Nonviral in vivo gene transfer in the mucopolysaccharidosis I murine model

Journal of Inherited Metabolic Disease

Volumn 28, Issue 6, 2005, Pages 1035-1043

  Camassola, M ^a   Braga, L M ^a   Delgado Canedo A ^a   Dalberto, T P ^a   Matte, U ^b   Burin, M ^b   Giugliani, R ^b   Nardi, N B ^a  

^a FEDERAL UNIVERSITY OF RIO GRANDE DO SUL   (Brazil)

^b HOSPITAL DE CLÍNICAS DE PORTO ALEGRE   (Brazil)

Author keywords

[No Author keywords available]

Indexed keywords

COMPLEMENTARY DNA; GLYCOSAMINOGLYCAN; LEVO IDURONIDASE;

ANIMAL EXPERIMENT; ANIMAL MODEL; ARTICLE; CONTROLLED STUDY; DISEASE MODEL; DRUG BRAIN LEVEL; DRUG LIVER LEVEL; DRUG TISSUE LEVEL; ENZYME ACTIVITY; EXPRESSION VECTOR; GENE TRANSFER; GENE VECTOR; GENETIC TRANSFECTION; HURLER SYNDROME; HYDRODYNAMICS; IN VIVO STUDY; KIDNEY PARENCHYMA; KNOCKOUT MOUSE; LUNG PARENCHYMA; MOUSE; NONHUMAN; NONVIRAL GENE DELIVERY SYSTEM; REAL TIME POLYMERASE CHAIN REACTION; REVERSE TRANSCRIPTION POLYMERASE CHAIN REACTION; SPLEEN; TRANSGENE; WILD TYPE;

ANIMALS; BONE MARROW TRANSPLANTATION; DERMATAN SULFATE; DISEASE MODELS, ANIMAL; DNA, COMPLEMENTARY; GENE THERAPY; GENE TRANSFER TECHNIQUES; GENETIC VECTORS; GLYCOSAMINOGLYCANS; HEPARITIN SULFATE; HUMANS; LYSOSOMES; MICE; MICE, INBRED C57BL; MICE, KNOCKOUT; MUCOPOLYSACCHARIDOSIS I; PLASMIDS; REVERSE TRANSCRIPTASE POLYMERASE CHAIN REACTION; RNA, MESSENGER; TISSUE DISTRIBUTION; TRANSDUCTION, GENETIC; TRANSFECTION;

EID: 31644437927     PISSN: 01418955     EISSN: 15732665     Source Type: Journal    
DOI: 10.1007/s10545-005-0070-5     Document Type: Article

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