-
1
-
-
0034142117
-
Gene therapy for chronic granulomatous disease
-
Kume A., Dinauer M.C. Gene therapy for chronic granulomatous disease. J Lab Clin Med 2000, 135:122-128.
-
(2000)
J Lab Clin Med
, vol.135
, pp. 122-128
-
-
Kume, A.1
Dinauer, M.C.2
-
2
-
-
0027374533
-
Gene targeting of X chromosome-linked chronic granulomatous disease locus in a human myeloid leukemia cell line and rescue by expression of recombinant gp91phox
-
Zhen L., King A.A., Xiao Y., Chanock S.J., Orkin S.H., Dinauer M.C. Gene targeting of X chromosome-linked chronic granulomatous disease locus in a human myeloid leukemia cell line and rescue by expression of recombinant gp91phox. Proc Natl Acad Sci U S A 1993, 90:9832-9836.
-
(1993)
Proc Natl Acad Sci U S A
, vol.90
, pp. 9832-9836
-
-
Zhen, L.1
King, A.A.2
Xiao, Y.3
Chanock, S.J.4
Orkin, S.H.5
Dinauer, M.C.6
-
3
-
-
77949327872
-
Retrovirus gene therapy for X-linked chronic granulomatous disease can achieve stable long-term correction of oxidase activity in peripheral blood neutrophils
-
Kang E.M., Choi U., Theobald N., et al. Retrovirus gene therapy for X-linked chronic granulomatous disease can achieve stable long-term correction of oxidase activity in peripheral blood neutrophils. Blood 2010, 115:783-791.
-
(2010)
Blood
, vol.115
, pp. 783-791
-
-
Kang, E.M.1
Choi, U.2
Theobald, N.3
-
4
-
-
0032847579
-
Bone marrow transplantation for chronic granulomatous disease: long-term follow-up and review of literature
-
Leung T., Chik K., Li C., Shing M., Yuen P. Bone marrow transplantation for chronic granulomatous disease: long-term follow-up and review of literature. Bone Marrow Transplant 1999, 24:567-570.
-
(1999)
Bone Marrow Transplant
, vol.24
, pp. 567-570
-
-
Leung, T.1
Chik, K.2
Li, C.3
Shing, M.4
Yuen, P.5
-
5
-
-
77953014023
-
Hematopoietic stem cell transplantation for chronic granulomatous disease
-
Seger R.A. Hematopoietic stem cell transplantation for chronic granulomatous disease. Immunol Allergy Clin North Am 2010, 30:195-208.
-
(2010)
Immunol Allergy Clin North Am
, vol.30
, pp. 195-208
-
-
Seger, R.A.1
-
6
-
-
0018861986
-
X-linked inheritance in females with chronic granulomatous disease
-
Mills E.L., Rholl K.S., Quie P.G. X-linked inheritance in females with chronic granulomatous disease. J Clin Invest 1980, 66:332-340.
-
(1980)
J Clin Invest
, vol.66
, pp. 332-340
-
-
Mills, E.L.1
Rholl, K.S.2
Quie, P.G.3
-
7
-
-
0003318703
-
X-linked carriers of gp91-phox chronic granulomatous disease (CGD): clinical and potential therapeutic implications of extreme unbalanced X chromosome inactivation
-
Woodman R., Teoh D., Johnston F., et al. X-linked carriers of gp91-phox chronic granulomatous disease (CGD): clinical and potential therapeutic implications of extreme unbalanced X chromosome inactivation. Blood 1995, 86:27a.
-
(1995)
Blood
, vol.86
-
-
Woodman, R.1
Teoh, D.2
Johnston, F.3
-
8
-
-
33645734405
-
Correction of X-linked chronic granulomatous disease by gene therapy, augmented by insertional activation of MDS1-EVI1, PRDM16 or SETBP1
-
Ott M.G., Schmidt M., Schwarzwaelder K., et al. Correction of X-linked chronic granulomatous disease by gene therapy, augmented by insertional activation of MDS1-EVI1, PRDM16 or SETBP1. Nat Med 2006, 12:401-409.
-
(2006)
Nat Med
, vol.12
, pp. 401-409
-
-
Ott, M.G.1
Schmidt, M.2
Schwarzwaelder, K.3
-
9
-
-
76249131912
-
Genomic instability and myelodysplasia with monosomy 7 consequent to EVI1 activation after gene therapy for chronic granulomatous disease
-
Stein S., Ott M.G., Schultze-Strasser S., et al. Genomic instability and myelodysplasia with monosomy 7 consequent to EVI1 activation after gene therapy for chronic granulomatous disease. Nat Med 2010, 16:198-204.
-
(2010)
Nat Med
, vol.16
, pp. 198-204
-
-
Stein, S.1
Ott, M.G.2
Schultze-Strasser, S.3
-
10
-
-
12644293807
-
Prolonged production of NADPH oxidase corrected granulocytes after gene therapy of chronic granulomatous disease
-
22133-12138
-
Malech H.L., Maples P.B., Whiting-Theobald N., et al. Prolonged production of NADPH oxidase corrected granulocytes after gene therapy of chronic granulomatous disease. Proc Natl Acad Sci U S A 1997, 94. 22133-12138.
-
(1997)
Proc Natl Acad Sci U S A
, vol.94
-
-
Malech, H.L.1
Maples, P.B.2
Whiting-Theobald, N.3
-
11
-
-
0003310473
-
Extended production of oxidase normal neutrophils in X-linked chronic granulomatous disease following gene therapy with gp91phox transduced CD34+ cells
-
Malech H.L., Horwitz M.E., Linton G.F., et al. Extended production of oxidase normal neutrophils in X-linked chronic granulomatous disease following gene therapy with gp91phox transduced CD34+ cells. Blood 1998, 92:690.
-
(1998)
Blood
, vol.92
, pp. 690
-
-
Malech, H.L.1
Horwitz, M.E.2
Linton, G.F.3
-
12
-
-
66549113184
-
Advances in treatment for chronic granulomatous disease
-
Kang E., Malech H. Advances in treatment for chronic granulomatous disease. Immunol Res 2009, 43:77-84.
-
(2009)
Immunol Res
, vol.43
, pp. 77-84
-
-
Kang, E.1
Malech, H.2
-
13
-
-
58149469932
-
Transgene optimization significantly improves SIN vector titers, gp91phox expression and reconstitution of superoxide production in X-CGD cells
-
Moreno-Carranza B., Gentsch M., Stein S., et al. Transgene optimization significantly improves SIN vector titers, gp91phox expression and reconstitution of superoxide production in X-CGD cells. Gene Ther 2009, 16:111-118.
-
(2009)
Gene Ther
, vol.16
, pp. 111-118
-
-
Moreno-Carranza, B.1
Gentsch, M.2
Stein, S.3
-
16
-
-
34547807068
-
Foamy virus vectors: an awaited alternative to gammaretro- and lentiviral vectors
-
Rethwilm A. Foamy virus vectors: an awaited alternative to gammaretro- and lentiviral vectors. Curr Gene Ther 2007, 7:261-271.
-
(2007)
Curr Gene Ther
, vol.7
, pp. 261-271
-
-
Rethwilm, A.1
-
17
-
-
0035437131
-
Gene transfer into murine hematopoietic stem cells with helper-free foamy virus vectors
-
Vassilopoulos G., Trobridge G., Josephson N.C., Russell D.W. Gene transfer into murine hematopoietic stem cells with helper-free foamy virus vectors. Blood 2001, 98:604-609.
-
(2001)
Blood
, vol.98
, pp. 604-609
-
-
Vassilopoulos, G.1
Trobridge, G.2
Josephson, N.C.3
Russell, D.W.4
-
19
-
-
0037062431
-
Transduction of human NOD/SCID-repopulating cells with both lymphoid and myeloid potential by foamy virus vectors
-
Josephson N.C., Vassilopoulos G., Trobridge G.D., et al. Transduction of human NOD/SCID-repopulating cells with both lymphoid and myeloid potential by foamy virus vectors. Proc Natl Acad Sci U S A 2002, 99:8295-8300.
-
(2002)
Proc Natl Acad Sci U S A
, vol.99
, pp. 8295-8300
-
-
Josephson, N.C.1
Vassilopoulos, G.2
Trobridge, G.D.3
-
20
-
-
0742290135
-
Transduction of long-term and mobilized peripheral blood-derived NOD/SCID repopulating cells by foamy virus vectors
-
Josephson N.C., Trobridge G., Russell D.W. Transduction of long-term and mobilized peripheral blood-derived NOD/SCID repopulating cells by foamy virus vectors. Hum Gene Ther 2004, 15:87-92.
-
(2004)
Hum Gene Ther
, vol.15
, pp. 87-92
-
-
Josephson, N.C.1
Trobridge, G.2
Russell, D.W.3
-
21
-
-
77949424086
-
Dual transgene expression by foamy virus vectors carrying an endogenous bidirectional promoter
-
Andrianaki A., Siapati E.K., Hirata R.K., Russell D.W., Vassilopoulos G. Dual transgene expression by foamy virus vectors carrying an endogenous bidirectional promoter. Gene Ther 2010, 17:380-388.
-
(2010)
Gene Ther
, vol.17
, pp. 380-388
-
-
Andrianaki, A.1
Siapati, E.K.2
Hirata, R.K.3
Russell, D.W.4
Vassilopoulos, G.5
-
22
-
-
33846030431
-
Foamy-virus-mediated gene transfer to canine repopulating cells
-
Kiem H.P., Allen J., Trobridge G., et al. Foamy-virus-mediated gene transfer to canine repopulating cells. Blood 2007, 109:65-70.
-
(2007)
Blood
, vol.109
, pp. 65-70
-
-
Kiem, H.P.1
Allen, J.2
Trobridge, G.3
-
23
-
-
38049016006
-
Successful treatment of canine leukocyte adhesion deficiency by foamy virus vectors
-
Bauer T.R., Allen J.M., Hai M., et al. Successful treatment of canine leukocyte adhesion deficiency by foamy virus vectors. Nat Med 2008, 14:93-97.
-
(2008)
Nat Med
, vol.14
, pp. 93-97
-
-
Bauer, T.R.1
Allen, J.M.2
Hai, M.3
-
24
-
-
34249804819
-
Unique integration profiles in a canine model of long-term repopulating cells transduced with gammaretrovirus, lentivirus, or foamy virus
-
Beard B.C., Keyser K.A., Trobridge G.D., et al. Unique integration profiles in a canine model of long-term repopulating cells transduced with gammaretrovirus, lentivirus, or foamy virus. Hum Gene Ther 2007, 18:423-434.
-
(2007)
Hum Gene Ther
, vol.18
, pp. 423-434
-
-
Beard, B.C.1
Keyser, K.A.2
Trobridge, G.D.3
-
25
-
-
33646161948
-
Genome-wide mapping of foamy virus vector integrations into a human cell line
-
Nowrouzi A., Dittrich M., Klanke C., et al. Genome-wide mapping of foamy virus vector integrations into a human cell line. J Gen Virol 2006, 87:1339-1347.
-
(2006)
J Gen Virol
, vol.87
, pp. 1339-1347
-
-
Nowrouzi, A.1
Dittrich, M.2
Klanke, C.3
-
26
-
-
0036764805
-
Improved foamy virus vectors with minimal viral sequences
-
Trobridge G., Josephson N., Vassilopoulos G., Mac J., Russell D.W. Improved foamy virus vectors with minimal viral sequences. Mol Ther 2002, 6:321-328.
-
(2002)
Mol Ther
, vol.6
, pp. 321-328
-
-
Trobridge, G.1
Josephson, N.2
Vassilopoulos, G.3
Mac, J.4
Russell, D.W.5
-
28
-
-
0004136246
-
-
Cold Spring Harbor Laboratory Press, Plainview, NY
-
Sambrook J., Fritsch E.F., Maniatis T. Molecular Cloning: A Laboratory Manual 1989, Cold Spring Harbor Laboratory Press, Plainview, NY. 2nd ed.
-
(1989)
Molecular Cloning: A Laboratory Manual
-
-
Sambrook, J.1
Fritsch, E.F.2
Maniatis, T.3
-
29
-
-
0028893203
-
Mouse model of X-linked chronic granulomatous disease, an inherited defect in phagocyte superoxide production
-
Pollock J.D., Williams D.A., Gifford M.A., et al. Mouse model of X-linked chronic granulomatous disease, an inherited defect in phagocyte superoxide production. Nat Genet 1995, 9:202-209.
-
(1995)
Nat Genet
, vol.9
, pp. 202-209
-
-
Pollock, J.D.1
Williams, D.A.2
Gifford, M.A.3
-
30
-
-
33750003893
-
Human cell engraftment after busulfan or irradiation conditioning of NOD/SCID mice
-
Robert-Richard E., Ged C., Ortet J., et al. Human cell engraftment after busulfan or irradiation conditioning of NOD/SCID mice. Haematologica 2006, 91:1384-1387.
-
(2006)
Haematologica
, vol.91
, pp. 1384-1387
-
-
Robert-Richard, E.1
Ged, C.2
Ortet, J.3
-
31
-
-
0036713250
-
Engraftment assessment in human and mouse liver tissue after sex-mismatched liver cell transplantation by real time quantitative PCR for Y chromosome sequences
-
Wang L.J., Chen Y.M., George D., et al. Engraftment assessment in human and mouse liver tissue after sex-mismatched liver cell transplantation by real time quantitative PCR for Y chromosome sequences. Liver Transpl 2002, 8:822-828.
-
(2002)
Liver Transpl
, vol.8
, pp. 822-828
-
-
Wang, L.J.1
Chen, Y.M.2
George, D.3
-
32
-
-
0141889328
-
Concentrated RD114-pseudotyped MFGS-gp91phox vector achieves high levels of functional correction of the chronic granulomatous disease oxidase defect in NOD/SCID/beta -microglobulin-/- repopulating mobilized human peripheral blood CD34+ cells
-
Brenner S., Whiting-Theobald N.L., Linton G.F., et al. Concentrated RD114-pseudotyped MFGS-gp91phox vector achieves high levels of functional correction of the chronic granulomatous disease oxidase defect in NOD/SCID/beta -microglobulin-/- repopulating mobilized human peripheral blood CD34+ cells. Blood 2003, 102:2789-2797.
-
(2003)
Blood
, vol.102
, pp. 2789-2797
-
-
Brenner, S.1
Whiting-Theobald, N.L.2
Linton, G.F.3
-
33
-
-
52049101127
-
The usefulness of a perfect parasite
-
Vassilopoulos G., Rethwilm A. The usefulness of a perfect parasite. Gene Ther 2008, 15:1299-1301.
-
(2008)
Gene Ther
, vol.15
, pp. 1299-1301
-
-
Vassilopoulos, G.1
Rethwilm, A.2
-
34
-
-
7544248864
-
Stable long-term gene correction with low-dose radiation conditioning in murine X-linked chronic granulomatous disease
-
Goebel W.S., Pech N.K., Dinauer M.C. Stable long-term gene correction with low-dose radiation conditioning in murine X-linked chronic granulomatous disease. Blood Cells Mol Dis 2004, 33:365-371.
-
(2004)
Blood Cells Mol Dis
, vol.33
, pp. 365-371
-
-
Goebel, W.S.1
Pech, N.K.2
Dinauer, M.C.3
-
35
-
-
0029817964
-
High-level reconstitution of respiratory burst activity in a human X-linked chronic granulomatous disease (X-CGD) cell line and correction of murine X-CGD bone marrow cells by retroviral-mediated gene transfer of human gp91phox
-
Ding C., Kume A., Björgvinsdóttir H., Hawley R.G., Pech N., Dinauer M.C. High-level reconstitution of respiratory burst activity in a human X-linked chronic granulomatous disease (X-CGD) cell line and correction of murine X-CGD bone marrow cells by retroviral-mediated gene transfer of human gp91phox. Blood 1996, 88:1834-1840.
-
(1996)
Blood
, vol.88
, pp. 1834-1840
-
-
Ding, C.1
Kume, A.2
Björgvinsdóttir, H.3
Hawley, R.G.4
Pech, N.5
Dinauer, M.C.6
-
36
-
-
1842370351
-
Retroviral-mediated gene transfer of gp91phox into bone marrow cells rescues defect in host defense against Aspergillusfumigatus in murine X-linked chronic granulomatous disease
-
Björgvinsdóttir H., Ding C., Pech N., Gifford M.A., Li L.L., Dinauer M.C. Retroviral-mediated gene transfer of gp91phox into bone marrow cells rescues defect in host defense against Aspergillusfumigatus in murine X-linked chronic granulomatous disease. Blood 1997, 89:41-48.
-
(1997)
Blood
, vol.89
, pp. 41-48
-
-
Björgvinsdóttir, H.1
Ding, C.2
Pech, N.3
Gifford, M.A.4
Li, L.L.5
Dinauer, M.C.6
-
37
-
-
0344947883
-
Long-term correction of phagocyte NADPH oxidase activity by retroviral-mediated gene transfer in murine X-linked chronic granulomatous disease
-
Dinauer M.C., Li L.L., Björgvinsdóttir H., Ding C., Pech N. Long-term correction of phagocyte NADPH oxidase activity by retroviral-mediated gene transfer in murine X-linked chronic granulomatous disease. Blood 1999, 94:914-922.
-
(1999)
Blood
, vol.94
, pp. 914-922
-
-
Dinauer, M.C.1
Li, L.L.2
Björgvinsdóttir, H.3
Ding, C.4
Pech, N.5
-
38
-
-
0038407862
-
Long-term high-level reconstitution of NADPH oxidase activity in murine X-linked chronic granulomatous disease using a bicistronic vector expressing gp91phox and a Delta LNGFR cell surface marker
-
Sadat M.A., Pech N., Saulnier S., et al. Long-term high-level reconstitution of NADPH oxidase activity in murine X-linked chronic granulomatous disease using a bicistronic vector expressing gp91phox and a Delta LNGFR cell surface marker. Hum Gene Ther 2003, 14:651-666.
-
(2003)
Hum Gene Ther
, vol.14
, pp. 651-666
-
-
Sadat, M.A.1
Pech, N.2
Saulnier, S.3
|