Design principles for bifunctional targeted oligonucleotide enhancers of splicing

Nucleic Acids Research

Volumn 39, Issue 16, 2011, Pages 7194-7208

  Owen, Nicholas ^a   Zhou, Haiyan ^b   Malygin, Alexey A ^a,c   Sangha, Jason ^a   Smith, Lindsay D ^a   Muntoni, Francesco ^b   Eperon, Ian C ^a,b  

^a UNIVERSITY OF LEICESTER   (United Kingdom)

^b UNIVERSITY COLLEGE LONDON   (United Kingdom)

^c INSTITUTE OF CHEMICAL BIOLOGY AND FUNDAMENTAL MEDICINE   (Russian Federation)

Author keywords

[No Author keywords available]

Indexed keywords

MESSENGER RNA; MESSENGER RNA PRECURSOR; OLIGONUCLEOTIDE; POLYPYRIMIDINE TRACT BINDING PROTEIN; SURVIVAL MOTOR NEURON PROTEIN 2; TARGETED OLIGONUCLEOTIDE ENHANCERS OF SPLICING; UNCLASSIFIED DRUG;

ALTERNATIVE RNA SPLICING; AMINO ACID SEQUENCE; ARTICLE; CHEMICAL STRUCTURE; CONTROLLED STUDY; EXON; FIBROBLAST; GENE DELETION; HUMAN; HUMAN CELL; IN VITRO STUDY; INTRON; PRIORITY JOURNAL; PROTEIN DOMAIN; PROTEIN EXPRESSION; PROTEIN MOTIF; QUANTITATIVE ANALYSIS; REAL TIME POLYMERASE CHAIN REACTION; REVERSE TRANSCRIPTION POLYMERASE CHAIN REACTION;

BASE SEQUENCE; BINDING SITES; CELL LINE; EXONS; HUMANS; KINETICS; NUCLEAR PROTEINS; OLIGONUCLEOTIDES; RNA SPLICING; RNA-BINDING PROTEINS; SURVIVAL OF MOTOR NEURON 2 PROTEIN;

EID: 79960994014     PISSN: 03051048     EISSN: 13624962     Source Type: Journal    
DOI: 10.1093/nar/gkr152     Document Type: Article

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