Correction of Hunter syndrome in the MPSII mouse model by AAV2/8-mediated gene delivery

Human Molecular Genetics

Volumn 15, Issue 7, 2006, Pages 1225-1236

  Cardone, Monica ^a   Polito, Vinicia Assunta ^a   Pepe, Stefano ^a   Mann, Linda ^b   D'Azzo, Alessandra ^b   Auricchio, Alberto ^a   Ballabio, Andrea ^a   Cosma, Maria Pia ^a  

^a TELETHON INSTITUTE OF GENETICS AND MEDICINE TIGEM   (Italy)

^b ST JUDE CHILDREN S RESEARCH HOSPITAL   (United States)

Author keywords

[No Author keywords available]

Indexed keywords

GLYCOSAMINOGLYCAN; IDURONATE 2 SULFATASE;

ALOPECIA; ANIMAL EXPERIMENT; ANIMAL MODEL; ANIMAL TISSUE; ARTICLE; BONE MALFORMATION; CONTROLLED STUDY; CRANIOFACIAL MALFORMATION; ENZYME ACTIVITY; GAIT DISORDER; GENE TARGETING; GENE THERAPY; GENE TRANSFER; HUNTER SYNDROME; IN VIVO STUDY; MALE; MOUSE; NEUROPATHOLOGY; NONHUMAN; OPEN FIELD TEST; PARVOVIRUS VECTOR; PHENOTYPE; PRIORITY JOURNAL; TASK PERFORMANCE; URINARY EXCRETION; VIRUS PARTICLE;

ANIMALS; DEPENDOVIRUS; DISEASE MODELS, ANIMAL; FLUORESCENT ANTIBODY TECHNIQUE; GENE THERAPY; GENETIC VECTORS; GLYCOSAMINOGLYCANS; HUMANS; IDURONATE SULFATASE; KIDNEY; LIVER; LYSOSOMES; MICE; MICE, KNOCKOUT; MOTOR ACTIVITY; MUCOPOLYSACCHARIDOSIS II; SPLEEN; THYROXINE-BINDING PROTEINS;

ANIMALIA; PARVOVIRUS;

EID: 33645110474     PISSN: 09646906     EISSN: 14602083     Source Type: Journal    
DOI: 10.1093/hmg/ddl038     Document Type: Article

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