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Volumn 118, Issue 5, 2011, Pages 1197-1207

Allogeneic hematopoietic stem cell transplantation for sickle cell disease: The time is now

Author keywords

[No Author keywords available]

Indexed keywords

ALEMTUZUMAB; BUSULFAN; CYCLOPHOSPHAMIDE; CYCLOSPORIN A; FLUDARABINE; GRANULOCYTE COLONY STIMULATING FACTOR; HYDROXYUREA; MELPHALAN; METHOTREXATE; MYCOPHENOLIC ACID 2 MORPHOLINOETHYL ESTER; RAPAMYCIN; THIOTEPA; THYMOCYTE ANTIBODY; VIRUS VECTOR;

EID: 80051562984     PISSN: 00064971     EISSN: 15280020     Source Type: Journal    
DOI: 10.1182/blood-2011-01-332510     Document Type: Review
Times cited : (113)

References (96)
  • 1
    • 0029025475 scopus 로고
    • Effect of hydroxyurea on the frequency of painful crises in sickle cell anemia. Investigators of the Multicenter Study of Hydroxyurea in Sickle Cell Anemia
    • see comments
    • Charache S, Terrin ML, Moore RD, et al. Effect of hydroxyurea on the frequency of painful crises in sickle cell anemia. Investigators of the Multicenter Study of Hydroxyurea in Sickle Cell Anemia [see comments]. N Engl J Med. 1995;332(20):1317-1322.
    • (1995) N Engl J Med , vol.332 , Issue.20 , pp. 1317-1322
    • Charache, S.1    Terrin, M.L.2    Moore, R.D.3
  • 4
    • 0034307369 scopus 로고    scopus 로고
    • Financial analysis of chronic transfusion for stroke prevention in sickle cell disease
    • Wayne AS, Schoenike SE, Pegelow CH. Financial analysis of chronic transfusion for stroke prevention in sickle cell disease. Blood. 2000;96(7):2369-2372.
    • (2000) Blood , vol.96 , Issue.7 , pp. 2369-2372
    • Wayne, A.S.1    Schoenike, S.E.2    Pegelow, C.H.3
  • 5
    • 79251628870 scopus 로고    scopus 로고
    • Impact of early transcranial Doppler screening and intensive therapy on cerebral vasculopathy outcome in a newborn sickle cell anemia cohort
    • Bernaudin F, Verlhac S, Arnaud C, et al. Impact of early transcranial Doppler screening and intensive therapy on cerebral vasculopathy outcome in a newborn sickle cell anemia cohort. Blood. 2011;117(4):1130-1140.
    • (2011) Blood , vol.117 , Issue.4 , pp. 1130-1140
    • Bernaudin, F.1    Verlhac, S.2    Arnaud, C.3
  • 6
    • 79952158820 scopus 로고    scopus 로고
    • Effect of transfusion therapy on transcranial Doppler ultrasonography velocities in children with sickle cell disease
    • Kwiatkowski JL, Yim E, Miller S, Adams RJ. Effect of transfusion therapy on transcranial Doppler ultrasonography velocities in children with sickle cell disease. Pediatr Blood Cancer. 2011;56(5):777-782.
    • (2011) Pediatr Blood Cancer , vol.56 , Issue.5 , pp. 777-782
    • Kwiatkowski, J.L.1    Yim, E.2    Miller, S.3    Adams, R.J.4
  • 7
    • 78751697297 scopus 로고    scopus 로고
    • Silent cerebral infarcts occur despite regular blood transfusion therapy after first strokes in children with sickle cell disease
    • Jan 20
    • Hulbert ML, McKinstry RC, Lacey JL, et al. Silent cerebral infarcts occur despite regular blood transfusion therapy after first strokes in children with sickle cell disease. Blood. Jan 20;117(3):772-779.
    • Blood , vol.117 , Issue.3 , pp. 772-779
    • Hulbert, M.L.1    McKinstry, R.C.2    Lacey, J.L.3
  • 8
    • 77958552396 scopus 로고    scopus 로고
    • Antibody development in pediatric sickle cell patients undergoing erythrocytapheresis
    • Godfrey GJ, Lockwood W, Kong M, Bertolone S, Raj A. Antibody development in pediatric sickle cell patients undergoing erythrocytapheresis. Pediatr Blood Cancer. 2010;55(6):1134-1137.
    • (2010) Pediatr Blood Cancer , vol.55 , Issue.6 , pp. 1134-1137
    • Godfrey, G.J.1    Lockwood, W.2    Kong, M.3    Bertolone, S.4    Raj, A.5
  • 9
    • 80051563022 scopus 로고    scopus 로고
    • Extended red blood cell antigen matching for transfusions in sickle cell disease: A review of a 14-year experience from a single center
    • published online ahead of print February 18, 2011 doi: 10.1111/j.1537-2995.2010.03045.x
    • Lasalle-Williams M, Nuss R, Le T, et al. Extended red blood cell antigen matching for transfusions in sickle cell disease: a review of a 14-year experience from a single center [published online ahead of print February 18, 2011]. Transfusion. doi: 10.1111/j.1537-2995.2010.03045.x.
    • Transfusion
    • Lasalle-Williams, M.1    Nuss, R.2    Le, T.3
  • 10
    • 77649128081 scopus 로고    scopus 로고
    • HLA alloimmunization is associated with RBC antibodies in multiply transfused patients with sickle cell disease
    • McPherson ME, Anderson AR, Castillejo MI, et al. HLA alloimmunization is associated with RBC antibodies in multiply transfused patients with sickle cell disease. Pediatr Blood Cancer. 2010;54(4):552-558.
    • (2010) Pediatr Blood Cancer , vol.54 , Issue.4 , pp. 552-558
    • McPherson, M.E.1    Anderson, A.R.2    Castillejo, M.I.3
  • 13
    • 74049151134 scopus 로고    scopus 로고
    • Cardiopulmonary complications leading to premature deaths in adult patients with sickle cell disease
    • Fitzhugh CD, Lauder N, Jonassaint JC, et al. Cardiopulmonary complications leading to premature deaths in adult patients with sickle cell disease. Am J Hematol. 2010;85(1):36-40.
    • (2010) Am J Hematol , vol.85 , Issue.1 , pp. 36-40
    • Fitzhugh, C.D.1    Lauder, N.2    Jonassaint, J.C.3
  • 14
    • 27944496081 scopus 로고    scopus 로고
    • Outcome of sickle cell anemia: A 4-decade observational study of 1056 patients
    • DOI 10.1097/01.md.0000189089.45003.52
    • Powars DR, Chan LS, Hiti A, Ramicone E, Johnson C. Outcome of sickle cell anemia: a 4-decade observational study of 1056 patients. Medicine (Baltimore). 2005;84(6):363-376. (Pubitemid 41668935)
    • (2005) Medicine , vol.84 , Issue.6 , pp. 363-376
    • Powars, D.R.1    Chan, L.S.2    Hiti, A.3    Ramicone, E.4    Johnson, C.5
  • 15
    • 10744233940 scopus 로고    scopus 로고
    • Pulmonary hypertension as a risk factor for death in patients with sickle cell disease
    • Gladwin Mt, Sachdev V, Jison ML, et al. Pulmonary hypertension as a risk factor for death in patients with sickle cell disease. N Engl J Med. 2004;350(9):886-895.
    • (2004) N Engl J Med , vol.350 , Issue.9 , pp. 886-895
    • Gladwin, Mt.1    Sachdev, V.2    Jison, M.L.3
  • 16
    • 0025939624 scopus 로고
    • Chronic renal failure in sickle cell disease: Risk factors, clinical course, and mortality
    • Powars DR, Elliott-Mills DD, Chan L, et al. Chronic renal failure in sickle cell disease: risk factors, clinical course, and mortality. Ann Intern Med. 1991;115(8):614-620.
    • (1991) Ann Intern Med , vol.115 , Issue.8 , pp. 614-620
    • Powars, D.R.1    Elliott-Mills, D.D.2    Chan, L.3
  • 17
    • 0023279105 scopus 로고
    • Prognosis of the nephrotic syndrome in sickle glomerulopathy. A retrospective study
    • Bakir AA, Hathiwala SC, Ainis H, et al. Prognosis of the nephrotic syndrome in sickle glomerulopathy. A retrospective study. Am J Nephrol. 1987;7(2):110-115. (Pubitemid 17094643)
    • (1987) American Journal of Nephrology , vol.7 , Issue.2 , pp. 110-115
    • Bakir, A.A.1    Hathiwala, S.C.2    Ainis, H.3
  • 19
    • 22244448421 scopus 로고    scopus 로고
    • Sickle cell hepatopathy: Clinical presentation, treatment, and outcome in pediatric and adult patients
    • DOI 10.1002/pbc.20317
    • Ahn H, Li CS, Wang W. Sickle cell hepatopathy: clinical presentation, treatment, and outcome in pediatric and adult patients. Pediatr Blood Cancer. 2005;45(2):184-190. (Pubitemid 40993585)
    • (2005) Pediatric Blood and Cancer , vol.45 , Issue.2 , pp. 184-190
    • Ahn, H.1    Li, C.-S.2    Wang, W.3
  • 20
    • 0021593369 scopus 로고
    • Bone-marrow transplantation in a patient with sickle-cell anemia
    • Johnson FL, Look AT, Gockerman J, Ruggiero MR, Dalla-Pozza L, Billings FT 3rd. Bone-marrow transplantation in a patient with sickle-cell anemia. N Engl J Med. 1984;311(12):780-783. (Pubitemid 14026230)
    • (1984) New England Journal of Medicine , vol.311 , Issue.12 , pp. 780-783
    • Johnson, F.L.1    Look, A.T.2    Gockerman, J.3
  • 21
    • 0027185471 scopus 로고
    • Bone marrow transplantation in sickle cell disease: The Belgian experience
    • Vermylen C, Cornu G, Ferster A, Ninane J, Sariban E. Bone marrow transplantation in sickle cell disease: the Belgian experience. Bone Marrow Transplant. 1993;12(suppl 1):116-117. (Pubitemid 23231081)
    • (1993) Bone Marrow Transplantation , vol.12 , Issue.SUPPL. 1 , pp. 116-117
    • Vermylen, C.1    Cornu, G.2    Ferster, A.3    Ninane, J.4    Sariban, E.5
  • 23
    • 0028966027 scopus 로고
    • Neurologic complications after allogeneic marrow transplantation for sickle cell anemia
    • see comments
    • Walters MC, Sullivan KM, Bernaudin F, et al. Neurologic complications after allogeneic marrow transplantation for sickle cell anemia [see comments]. Blood. 1995;85(4):879-884.
    • (1995) Blood , vol.85 , Issue.4 , pp. 879-884
    • Walters, M.C.1    Sullivan, K.M.2    Bernaudin, F.3
  • 29
    • 3042753988 scopus 로고    scopus 로고
    • Reduced intensity haemopoietic stem-cell transplantation for treatment of non-malignant diseases in children
    • DOI 10.1016/S0140-6736(04)16628-2, PII S0140673604166282
    • Jacobsohn DA, Duerst R, Tse W, Kletzel M. Reduced intensity haemopoietic stem-cell transplantation for treatment of non-malignant diseases in children. Lancet. 2004;364(9429):156-162. (Pubitemid 38891687)
    • (2004) Lancet , vol.364 , Issue.9429 , pp. 156-162
    • Jacobsohn, D.A.1    Duerst, R.2    Tse, W.3    Kletzel, M.4
  • 30
    • 35648951105 scopus 로고    scopus 로고
    • Has stem cell transplantation come of age in the treatment of sickle cell disease?
    • DOI 10.1038/sj.bmt.1705779, PII 1705779
    • Shenoy S. Has stem cell transplantation come of age in the treatment of sickle cell disease? Bone Marrow Transplant. 2007;40(9):813-821. (Pubitemid 350020314)
    • (2007) Bone Marrow Transplantation , vol.40 , Issue.9 , pp. 813-821
    • Shenoy, S.1
  • 31
    • 70350764819 scopus 로고    scopus 로고
    • Defining the intensity of conditioning regimens: Working definitions
    • Bacigalupo A, Ballen K, Rizzo D, et al. Defining the intensity of conditioning regimens: working definitions. Biol Blood Marrow Transplant. 2009;15(12):1628-1633.
    • (2009) Biol Blood Marrow Transplant , vol.15 , Issue.12 , pp. 1628-1633
    • Bacigalupo, A.1    Ballen, K.2    Rizzo, D.3
  • 32
    • 0034648702 scopus 로고    scopus 로고
    • Regression of metastatic renal-cell carcinoma after non-myeloablative allogeneic peripheral-blood stemcell transplantation
    • Childs R, Chernoff A, Contentin N, et al. Regression of metastatic renal-cell carcinoma after non-myeloablative allogeneic peripheral-blood stemcell transplantation. N Engl J Med. 2000;343(11):750-758.
    • (2000) N Engl J Med , vol.343 , Issue.11 , pp. 750-758
    • Childs, R.1    Chernoff, A.2    Contentin, N.3
  • 33
    • 33645454939 scopus 로고    scopus 로고
    • Overcoming graft rejection in heavily transfused and allo-immunised patients with bone marrow failure syndromes using fludarabine-based haematopoietic cell transplantation
    • Srinivasan R, Takahashi Y, McCoy JP, et al. Overcoming graft rejection in heavily transfused and allo-immunised patients with bone marrow failure syndromes using fludarabine-based haematopoietic cell transplantation. Br J Haematol. 2006;133(3):305-314.
    • (2006) Br J Haematol , vol.133 , Issue.3 , pp. 305-314
    • Srinivasan, R.1    Takahashi, Y.2    McCoy, J.P.3
  • 35
    • 0033104824 scopus 로고    scopus 로고
    • Inhibition of cell cycle progression by rapamycin induces T cell clonal anergy even in the presence of costimulation
    • Powell JD, Lerner CG, Schwartz RH. Inhibition of cell cycle progression by rapamycin induces T cell clonal anergy even in the presence of costimulation. J Immunol. 1999;162(5):2775-2784. (Pubitemid 29309302)
    • (1999) Journal of Immunology , vol.162 , Issue.5 , pp. 2775-2784
    • Powell, J.D.1    Lerner, C.G.2    Schwartz, R.H.3
  • 36
    • 29344456390 scopus 로고    scopus 로고
    • Low-dose radiation plus rapamycin promotes long-term bone marrow chimerism
    • DOI 10.1097/01.tp.0000185299.72295.90
    • Powell JD, Fitzhugh C, Kang EM, Hsieh M, Schwartz RH, Tisdale JF. Low-dose radiation plus rapamycin promotes long-term bone marrow chimerism. Transplantation. 2005;80(11):1541-1545. (Pubitemid 43005862)
    • (2005) Transplantation , vol.80 , Issue.11 , pp. 1541-1545
    • Powell, J.D.1    Fitzhugh, C.2    Kang, E.M.3    Hsieh, M.4    Schwartz, R.H.5    Tisdale, J.F.6
  • 37
    • 0032495656 scopus 로고    scopus 로고
    • Granulocytosis causing sickle-cell crisis
    • Abboud M, Laver J, Blau CA. Granulocytosis causing sickle-cell crisis [letter]. Lancet. 1998;351(9107):959. (Pubitemid 28138477)
    • (1998) Lancet , vol.351 , Issue.9107 , pp. 959
    • Abboud, M.1    Laver, J.2    Blau, C.A.3
  • 38
    • 0035874493 scopus 로고    scopus 로고
    • Fatal sickle cell crisis after granulocyte colony-stimulating factor administration
    • Adler BK, Salzman DE, Carabasi MH, Vaughan WP, Reddy VV, Prchal JT. Fatal sickle cell crisis after granulocyte colony-stimulating factor administration. Blood. 2001;97(10):3313-3314.
    • (2001) Blood , vol.97 , Issue.10 , pp. 3313-3314
    • Adler, B.K.1    Salzman, D.E.2    Carabasi, M.H.3    Vaughan, W.P.4    Reddy, V.V.5    Prchal, J.T.6
  • 39
    • 0035878007 scopus 로고    scopus 로고
    • Granulocyte colony-stimulating factorinduced sickle cell crisis and multiorgan dysfunction in a patient with compound heterozygous sickle cell/beta+ thalassemia
    • Grigg AP. Granulocyte colony-stimulating factorinduced sickle cell crisis and multiorgan dysfunction in a patient with compound heterozygous sickle cell/beta+ thalassemia. Blood. 2001;97(12):3998-3999.
    • (2001) Blood , vol.97 , Issue.12 , pp. 3998-3999
    • Grigg, A.P.1
  • 40
    • 68049130981 scopus 로고    scopus 로고
    • Granulocyte colony-stimulating factor (G-CSF) administration in individuals with sickle cell disease: Time for a moratorium?
    • Fitzhugh CD, Hsieh MM, Bolan CD, Saenz C, Tisdale JF. Granulocyte colony-stimulating factor (G-CSF) administration in individuals with sickle cell disease: time for a moratorium? Cytotherapy. 2009;11(4):464-471.
    • (2009) Cytotherapy , vol.11 , Issue.4 , pp. 464-471
    • Fitzhugh, C.D.1    Hsieh, M.M.2    Bolan, C.D.3    Saenz, C.4    Tisdale, J.F.5
  • 41
    • 0017056967 scopus 로고
    • Freezing and deglycerolizing sickle trait red blood cells
    • Meryman HT, Hornblower M. Freezing and deglycerolizing sickle-trait red blood cells. Transfusion. 1976;16(6):627-632. (Pubitemid 8027823)
    • (1976) Transfusion , vol.16 , Issue.6 , pp. 627-632
    • Meryman, H.T.1    Hornblower, M.2
  • 42
    • 0027931352 scopus 로고
    • White cell reduction in blood from donors with sickle cell trait
    • letter
    • Bodensteiner D. White cell reduction in blood from donors with sickle cell trait [letter]. Transfusion. 1994;34(1):84.
    • (1994) Transfusion , vol.34 , Issue.1 , pp. 84
    • Bodensteiner, D.1
  • 43
    • 0021246762 scopus 로고
    • Transfusion of frozen erythrocytes from a donor with sickle trait
    • Kelleher JF Jr, Luban NL. Transfusion of frozen erythrocytes from a donor with sickle trait. Transfusion. 1984;24(2):167-168. (Pubitemid 14135428)
    • (1984) Transfusion , vol.24 , Issue.2 , pp. 167-168
    • Kelleher Jr., J.F.1    Luban, N.L.C.2
  • 45
    • 13244269889 scopus 로고    scopus 로고
    • Hematopoietic stem cell transplantation for multiply transfused patients with sickle cell disease and thalassemia after low-dose total body irradiation, fludarabine, and rabbit anti-thymocyte globulin
    • DOI 10.1038/sj.bmt.1704745
    • Horan JT, Liesveld JL, Fenton P, Blumberg N, Walters MC. Hematopoietic stem cell transplantation for multiply transfused patients with sicklecell disease and thalassemia after low-dose total body irradiation, fludarabine, and rabbit anti-thymocyte globulin. Bone Marrow Transplant. 2005;35(2):171-177. (Pubitemid 40185933)
    • (2005) Bone Marrow Transplantation , vol.35 , Issue.2 , pp. 171-177
    • Horan, J.T.1    Liesveld, J.L.2    Fenton, P.3    Blumberg, N.4    Walters, M.C.5
  • 46
    • 0034307366 scopus 로고    scopus 로고
    • In vivo CAMPATH-1H prevents graft-versus-host disease following nonmyeloablative stem cell transplantation
    • Kottaridis PD, Milligan DW, Chopra R, et al. In vivo CAMPATH-1H prevents graft-versus-host disease following nonmyeloablative stem cell transplantation. Blood. 2000;96(7):2419-2425.
    • (2000) Blood , vol.96 , Issue.7 , pp. 2419-2425
    • Kottaridis, P.D.1    Milligan, D.W.2    Chopra, R.3
  • 48
    • 71849118976 scopus 로고    scopus 로고
    • Allogeneic hematopoietic stem-cell transplantation for sickle cell disease
    • Hsieh MM, Kang EM, Fitzhugh CD, et al. Allogeneic hematopoietic stem-cell transplantation for sickle cell disease. N Engl J Med. 2009;361(24): 2309-2317.
    • (2009) N Engl J Med , vol.361 , Issue.24 , pp. 2309-2317
    • Hsieh, M.M.1    Kang, E.M.2    Fitzhugh, C.D.3
  • 49
    • 38949124765 scopus 로고    scopus 로고
    • Late effects of myeloablative bone marrow transplantation (BMT) in sickle cell disease (SCD)
    • author reply 1744
    • Fitzhugh CD, Perl S, Hsieh MM. Late effects of myeloablative bone marrow transplantation (BMT) in sickle cell disease (SCD). Blood. 2008;111(3):1742- 1743; author reply 1744.
    • (2008) Blood , vol.111 , Issue.3 , pp. 1742-1743
    • Fitzhugh, C.D.1    Perl, S.2    Hsieh, M.M.3
  • 50
    • 53749086728 scopus 로고    scopus 로고
    • Stable long-term donor engraftment following reduced-intensity hematopoietic cell transplantation for sickle cell disease
    • Krishnamurti L, Kharbanda S, Biernacki MA, et al. Stable long-term donor engraftment following reduced-intensity hematopoietic cell transplantation for sickle cell disease. Biol Blood Marrow Transplant. 2008;14(11):1270-1278.
    • (2008) Biol Blood Marrow Transplant , vol.14 , Issue.11 , pp. 1270-1278
    • Krishnamurti, L.1    Kharbanda, S.2    Biernacki, M.A.3
  • 52
    • 59449098985 scopus 로고    scopus 로고
    • Gene therapy for immunodeficiency due to adenosine deaminase deficiency
    • Aiuti A, Cattaneo F, Galimberti S, et al. Gene therapy for immunodeficiency due to adenosine deaminase deficiency. N Engl J Med. 2009;360(5):447-458.
    • (2009) N Engl J Med , vol.360 , Issue.5 , pp. 447-458
    • Aiuti, A.1    Cattaneo, F.2    Galimberti, S.3
  • 53
    • 77954833516 scopus 로고    scopus 로고
    • Efficacy of gene therapy for X-linked severe combined immunodeficiency
    • Hacein-Bey-Abina S, Hauer J, Lim A, et al. Efficacy of gene therapy for X-linked severe combined immunodeficiency. N Engl J Med. 2010;363(4):355-364.
    • (2010) N Engl J Med , vol.363 , Issue.4 , pp. 355-364
    • Hacein-Bey-Abina, S.1    Hauer, J.2    Lim, A.3
  • 54
    • 76249131912 scopus 로고    scopus 로고
    • Genomic instability and myelodysplasia with monosomy 7 consequent to EVI1 activation after gene therapy for chronic granulomatous disease
    • Stein S, Ott MG, Schultze-Strasser S, et al. Genomic instability and myelodysplasia with monosomy 7 consequent to EVI1 activation after gene therapy for chronic granulomatous disease. Nat Med. 2010;16(2):198-204.
    • (2010) Nat Med , vol.16 , Issue.2 , pp. 198-204
    • Stein, S.1    Ott, M.G.2    Schultze-Strasser, S.3
  • 55
    • 0035874519 scopus 로고    scopus 로고
    • Functional requirements for phenotypic correction of murine beta-thalassemia: Implications for human gene therapy
    • Persons DA, Allay ER, Sabatino DE, Kelly P, Bodine DM, Nienhuis AW. Functional requirements for phenotypic correction of murine beta-thalassemia: implications for human gene therapy. Blood. 2001;97(10):3275-3282.
    • (2001) Blood , vol.97 , Issue.10 , pp. 3275-3282
    • Persons, D.A.1    Allay, E.R.2    Sabatino, D.E.3    Kelly, P.4    Bodine, D.M.5    Nienhuis, A.W.6
  • 56
    • 78650991791 scopus 로고    scopus 로고
    • Quantitatively different red cells/nucleated cell chimerism in patients with long-term persistant hematopoietic mixed chimerism after bone marrow transplantation for thalassemia major or sickle cell disease
    • Andreani M, Testi M, Gaziev J, et al. Quantitatively different red cells/nucleated cell chimerism in patients with long-term persistant hematopoietic mixed chimerism after bone marrow transplantation for thalassemia major or sickle cell disease. Haematologica. 2011;96(1):128-133.
    • (2011) Haematologica , vol.96 , Issue.1 , pp. 128-133
    • Andreani, M.1    Testi, M.2    Gaziev, J.3
  • 62
    • 0026040687 scopus 로고
    • Bone marrow transplantation for sickle cell disease.Astudy of parents' decisions
    • Kodish E, Lantos J, Stocking C, Singer PA, Siegler M, Johnson FL. Bone marrow transplantation for sickle cell disease.Astudy of parents' decisions. N Engl J Med. 1991;325(19):1349-1353.
    • (1991) N Engl J Med , vol.325 , Issue.19 , pp. 1349-1353
    • Kodish, E.1    Lantos, J.2    Stocking, C.3    Singer, P.A.4    Siegler, M.5    Johnson, F.L.6
  • 64
    • 0030051313 scopus 로고    scopus 로고
    • Persistence of fetal hemoglobin production after successful transplantation of cord blood stem cells in a patient with sickle cell anemia
    • DOI 10.1016/S0022-3476(96)70398-0
    • Brichard B, Vermylen C, Ninane J, Cornu G. Persistence of fetal hemoglobin production after successful transplantation of cord blood stem cells in a patient with sickle cell anemia [see comments]. J Pediatr. 1996;128(2):241-243. (Pubitemid 26065950)
    • (1996) Journal of Pediatrics , vol.128 , Issue.2 , pp. 241-243
    • Brichard, B.1    Vermylen, C.2    Ninane, J.3    Cornu, G.4
  • 66
    • 0034268110 scopus 로고    scopus 로고
    • Successful cord blood transplantation for sickle cell anemia from a sibling who is human leukocyte Antigen-Identical: Implications for comprehensive care
    • DOI 10.1097/00043426-200009000-00010
    • Gore L, Lane PA, Quinones RR, Giller RH. Successful cord blood transplantation for sickle cell anemia from a sibling who is human leukocyte antigen-identical: implications for comprehensive care. J Pediatr Hematol Oncol. 2000;22(5):437-440. (Pubitemid 33599752)
    • (2001) Journal of Pediatric Hematology/Oncology , vol.22 , Issue.5 , pp. 437-440
    • Gore, L.1    Lane, P.A.2    Quinones, R.R.3    Giller, R.H.4
  • 70
    • 33845712655 scopus 로고    scopus 로고
    • Transplantation of a child with sickle cell anemia with an unrelated cord blood unit after reduced intensity conditioning
    • DOI 10.1097/MPH.0b013e31802d3e53, PII 0004342620061200000015
    • Mazur M, Kurtzberg J, Halperin E, Ciocci G, Szabolcs P. Transplantation of a child with sickle cell anemia with an unrelated cord blood unit after reduced intensity conditioning. J Pediatr Hematol Oncol. 2006;28(12):840-844. (Pubitemid 44967683)
    • (2006) Journal of Pediatric Hematology/Oncology , vol.28 , Issue.12 , pp. 840-844
    • Mazur, M.1    Kurtzberg, J.2    Halperin, E.3    Ciocci, G.4    Szabolcs, P.5
  • 71
    • 77955014034 scopus 로고    scopus 로고
    • Successful unrelated donor cord blood transplantation for adult sickle cell disease and Hodgkin lymphoma
    • Sauter C, Rausen AR, Barker JN. Successful unrelated donor cord blood transplantation for adult sickle cell disease and Hodgkin lymphoma. Bone Marrow Transplant. 2010;45(7):1252.
    • (2010) Bone Marrow Transplant , vol.45 , Issue.7 , pp. 1252
    • Sauter, C.1    Rausen, A.R.2    Barker, J.N.3
  • 72
    • 0038743168 scopus 로고    scopus 로고
    • Availability of unrelated donors for hematopoietic stem cell transplantation for hemoglobinopathies
    • DOI 10.1038/sj.bmt.1703887
    • Krishnamurti L, Abel S, Maiers M, Flesch S. Availability of unrelated donors for hematopoietic stem cell transplantation for hemoglobinopathies. Bone Marrow Transplant. 2003;31(7):547-550. (Pubitemid 36546831)
    • (2003) Bone Marrow Transplantation , vol.31 , Issue.7 , pp. 547-550
    • Krishnamurti, L.1    Abel, S.2    Maiers, M.3    Flesch, S.4
  • 73
    • 33644847688 scopus 로고    scopus 로고
    • Identification of unrelated cord blood units for hematopoietic stem cell transplantation in children with sickle cell disease
    • PII 0004342620060100000006
    • Adamkiewicz TV, Boyer MW, Bray R, Haight A, Yeager AM. Identification of unrelated cord blood units for hematopoietic stem cell transplantation in children with sickle cell disease. J Pediatr Hematol Oncol. 2006;28(1):29-32. (Pubitemid 43361615)
    • (2006) Journal of Pediatric Hematology/Oncology , vol.28 , Issue.1 , pp. 29-32
    • Adamkiewicz, T.V.1    Boyer, M.W.2    Bray, R.3    Haight, A.4    Yeager, A.M.5
  • 75
    • 47249083472 scopus 로고    scopus 로고
    • Paucity of HLA-Identical Unrelated Donors for African-Americans with Hematologic Malignancies: The Need for New Donor Options
    • DOI 10.1016/j.bbmt.2008.06.005, PII S1083879108002486
    • Dew A, Collins D, Artz A, et al. Paucity of HLAidentical unrelated donors for African-Americans with hematologic malignancies: the need for new donor options. Biol Blood Marrow Transplant. 2008;14(8):938-941. (Pubitemid 351985032)
    • (2008) Biology of Blood and Marrow Transplantation , vol.14 , Issue.8 , pp. 938-941
    • Dew, A.1    Collins, D.2    Artz, A.3    Rich, E.4    Stock, W.5    Swanson, K.6    Van Besien, K.7
  • 78
    • 0025011798 scopus 로고
    • Effect of HLA incompatibility on graft-versus-host disease, relapse, and survival after marrow transplantation for patients with leukemia or lymphoma
    • DOI 10.1016/0198-8859(90)90071-V
    • Anasetti C, Beatty PG, Storb R, et al. Effect of HLA incompatibility on graft-versus-host disease, relapse, and survival after marrow transplantation for patients with leukemia or lymphoma. Hum Immunol. 1990;29(2):79-91. (Pubitemid 20357658)
    • (1990) Human Immunology , vol.29 , Issue.2 , pp. 79-91
    • Anasetti, C.1    Beatty, P.G.2    Storb, R.3    Martin, P.J.4    Mori, M.5    Sanders, J.E.6    Thomas, E.D.7    Hansen, J.A.8
  • 79
    • 67651149659 scopus 로고    scopus 로고
    • Haploidentical hematopoietic stem cell transplantation in child hematologic malignancies with G-CSF-mobilized marrow grafts without T-cell depletion: A single-center report of 45 cases
    • Wang HX, Yan HM, Duan LN, et al. Haploidentical hematopoietic stem cell transplantation in child hematologic malignancies with G-CSF-mobilized marrow grafts without T-cell depletion: a single-center report of 45 cases. Pediatr Hematol Oncol. 2009;26(3):119-128.
    • (2009) Pediatr Hematol Oncol , vol.26 , Issue.3 , pp. 119-128
    • Wang, H.X.1    Yan, H.M.2    Duan, L.N.3
  • 80
    • 66549125203 scopus 로고    scopus 로고
    • Haploidentical stem cell transplantation after a reduced- intensity conditioning regimen for the treatment of advanced hematologic malignancies: Posttransplantation CD8-depleted donor lymphocyte infusions contribute to improve T-cell recovery
    • Dodero A, Carniti C, Raganato A, et al. Haploidentical stem cell transplantation after a reduced- intensity conditioning regimen for the treatment of advanced hematologic malignancies: posttransplantation CD8-depleted donor lymphocyte infusions contribute to improve T-cell recovery. Blood. 2009;113(19):4771-4779.
    • (2009) Blood , vol.113 , Issue.19 , pp. 4771-4779
    • Dodero, A.1    Carniti, C.2    Raganato, A.3
  • 81
    • 64749113174 scopus 로고    scopus 로고
    • Haploidentical hematopoietic stem cell transplantation without in vitro T cell depletion for treatment of hematologic malignancies in children
    • Huang X, Liu D, Liu K, et al. Haploidentical hematopoietic stem cell transplantation without in vitro T cell depletion for treatment of hematologic malignancies in children. Biol Blood Marrow Transplant. 2009;15(1 suppl):91-94.
    • (2009) Biol Blood Marrow Transplant , vol.15 , Issue.1 SUPPL. , pp. 91-94
    • Huang, X.1    Liu, D.2    Liu, K.3
  • 82
    • 33746936705 scopus 로고    scopus 로고
    • Haploidentical hematopoietic stem cell transplantation without in vitro T-cell depletion for the treatment of hematological malignancies
    • Huang XJ, Liu DH, Liu KY, et al. Haploidentical hematopoietic stem cell transplantation without in vitro T-cell depletion for the treatment of hematological malignancies. Bone Marrow Transplant. 2006;38(4):291-297.
    • (2006) Bone Marrow Transplant , vol.38 , Issue.4 , pp. 291-297
    • Huang, X.J.1    Liu, D.H.2    Liu, K.Y.3
  • 84
    • 2442420923 scopus 로고    scopus 로고
    • Successful Treatment of Refractory Autoimmune Hemolytic Anemia with Monthly Rituximab Following Nonmyeloablative Stem Cell Transplantation for Sickle Cell Disease
    • DOI 10.1097/00043426-200405000-00011
    • Raj A, Bertolone S, Cheerva A. Successful treatment of refractory autoimmune hemolytic anemia with monthly rituximab following nonmyeloablative stem cell transplantation for sickle cell disease. J Pediatr Hematol Oncol. 2004;26(5):312-314. (Pubitemid 38621373)
    • (2004) Journal of Pediatric Hematology/Oncology , vol.26 , Issue.5 , pp. 312-314
    • Raj, A.1    Bertolone, S.2    Cheerva, A.3
  • 85
    • 55549090680 scopus 로고    scopus 로고
    • Reduced intensity HLAhaploidentical BMT with post transplantation cyclophosphamide in nonmalignant hematologic diseases
    • Brodsky RA, Luznik L, Bolanos-Meade J, Leffell MS, Jones RJ, Fuchs EJ. Reduced intensity HLAhaploidentical BMT with post transplantation cyclophosphamide in nonmalignant hematologic diseases. Bone Marrow Transplant. 2008;42(8):523-527.
    • (2008) Bone Marrow Transplant , vol.42 , Issue.8 , pp. 523-527
    • Brodsky, R.A.1    Luznik, L.2    Bolanos-Meade, J.3    Leffell, M.S.4    Jones, R.J.5    Fuchs, E.J.6
  • 89
    • 33645734405 scopus 로고    scopus 로고
    • Correction of X-linked chronic granulomatous disease by gene therapy, augmented by insertional activation of MDS1-EVI1, PRDM16 or SETBP1
    • Ott MG, Schmidt M, Schwarzwaelder K, et al. Correction of X-linked chronic granulomatous disease by gene therapy, augmented by insertional activation of MDS1-EVI1, PRDM16 or SETBP1. Nat Med. 2006;12(4):401-409.
    • (2006) Nat Med , vol.12 , Issue.4 , pp. 401-409
    • Ott, M.G.1    Schmidt, M.2    Schwarzwaelder, K.3
  • 91
    • 0343628721 scopus 로고    scopus 로고
    • Therapeutic haemoglobin synthesis in beta-thalassaemic mice expressing lentivirus-encoded human beta-globin
    • DOI 10.1038/35017565
    • May C, Rivella S, Callegari J, et al. Therapeutic haemoglobin synthesis in beta-thalassaemic mice expressing lentivirus-encoded human beta-globin. Nature. 2000;406(6791):82-86. (Pubitemid 30460215)
    • (2000) Nature , vol.406 , Issue.6791 , pp. 82-86
    • Chad, M.1    Rivella, S.2    Callegari, J.3    Heller, G.4    Gaensler, K.M.L.5    Luzzatto, L.6    Sadelain, M.7
  • 92
    • 0037772187 scopus 로고    scopus 로고
    • Successful treatment of murine beta-thalassemia using in vivo selection of genetically modified, drug-resistant hematopoietic stem cells
    • DOI 10.1182/blood-2003-03-0677
    • Persons DA, Allay ER, Sawai N, et al. Successful treatment of murine beta-thalassemia using in vivo selection of genetically modified, drug-resistant hematopoietic stem cells. Blood. 2003;102(2):506-513. (Pubitemid 36841967)
    • (2003) Blood , vol.102 , Issue.2 , pp. 506-513
    • Persons, D.A.1    Allay, E.R.2    Sawai, N.3    Hargrove, P.W.4    Brent, T.P.5    Hanawa, H.6    Nienhuis, A.W.7    Sorrentino, B.P.8
  • 93
    • 0037443467 scopus 로고    scopus 로고
    • The degree of phenotypic correction of murine beta-thalassemia intermedia following lentiviral-mediated transfer of a human gamma-globin gene is influenced by chromosomal position effects and vector copy number
    • DOI 10.1182/blood-2002-07-2211
    • Persons DA, Hargrove PW, Allay ER, Hanawa H, Nienhuis AW. The degree of phenotypic correction of murine beta -thalassemia intermedia following lentiviral-mediated transfer of a human gamma-globin gene is influenced by chromosomal position effects and vector copy number. Blood. 2003;101(6):2175- 2183. (Pubitemid 36302055)
    • (2003) Blood , vol.101 , Issue.6 , pp. 2175-2183
    • Persons, D.A.1    Hargrove, P.W.2    Allay, E.R.3    Hanawa, H.4    Nienhuis, A.W.5
  • 96
    • 79958017228 scopus 로고    scopus 로고
    • 3′UTR-truncated Hmga2 cDNA causes MPN-like hematopoiesis by conferring a clonal growth advantage at the level of HSC in mice
    • Ikeda K, Mason PJ, Bessler M. 3′UTR-truncated Hmga2 cDNA causes MPN-like hematopoiesis by conferring a clonal growth advantage at the level of HSC in mice. Blood. 2011;117(22):5860-5869.
    • (2011) Blood , vol.117 , Issue.22 , pp. 5860-5869
    • Ikeda, K.1    Mason, P.J.2    Bessler, M.3


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