Novel compounds for the treatment of Duchenne muscular dystrophy: Emerging therapeutic agents

Application of Clinical Genetics

Volumn 4, Issue , 2011, Pages 29-44

  Wilton, Steve D ^a   Fletcher, Sue ^a  

^a UNIVERSITY OF WESTERN AUSTRALIA   (Australia)

Author keywords

Duchenne muscular dystrophy; Molecular therapeutics; Small molecules

Indexed keywords

ACE 031; AGENTS ACTING ON THE PERIPHERAL NERVOUS AND NEUROMUSCULAR SYSTEMS; ANTISENSE OLIGOMER; ATALUREN; AVI 4658; CELL PENETRATING PEPTIDE PHOSPHORODIAMIDATE MORPHOLINO OLIGOMER CONJUGATE; COPOLYMER; CORTICOSTEROID; DEOXYRIBONUCLEOTIDE; DYSTROPHIN; FOLLISTATIN; GENTAMICIN; IDEBENONE; LIPOSOME; LISINOPRIL; MUSCLE RELAXANT AGENT; MYOSTATIN; NANOPARTICLE; OLIGOMER; PHOSPHORODIAMIDATE MORPHOLINO OLIGOMER; PLACEBO; POLYMER; PREDNISONE; PRO 051; SOMATOMEDIN C; TADALAFIL; UBIDECARENONE; UNCLASSIFIED DRUG;

ABSENCE OF SIDE EFFECTS; BECKER MUSCULAR DYSTROPHY; DOSAGE SCHEDULE COMPARISON; DOSE RESPONSE; DRUG DELIVERY SYSTEM; DRUG DOSE ESCALATION; DRUG EFFICACY; DRUG MECHANISM; DRUG MEGADOSE; DRUG SAFETY; DRUG SCREENING; DRUG TOLERABILITY; DUCHENNE MUSCULAR DYSTROPHY; HEART DISEASE; HUMAN; LOW DRUG DOSE; MOLECULAR THERAPY; MUSCLE FUNCTION; NONHUMAN; PATHOPHYSIOLOGY; REVIEW; SINGLE DRUG DOSE; UNSPECIFIED SIDE EFFECT;

EID: 79953148068     PISSN: 1178704X     EISSN: None     Source Type: Journal    
DOI: 10.2147/TACG.S8762     Document Type: Review

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