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Volumn 10, Issue , 2012, Pages

Treatment of adult MPSI mouse brains with IDUA-expressing mesenchymal stem cells decreases GAG deposition and improves exploratory behavior

Author keywords

Gene therapy; IDUA; Lysosomal storage disorder; Mesenchymal stem cell; MPSI; Retroviral vectors

Indexed keywords

DERMATAN; HEPARAN SULFATE; LEVO IDURONIDASE; MURINE LEUKEMIA VIRUS VECTOR LEVO IDURONIDASE; UNCLASSIFIED DRUG; VIRUS VECTOR;

EID: 84862228938     PISSN: None     EISSN: 14790556     Source Type: Journal    
DOI: 10.1186/1479-0556-10-2     Document Type: Article
Times cited : (6)

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