filter rooms: Initial experience from a single center in India
    • Kumar R, Naithani R, Mishra P, et al. Allogeneic hematopoietic SCT performed in non-HEPA filter rooms: initial experience from a single center in India. BoneMarrow Transplant. 2009;43:115-119.
    • (2009) BoneMarrow Transplant , vol.43 , pp. 115-119
    • Kumar, R.1    Naithani, R.2    Mishra, P.3
  • 28
    • 69849102119 scopus 로고    scopus 로고
    • Guidelines for preventing infectious complications among hematopoietic cell transplantation recipients: A global perspective
    • Tomblyn M, Chiller T, Einsele H, et al. Guidelines for preventing infectious complications among hematopoietic cell transplantation recipients: a global perspective. Biol Blood Marrow Transplant. 2009;15:1143-1238.
    • (2009) Biol Blood Marrow Transplant , vol.15 , pp. 1143-1238
    • Tomblyn, M.1    Chiller, T.2    Einsele, H.3
  • 29
    • 0037114629 scopus 로고    scopus 로고
    • Home care during the pancytopenic phase after allogeneic hematopoietic stem cell transplantation is advantageous compared with hospital care
    • Svahn B-M, Remberger M, Myrbäck K-E, et al. Home care during the pancytopenic phase after allogeneic hematopoietic stem cell transplantation is advantageous compared with hospital care. Blood. 2002;100:4317-4324.
    • (2002) Blood , vol.100 , pp. 4317-4324
    • Svahn, B.-M.1    Remberger, M.2    Myrbäck, K.-E.3
  • 30
    • 77949424430 scopus 로고    scopus 로고
    • Outpatient myeloablative allo-SCT: A comprehensive approach yields decreased hospital utilization and low TRM
    • Solomon SR, Matthews RH, Barreras AM, et al. Outpatient myeloablative allo-SCT: a comprehensive approach yields decreased hospital utilization and low TRM. Bone Marrow Transplant. 2010;45:468-475.
    • (2010) Bone Marrow Transplant , vol.45 , pp. 468-475
    • Solomon, S.R.1    Matthews, R.H.2    Barreras, A.M.3
  • 31
    • 27244454795 scopus 로고    scopus 로고
    • The metrics of the physician brain drain
    • Mullan F. The metrics of the physician brain drain. N Engl J Med. 2005;353:1810-1818.
    • (2005) N Engl J Med , vol.353 , pp. 1810-1818
    • Mullan, F.1
  • 32
    • 0032512307 scopus 로고    scopus 로고
    • North-South twinning in paediatric haemato-oncology: The la Mascota programme
    • Masera G, Baez F, Biondi A, et al. North-South twinning in paediatric haemato-oncology: the La Mascota programme, Nicaragua. Lancet. 1998;352:1923-1926.
    • (1998) Nicaragua. Lancet , vol.352 , pp. 1923-1926
    • Masera, G.1    Baez, F.2    Biondi, A.3
  • 33
    • 84881475157 scopus 로고    scopus 로고
    • The la mascota twinning program between monza (Italy) and managua (Nicaragua): A 23-year experience
    • Reaman GH , Smith, FO, eds Available at
    • Masera G. The "La Mascota" Twinning Program Between Monza (Italy) and Managua (Nicaragua): A 23-year Experience. In: Reaman GH , Smith, FO, eds. Childhood Leukemia: A Practical Handbook. 2011: 309-313. Available at: http://books.google.it/books?id=7PguSZ1LLq4C&printsec=front cover.
    • (2011) Childhood Leukemia: A Practical Handbook , pp. 309-313
    • Masera, G.1
  • 34
    • 84881475680 scopus 로고    scopus 로고
    • International standards for cellular therapy product collection
    • FACT-JACIE FACT-JACIE Available at
    • McGrath E, FACT-JACIE. International Standards for Cellular Therapy Product Collection, Processing and Administration. 4th ed. FACT-JACIE. Available at: http://www.jacie.org/document-centre/Standards%204.1%20ed.pdf?attredirects= 0; 2012.
    • (2012) Processing and Administration. 4th Ed
    • McGrath, E.1


* 이 정보는 Elsevier사의 SCOPUS DB에서 KISTI가 분석하여 추출한 것입니다.