-
1
-
-
0033916804
-
Epidemiology of hepatitis C: Geographic differences and temporal trends
-
Wasley, A and Alter, MJ (2000). Epidemiology of hepatitis C: geographic differences and temporal trends. Semin Liver Dis 20: 1-16.
-
(2000)
Semin Liver Dis
, vol.20
, pp. 1-16
-
-
Wasley, A.1
Alter, M.J.2
-
2
-
-
23944482649
-
Challenges and successes in developing new therapies for hepatitis C
-
De Francesco, R and Migliaccio, G (2005). Challenges and successes in developing new therapies for hepatitis C. Nature 436: 953-960.
-
(2005)
Nature
, vol.436
, pp. 953-960
-
-
De Francesco, R.1
Migliaccio, G.2
-
3
-
-
80053116412
-
MicroRNA-122: A therapeutic target for hepatitis C virus (HCV) infection
-
Nunnari, G and Schnell, MJ (2011). MicroRNA-122: a therapeutic target for hepatitis C virus (HCV) infection. Front Biosci (Schol Ed) 3: 1032-1037.
-
(2011)
Front Biosci (Schol Ed)
, vol.3
, pp. 1032-1037
-
-
Nunnari, G.1
Schnell, M.J.2
-
4
-
-
84862740452
-
Chronic hepatitis C: Treatments of the future
-
Bourlière, M, Khaloun, A, Wartelle-Bladou, C, Oules, V, Portal, I, Benali, S et al. (2011). Chronic hepatitis C: treatments of the future. Clin Res Hepatol Gastroenterol 35 Suppl 2: S84-S95.
-
(2011)
Clin Res Hepatol Gastroenterol
, vol.35
, Issue.SUPPL. 2
-
-
Bourlière, M.1
Khaloun, A.2
Wartelle-Bladou, C.3
Oules, V.4
Portal, I.5
Benali, S.6
-
5
-
-
77953013128
-
Rapid emergence of protease inhibitor resistance in hepatitis C virus
-
Rong, L, Dahari, H, Ribeiro, RM and Perelson, AS (2010). Rapid emergence of protease inhibitor resistance in hepatitis C virus. Sci Transl Med 2: 30ra32.
-
(2010)
Sci Transl Med
, vol.2
-
-
Rong, L.1
Dahari, H.2
Ribeiro, R.M.3
Perelson, A.S.4
-
6
-
-
78649553490
-
Inhibition of hepatitis C virus replication using adeno-associated virus vector delivery of an exogenous antihepatitis C virus microRNA cluster
-
Yang, X, Haurigot, V, Zhou, S, Luo, G and Couto, LB (2010). Inhibition of hepatitis C virus replication using adeno-associated virus vector delivery of an exogenous antihepatitis C virus microRNA cluster. Hepatology 52: 1877-1887.
-
(2010)
Hepatology
, vol.52
, pp. 1877-1887
-
-
Yang, X.1
Haurigot, V.2
Zhou, S.3
Luo, G.4
Couto, L.B.5
-
7
-
-
0142165224
-
Functional siRNAs and miRNAs exhibit strand bias
-
Khvorova, A, Reynolds, A and Jayasena, SD (2003). Functional siRNAs and miRNAs exhibit strand bias. Cell 115: 209-216.
-
(2003)
Cell
, vol.115
, pp. 209-216
-
-
Khvorova, A.1
Reynolds, A.2
Jayasena, S.D.3
-
8
-
-
10744225153
-
Asymmetry in the assembly of the RNAi enzyme complex
-
Schwarz, DS, Hutvágner, G, Du, T, Xu, Z, Aronin, N and Zamore, PD (2003). Asymmetry in the assembly of the RNAi enzyme complex. Cell 115: 199-208.
-
(2003)
Cell
, vol.115
, pp. 199-208
-
-
Schwarz, D.S.1
Hutvágner, G.2
Du, T.3
Xu, Z.4
Aronin, N.5
Zamore, P.D.6
-
9
-
-
56349155978
-
Engineering and optimization of the miR-106b cluster for ectopic expression of multiplexed anti-HIV RNAs
-
Aagaard, LA, Zhang, J, von Eije, KJ, Li, H, Saetrom, P, Amarzguioui, M et al. (2008). Engineering and optimization of the miR-106b cluster for ectopic expression of multiplexed anti-HIV RNAs. Gene Ther 15: 1536-1549.
-
(2008)
Gene Ther
, vol.15
, pp. 1536-1549
-
-
Aagaard, L.A.1
Zhang, J.2
Von Eije, K.J.3
Li, H.4
Saetrom, P.5
Amarzguioui, M.6
-
10
-
-
44349164025
-
Inhibition of HIV-1 by multiple siRNAs expressed from a single microRNA polycistron
-
Liu, YP, Haasnoot, J, ter Brake, O, Berkhout, B and Konstantinova, P (2008). Inhibition of HIV-1 by multiple siRNAs expressed from a single microRNA polycistron. Nucleic Acids Res 36: 2811-2824.
-
(2008)
Nucleic Acids Res
, vol.36
, pp. 2811-2824
-
-
Liu, Y.P.1
Haasnoot, J.2
Ter Brake, O.3
Berkhout, B.4
Konstantinova, P.5
-
11
-
-
34548828780
-
Cell culture and infection system for hepatitis C virus
-
Kato, T, Date, T, Murayama, A, Morikawa, K, Akazawa, D and Wakita, T (2006). Cell culture and infection system for hepatitis C virus. Nat Protoc 1: 2334-2339.
-
(2006)
Nat Protoc
, vol.1
, pp. 2334-2339
-
-
Kato, T.1
Date, T.2
Murayama, A.3
Morikawa, K.4
Akazawa, D.5
Wakita, T.6
-
12
-
-
72849106317
-
Apolipoprotein e but not B is required for the formation of infectious hepatitis C virus particles
-
Jiang, J and Luo, G (2009). Apolipoprotein E but not B is required for the formation of infectious hepatitis C virus particles. J Virol 83: 12680-12691.
-
(2009)
J Virol
, vol.83
, pp. 12680-12691
-
-
Jiang, J.1
Luo, G.2
-
13
-
-
0042847091
-
Dynamics of hepatitis C virus replication in human liver
-
Chang, M, Williams, O, Mittler, J, Quintanilla, A, Carithers, RL Jr, Perkins, J et al. (2003). Dynamics of hepatitis C virus replication in human liver. Am J Pathol 163: 433-444.
-
(2003)
Am J Pathol
, vol.163
, pp. 433-444
-
-
Chang, M.1
Williams, O.2
Mittler, J.3
Quintanilla, A.4
Carithers Jr., R.L.5
Perkins, J.6
-
14
-
-
81255210927
-
Role of pri-miRNA tertiary structure in miR-17~92 miRNA biogenesis
-
Chaulk, SG, Thede, GL, Kent, OA, Xu, Z, Gesner, EM, Veldhoen, RA et al. (2011). Role of pri-miRNA tertiary structure in miR-17~92 miRNA biogenesis. RNA Biol 8: 1105-1114.
-
(2011)
RNA Biol
, vol.8
, pp. 1105-1114
-
-
Chaulk, S.G.1
Thede, G.L.2
Kent, O.A.3
Xu, Z.4
Gesner, E.M.5
Veldhoen, R.A.6
-
15
-
-
44449121785
-
Artificial miRNAs mitigate shRNA-mediated toxicity in the brain: Implications for the therapeutic development of RNAi
-
McBride, JL, Boudreau, RL, Harper, SQ, Staber, PD, Monteys, AM, Martins, I et al. (2008). Artificial miRNAs mitigate shRNA-mediated toxicity in the brain: implications for the therapeutic development of RNAi. Proc Natl Acad Sci USA 105: 5868-5873.
-
(2008)
Proc Natl Acad Sci USA
, vol.105
, pp. 5868-5873
-
-
McBride, J.L.1
Boudreau, R.L.2
Harper, S.Q.3
Staber, P.D.4
Monteys, A.M.5
Martins, I.6
-
16
-
-
24644483623
-
Modulation of hepatitis C virus RNA abundance by a liver-specific MicroRNA
-
Jopling, CL, Yi, M, Lancaster, AM, Lemon, SM and Sarnow, P (2005). Modulation of hepatitis C virus RNA abundance by a liver-specific MicroRNA. Science 309: 1577-1581.
-
(2005)
Science
, vol.309
, pp. 1577-1581
-
-
Jopling, C.L.1
Yi, M.2
Lancaster, A.M.3
Lemon, S.M.4
Sarnow, P.5
-
17
-
-
59649122961
-
Long-term correction of inhibitor-prone hemophilia B dogs treated with liverdirected AAV2-mediated factor IX gene therapy
-
Niemeyer, GP, Herzog, RW, Mount, J, Arruda, VR, Tillson, DM, Hathcock, J et al. (2009). Long-term correction of inhibitor-prone hemophilia B dogs treated with liverdirected AAV2-mediated factor IX gene therapy. Blood 113: 797-806.
-
(2009)
Blood
, vol.113
, pp. 797-806
-
-
Niemeyer, G.P.1
Herzog, R.W.2
Mount, J.3
Arruda, V.R.4
Tillson, D.M.5
Hathcock, J.6
-
18
-
-
0034960344
-
Extrachromosomal recombinant adeno-associated virus vector genomes are primarily responsible for stable liver transduction in vivo
-
Nakai, H, Yant, SR, Storm, TA, Fuess, S, Meuse, L and Kay, MA (2001). Extrachromosomal recombinant adeno-associated virus vector genomes are primarily responsible for stable liver transduction in vivo. J Virol 75: 6969-6976.
-
(2001)
J Virol
, vol.75
, pp. 6969-6976
-
-
Nakai, H.1
Yant, S.R.2
Storm, T.A.3
Fuess, S.4
Meuse, L.5
Kay, M.A.6
-
19
-
-
33644636312
-
Preclinical profile of VX-950, a potent, selective, and orally bioavailable inhibitor of hepatitis C virus NS3-4A serine protease
-
Perni, RB, Almquist, SJ, Byrn, RA, Chandorkar, G, Chaturvedi, PR, Courtney, LF et al. (2006). Preclinical profile of VX-950, a potent, selective, and orally bioavailable inhibitor of hepatitis C virus NS3-4A serine protease. Antimicrob Agents Chemother 50: 899-909.
-
(2006)
Antimicrob Agents Chemother
, vol.50
, pp. 899-909
-
-
Perni, R.B.1
Almquist, S.J.2
Byrn, R.A.3
Chandorkar, G.4
Chaturvedi, P.R.5
Courtney, L.F.6
-
20
-
-
0034882826
-
Self-complementary recombinant adeno-associated virus (scAAV) vectors promote efficient transduction independently of DNA synthesis
-
McCarty, DM, Monahan, PE and Samulski, RJ (2001). Self-complementary recombinant adeno-associated virus (scAAV) vectors promote efficient transduction independently of DNA synthesis. Gene Ther 8: 1248-1254.
-
(2001)
Gene Ther
, vol.8
, pp. 1248-1254
-
-
McCarty, D.M.1
Monahan, P.E.2
Samulski, R.J.3
-
21
-
-
0037015049
-
Novel adeno-associated viruses from rhesus monkeys as vectors for human gene therapy
-
Gao, GP, Alvira, MR, Wang, L, Calcedo, R, Johnston, J and Wilson, JM (2002). Novel adeno-associated viruses from rhesus monkeys as vectors for human gene therapy. Proc Natl Acad Sci USA 99: 11854-11859.
-
(2002)
Proc Natl Acad Sci USA
, vol.99
, pp. 11854-11859
-
-
Gao, G.P.1
Alvira, M.R.2
Wang, L.3
Calcedo, R.4
Johnston, J.5
Wilson, J.M.6
-
22
-
-
0032805251
-
Hydrodynamics-based transfection in animals by systemic administration of plasmid DNA
-
Liu, F, Song, Y and Liu, D (1999). Hydrodynamics-based transfection in animals by systemic administration of plasmid DNA. Gene Ther 6: 1258-1266.
-
(1999)
Gene Ther
, vol.6
, pp. 1258-1266
-
-
Liu, F.1
Song, Y.2
Liu, D.3
-
23
-
-
4644223259
-
Mechanisms of gene silencing by double-stranded RNA
-
Meister, G and Tuschl, T (2004). Mechanisms of gene silencing by double-stranded RNA. Nature 431: 343-349.
-
(2004)
Nature
, vol.431
, pp. 343-349
-
-
Meister, G.1
Tuschl, T.2
-
24
-
-
77953629046
-
Regulation of mRNA translation and stability by microRNAs
-
Fabian, MR, Sonenberg, N and Filipowicz, W (2010). Regulation of mRNA translation and stability by microRNAs. Annu Rev Biochem 79: 351-379.
-
(2010)
Annu Rev Biochem
, vol.79
, pp. 351-379
-
-
Fabian, M.R.1
Sonenberg, N.2
Filipowicz, W.3
-
25
-
-
54949095836
-
Misinterpreting the therapeutic effects of small interfering RNA caused by immune stimulation
-
Robbins, M, Judge, A, Ambegia, E, Choi, C, Yaworski, E, Palmer, L et al. (2008). Misinterpreting the therapeutic effects of small interfering RNA caused by immune stimulation. Hum Gene Ther 19: 991-999.
-
(2008)
Hum Gene Ther
, vol.19
, pp. 991-999
-
-
Robbins, M.1
Judge, A.2
Ambegia, E.3
Choi, C.4
Yaworski, E.5
Palmer, L.6
-
26
-
-
84865245416
-
Systemic errors in quantitative polymerase chain reaction titration of selfcomplementary adeno-associated viral vectors and improved alternative methods
-
Fagone, P, Wright, JF, Nathwani, AC, Nienhuis, AW, Davidoff, AM and Gray, JT (2012). Systemic errors in quantitative polymerase chain reaction titration of selfcomplementary adeno-associated viral vectors and improved alternative methods. Hum Gene Ther Methods 23: 1-7.
-
(2012)
Hum Gene Ther Methods
, vol.23
, pp. 1-7
-
-
Fagone, P.1
Wright, J.F.2
Nathwani, A.C.3
Nienhuis, A.W.4
Davidoff, A.M.5
Gray, J.T.6
-
27
-
-
80052335519
-
Vector characterization methods for quality control testing of recombinant adeno-associated viruses
-
Wright, JF and Zelenaia, O (2011). Vector characterization methods for quality control testing of recombinant adeno-associated viruses. Methods Mol Biol 737: 247-278.
-
(2011)
Methods Mol Biol
, vol.737
, pp. 247-278
-
-
Wright, J.F.1
Zelenaia, O.2
-
28
-
-
0037223085
-
Quantification of adeno-associated virus particles and empty capsids by optical density measurement
-
Sommer, JM, Smith, PH, Parthasarathy, S, Isaacs, J, Vijay, S, Kieran, J et al. (2003). Quantification of adeno-associated virus particles and empty capsids by optical density measurement. Mol Ther 7: 122-128.
-
(2003)
Mol Ther
, vol.7
, pp. 122-128
-
-
Sommer, J.M.1
Smith, P.H.2
Parthasarathy, S.3
Isaacs, J.4
Vijay, S.5
Kieran, J.6
-
29
-
-
33745299723
-
Fatality in mice due to oversaturation of cellular microRNA/short hairpin RNA pathways
-
Grimm, D, Streetz, KL, Jopling, CL, Storm, TA, Pandey, K, Davis, CR et al. (2006). Fatality in mice due to oversaturation of cellular microRNA/short hairpin RNA pathways. Nature 441: 537-541.
-
(2006)
Nature
, vol.441
, pp. 537-541
-
-
Grimm, D.1
Streetz, K.L.2
Jopling, C.L.3
Storm, T.A.4
Pandey, K.5
Davis, C.R.6
-
30
-
-
0344321890
-
RNA interference blocks gene expression and RNA synthesis from hepatitis C replicons propagated in human liver cells
-
Wilson, JA, Jayasena, S, Khvorova, A, Sabatinos, S, Rodrigue-Gervais, IG, Arya, S et al. (2003). RNA interference blocks gene expression and RNA synthesis from hepatitis C replicons propagated in human liver cells. Proc Natl Acad Sci USA 100: 2783-2788.
-
(2003)
Proc Natl Acad Sci USA
, vol.100
, pp. 2783-2788
-
-
Wilson, J.A.1
Jayasena, S.2
Khvorova, A.3
Sabatinos, S.4
Rodrigue-Gervais, I.G.5
Arya, S.6
-
31
-
-
7944228148
-
RNA interference as an antiviral approach: Targeting HIV-1
-
Berkhout, B (2004). RNA interference as an antiviral approach: targeting HIV-1. Curr Opin Mol Ther 6: 141-145.
-
(2004)
Curr Opin Mol Ther
, vol.6
, pp. 141-145
-
-
Berkhout, B.1
-
32
-
-
1842478962
-
Control of HIV-1 replication by RNA interference
-
Lee, NS and Rossi, JJ (2004). Control of HIV-1 replication by RNA interference. Virus Res 102: 53-58.
-
(2004)
Virus Res
, vol.102
, pp. 53-58
-
-
Lee, N.S.1
Rossi, J.J.2
-
33
-
-
13744250051
-
Computational design of antiviral RNA interference strategies that resist human immunodeficiency virus escape
-
Leonard, JN and Schaffer, DV (2005). Computational design of antiviral RNA interference strategies that resist human immunodeficiency virus escape. J Virol 79: 1645-1654.
-
(2005)
J Virol
, vol.79
, pp. 1645-1654
-
-
Leonard, J.N.1
Schaffer, D.V.2
-
34
-
-
78649251945
-
A perspective on modelling hepatitis C virus infection
-
Guedj, J, Rong, L, Dahari, H and Perelson, AS (2010). A perspective on modelling hepatitis C virus infection. J Viral Hepat 17: 825-833.
-
(2010)
J Viral Hepat
, vol.17
, pp. 825-833
-
-
Guedj, J.1
Rong, L.2
Dahari, H.3
Perelson, A.S.4
-
35
-
-
17044394814
-
Sustained correction of disease in naive and AAV2-pretreated hemophilia B dogs: AAV2/8-mediated, liver-directed gene therapy
-
Wang, L, Calcedo, R, Nichols, TC, Bellinger, DA, Dillow, A, Verma, IM et al. (2005). Sustained correction of disease in naive and AAV2-pretreated hemophilia B dogs: AAV2/8-mediated, liver-directed gene therapy. Blood 105: 3079-3086.
-
(2005)
Blood
, vol.105
, pp. 3079-3086
-
-
Wang, L.1
Calcedo, R.2
Nichols, T.C.3
Bellinger, D.A.4
Dillow, A.5
Verma, I.M.6
-
36
-
-
28844452008
-
Biology of AAV serotype vectors in liver-directed gene transfer to nonhuman primates
-
Gao, G, Lu, Y, Calcedo, R, Grant, RL, Bell, P, Wang, L et al. (2006). Biology of AAV serotype vectors in liver-directed gene transfer to nonhuman primates. Mol Ther 13: 77-87.
-
(2006)
Mol Ther
, vol.13
, pp. 77-87
-
-
Gao, G.1
Lu, Y.2
Calcedo, R.3
Grant, R.L.4
Bell, P.5
Wang, L.6
-
37
-
-
84855161388
-
Adenovirus-associated virus vector-mediated gene transfer in hemophilia B
-
Nathwani, AC, Tuddenham, EG, Rangarajan, S, Rosales, C, McIntosh, J, Linch, DC et al. (2011). Adenovirus-associated virus vector-mediated gene transfer in hemophilia B. N Engl J Med 365: 2357-2365.
-
(2011)
N Engl J Med
, vol.365
, pp. 2357-2365
-
-
Nathwani, A.C.1
Tuddenham, E.G.2
Rangarajan, S.3
Rosales, C.4
McIntosh, J.5
Linch, D.C.6
-
38
-
-
68949201638
-
Focal distribution of hepatitis C virus RNA in infected livers
-
Stiffler, JD, Nguyen, M, Sohn, JA, Liu, C, Kaplan, D and Seeger, C (2009). Focal distribution of hepatitis C virus RNA in infected livers. PLoS ONE 4: e6661.
-
(2009)
PLoS ONE
, vol.4
-
-
Stiffler, J.D.1
Nguyen, M.2
Sohn, J.A.3
Liu, C.4
Kaplan, D.5
Seeger, C.6
-
39
-
-
43149120419
-
Exosome function: From tumor immunology to pathogen biology
-
Schorey, JS and Bhatnagar, S (2008). Exosome function: from tumor immunology to pathogen biology. Traffic 9: 871-881.
-
(2008)
Traffic
, vol.9
, pp. 871-881
-
-
Schorey, J.S.1
Bhatnagar, S.2
-
40
-
-
61349173156
-
Characterization and comprehensive proteome profiling of exosomes secreted by hepatocytes
-
Conde-Vancells, J, Rodriguez-Suarez, E, Embade, N, Gil, D, Matthiesen, R, Valle, M et al. (2008). Characterization and comprehensive proteome profiling of exosomes secreted by hepatocytes. J Proteome Res 7: 5157-5166.
-
(2008)
J Proteome Res
, vol.7
, pp. 5157-5166
-
-
Conde-Vancells, J.1
Rodriguez-Suarez, E.2
Embade, N.3
Gil, D.4
Matthiesen, R.5
Valle, M.6
-
41
-
-
0348038748
-
Rapid and highly efficient transduction by double-stranded adeno-associated virus vectors in vitro and in vivo
-
Wang, Z, Ma, HI, Li, J, Sun, L, Zhang, J and Xiao, X (2003). Rapid and highly efficient transduction by double-stranded adeno-associated virus vectors in vitro and in vivo. Gene Ther 10: 2105-2111.
-
(2003)
Gene Ther
, vol.10
, pp. 2105-2111
-
-
Wang, Z.1
Ma, H.I.2
Li, J.3
Sun, L.4
Zhang, J.5
Xiao, X.6
-
42
-
-
33645528206
-
Self-complementary adeno-associated virus vectors containing a novel liver-specific human factor IX expression cassette enable highly efficient transduction of murine and nonhuman primate liver
-
Nathwani, AC, Gray, JT, Ng, CY, Zhou, J, Spence, Y, Waddington, SN et al. (2006). Self-complementary adeno-associated virus vectors containing a novel liver-specific human factor IX expression cassette enable highly efficient transduction of murine and nonhuman primate liver. Blood 107: 2653-2661.
-
(2006)
Blood
, vol.107
, pp. 2653-2661
-
-
Nathwani, A.C.1
Gray, J.T.2
Ng, C.Y.3
Zhou, J.4
Spence, Y.5
Waddington, S.N.6
-
43
-
-
0346777307
-
Adeno-associated virus terminal repeat (TR) mutant generates self-complementary vectors to overcome the rate-limiting step to transduction in vivo
-
McCarty, DM, Fu, H, Monahan, PE, Toulson, CE, Naik, P and Samulski, RJ (2003). Adeno-associated virus terminal repeat (TR) mutant generates self-complementary vectors to overcome the rate-limiting step to transduction in vivo. Gene Ther 10: 2112-2118.
-
(2003)
Gene Ther
, vol.10
, pp. 2112-2118
-
-
McCarty, D.M.1
Fu, H.2
Monahan, P.E.3
Toulson, C.E.4
Naik, P.5
Samulski, R.J.6
-
44
-
-
79955405275
-
Good manufacturing practice production of self-complementary serotype 8 adenoassociated viral vector for a hemophilia B clinical trial
-
Allay, JA, Sleep, S, Long, S, Tillman, DM, Clark, R, Carney, G et al. (2011). Good manufacturing practice production of self-complementary serotype 8 adenoassociated viral vector for a hemophilia B clinical trial. Hum Gene Ther 22: 595-604.
-
(2011)
Hum Gene Ther
, vol.22
, pp. 595-604
-
-
Allay, J.A.1
Sleep, S.2
Long, S.3
Tillman, D.M.4
Clark, R.5
Carney, G.6
-
45
-
-
79954622209
-
Therapeutic in vivo gene transfer for genetic disease using AAV: Progress and challenges
-
Mingozzi, F and High, KA (2011). Therapeutic in vivo gene transfer for genetic disease using AAV: progress and challenges. Nat Rev Genet 12: 341-355.
-
(2011)
Nat Rev Genet
, vol.12
, pp. 341-355
-
-
Mingozzi, F.1
High, K.A.2
-
46
-
-
82955199935
-
Preclinical safety of RNAi-mediated HTT suppression in the rhesus macaque as a potential therapy for Huntington's disease
-
McBride, JL, Pitzer, MR, Boudreau, RL, Dufour, B, Hobbs, T, Ojeda, SR et al. (2011). Preclinical safety of RNAi-mediated HTT suppression in the rhesus macaque as a potential therapy for Huntington's disease. Mol Ther 19: 2152-2162.
-
(2011)
Mol Ther
, vol.19
, pp. 2152-2162
-
-
McBride, J.L.1
Pitzer, M.R.2
Boudreau, R.L.3
Dufour, B.4
Hobbs, T.5
Ojeda, S.R.6
-
47
-
-
77649242176
-
Gene therapy for Leber's congenital amaurosis is safe and effective through 1.5 years after vector administration
-
Simonelli, F, Maguire, AM, Testa, F, Pierce, EA, Mingozzi, F, Bennicelli, JL et al. (2010). Gene therapy for Leber's congenital amaurosis is safe and effective through 1.5 years after vector administration. Mol Ther 18: 643-650.
-
(2010)
Mol Ther
, vol.18
, pp. 643-650
-
-
Simonelli, F.1
Maguire, A.M.2
Testa, F.3
Pierce, E.A.4
Mingozzi, F.5
Bennicelli, J.L.6
-
48
-
-
79959201563
-
The genome of self-complementary adeno-associated viral vectors increases Toll-like receptor 9-dependent innate immune responses in the liver
-
Martino, AT, Suzuki, M, Markusic, DM, Zolotukhin, I, Ryals, RC, Moghimi, B et al. (2011). The genome of self-complementary adeno-associated viral vectors increases Toll-like receptor 9-dependent innate immune responses in the liver. Blood 117: 6459-6468.
-
(2011)
Blood
, vol.117
, pp. 6459-6468
-
-
Martino, A.T.1
Suzuki, M.2
Markusic, D.M.3
Zolotukhin, I.4
Ryals, R.C.5
Moghimi, B.6
-
49
-
-
0141482003
-
Preclinical in vivo evaluation of pseudotyped adeno-associated virus vectors for liver gene therapy
-
Grimm, D, Zhou, S, Nakai, H, Thomas, CE, Storm, TA, Fuess, S et al. (2003). Preclinical in vivo evaluation of pseudotyped adeno-associated virus vectors for liver gene therapy. Blood 102: 2412-2419.
-
(2003)
Blood
, vol.102
, pp. 2412-2419
-
-
Grimm, D.1
Zhou, S.2
Nakai, H.3
Thomas, C.E.4
Storm, T.A.5
Fuess, S.6
-
50
-
-
0033016820
-
Real-time detection system for quantification of hepatitis C virus genome
-
Takeuchi, T, Katsume, A, Tanaka, T, Abe, A, Inoue, K, Tsukiyama-Kohara, K et al. (1999). Real-time detection system for quantification of hepatitis C virus genome. Gastroenterology 116: 636-642.
-
(1999)
Gastroenterology
, vol.116
, pp. 636-642
-
-
Takeuchi, T.1
Katsume, A.2
Tanaka, T.3
Abe, A.4
Inoue, K.5
Tsukiyama-Kohara, K.6
|