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Volumn 17, Issue 5, 2007, Pages 423-428

145th ENMC International Workshop: Planning for an International Trial of Steroid Dosage Regimes in DMD (FOR DMD) 22-24th October 2006, Naarden, The Netherlands

Author keywords

[No Author keywords available]

Indexed keywords

BISPHOSPHONIC ACID DERIVATIVE; CORTICOSTEROID; DEFLAZACORT; MYOSTATIN; PREDNISONE; UTROPHIN;

EID: 34247584629     PISSN: 09608966     EISSN: None     Source Type: Journal    
DOI: 10.1016/j.nmd.2007.01.006     Document Type: Article
Times cited : (19)

References (31)
  • 1
    • 4344588135 scopus 로고    scopus 로고
    • Bushby K, Muntoni F, et al. (2004). Report on the 124th ENMC International Workshop. Treatment of Duchenne muscular dystrophy; defining the gold standards of management in the uses of corticosteroids. 2-4 April 2004, Naarden, The Netherlands. Neuromusc Disord 14(8-9):526-34.
  • 2
    • 3843121117 scopus 로고    scopus 로고
    • Glucocorticoid corticosteroids for Duchenne muscular dystrophy
    • Manzur A.Y., Kuntzer T., et al. Glucocorticoid corticosteroids for Duchenne muscular dystrophy. Cochrane Database Syst Rev 2 (2004) CD003725
    • (2004) Cochrane Database Syst Rev , Issue.2
    • Manzur, A.Y.1    Kuntzer, T.2
  • 3
    • 19944427852 scopus 로고    scopus 로고
    • Corticosteroid treatment of Duchenne dystrophy [Report of the Quality standards Subcommittee of the American Academy of Neurology and the Practice Committee of the Child Neurology Society]
    • Moxley R.T., Ashwal S., et al. Corticosteroid treatment of Duchenne dystrophy [Report of the Quality standards Subcommittee of the American Academy of Neurology and the Practice Committee of the Child Neurology Society]. Neurology 64 1 (2005) 13-20
    • (2005) Neurology , vol.64 , Issue.1 , pp. 13-20
    • Moxley, R.T.1    Ashwal, S.2
  • 4
    • 0037443583 scopus 로고    scopus 로고
    • Effects of deflazacort on left ventricular function in patients with Duchenne muscular dystrophy
    • Silversides C.K., Webb G.D., et al. Effects of deflazacort on left ventricular function in patients with Duchenne muscular dystrophy. Am J Cardiol 91 6 (2003) 769-772
    • (2003) Am J Cardiol , vol.91 , Issue.6 , pp. 769-772
    • Silversides, C.K.1    Webb, G.D.2
  • 5
    • 4344702443 scopus 로고    scopus 로고
    • Deflazacort in Duchenne muscular dystrophy: a comparison of two different protocols
    • Biggar W.D., Politano L., et al. Deflazacort in Duchenne muscular dystrophy: a comparison of two different protocols. Neuromuscul Disord 14 8-9 (2004) 476-482
    • (2004) Neuromuscul Disord , vol.14 , Issue.8-9 , pp. 476-482
    • Biggar, W.D.1    Politano, L.2
  • 6
    • 33646478253 scopus 로고    scopus 로고
    • Long-term benefits of deflazacort treatment for boys with Duchenne muscular dystrophy in their second decade
    • Biggar W.D., Harris V.A., et al. Long-term benefits of deflazacort treatment for boys with Duchenne muscular dystrophy in their second decade. Neuromuscul Disord 16 4 (2006) 249-255
    • (2006) Neuromuscul Disord , vol.16 , Issue.4 , pp. 249-255
    • Biggar, W.D.1    Harris, V.A.2
  • 7
    • 6344289543 scopus 로고    scopus 로고
    • Naked plasmid DNA for the treatment of muscular dystrophy
    • Braun S. Naked plasmid DNA for the treatment of muscular dystrophy. Curr Opin Mol Ther 6 5 (2004) 499-505
    • (2004) Curr Opin Mol Ther , vol.6 , Issue.5 , pp. 499-505
    • Braun, S.1
  • 8
    • 10044240371 scopus 로고    scopus 로고
    • Rescue of dystrophic muscle through U7 snRNA-mediated exon skipping
    • Goyenvalle A., Vulin A., et al. Rescue of dystrophic muscle through U7 snRNA-mediated exon skipping. Science 306 5702 (2004) 1796-1799
    • (2004) Science , vol.306 , Issue.5702 , pp. 1796-1799
    • Goyenvalle, A.1    Vulin, A.2
  • 9
    • 7544232737 scopus 로고    scopus 로고
    • Utrophin therapy for Duchenne muscular dystrophy?
    • Nelson R. Utrophin therapy for Duchenne muscular dystrophy?. Lancet Neurol 3 11 (2004) 637
    • (2004) Lancet Neurol , vol.3 , Issue.11 , pp. 637
    • Nelson, R.1
  • 10
    • 6344263893 scopus 로고    scopus 로고
    • Phase I study of dystrophin plasmid-based gene therapy in Duchenne/Becker muscular dystrophy
    • Romero N.B., Braun S., et al. Phase I study of dystrophin plasmid-based gene therapy in Duchenne/Becker muscular dystrophy. Hum Gene Ther 15 11 (2004) 1065-1076
    • (2004) Hum Gene Ther , vol.15 , Issue.11 , pp. 1065-1076
    • Romero, N.B.1    Braun, S.2
  • 11
    • 23444460999 scopus 로고    scopus 로고
    • [About a phase I gene therapy clinical trial with a full-length dystrophin gene-plasmid in Duchenne/Becker muscular dystrophy]
    • Fardeau M., Braun S., et al. [About a phase I gene therapy clinical trial with a full-length dystrophin gene-plasmid in Duchenne/Becker muscular dystrophy]. J Soc Biol 199 1 (2005) 29-32
    • (2005) J Soc Biol , vol.199 , Issue.1 , pp. 29-32
    • Fardeau, M.1    Braun, S.2
  • 12
    • 33645355101 scopus 로고    scopus 로고
    • Utrophin upregulation in Duchenne muscular dystrophy
    • Hirst R.C., McCullagh K.J., et al. Utrophin upregulation in Duchenne muscular dystrophy. Acta Myol 24 3 (2005) 209-216
    • (2005) Acta Myol , vol.24 , Issue.3 , pp. 209-216
    • Hirst, R.C.1    McCullagh, K.J.2
  • 13
    • 12744269885 scopus 로고    scopus 로고
    • Adeno-associated virus-mediated microdystrophin expression protects young mdx muscle from contraction-induced injury
    • Liu M., Yue Y., et al. Adeno-associated virus-mediated microdystrophin expression protects young mdx muscle from contraction-induced injury. Mol Ther 11 2 (2005) 245-256
    • (2005) Mol Ther , vol.11 , Issue.2 , pp. 245-256
    • Liu, M.1    Yue, Y.2
  • 14
    • 32244443828 scopus 로고    scopus 로고
    • Systemic delivery of morpholino oligonucleotide restores dystrophin expression bodywide and improves dystrophic pathology
    • Alter J., Lou F., et al. Systemic delivery of morpholino oligonucleotide restores dystrophin expression bodywide and improves dystrophic pathology. Nat Med 12 2 (2006) 175-177
    • (2006) Nat Med , vol.12 , Issue.2 , pp. 175-177
    • Alter, J.1    Lou, F.2
  • 15
    • 34247612191 scopus 로고    scopus 로고
    • Multiexon skipping leading to an artificial DMD protein lacking amino acids from exons 45 through 55 could rescue up to 63% of patients with Duchenne muscular dystrophy
    • Beroud C., Tuffery-Giraud S., et al. Multiexon skipping leading to an artificial DMD protein lacking amino acids from exons 45 through 55 could rescue up to 63% of patients with Duchenne muscular dystrophy. Hum Mutat (2006)
    • (2006) Hum Mutat
    • Beroud, C.1    Tuffery-Giraud, S.2
  • 16
    • 32844460899 scopus 로고    scopus 로고
    • Dystrophin expression in the mdx mouse after localised and systemic administration of a morpholino antisense oligonucleotide
    • Fletcher S., Honeyman K., et al. Dystrophin expression in the mdx mouse after localised and systemic administration of a morpholino antisense oligonucleotide. J Gene Med 8 2 (2006) 207-216
    • (2006) J Gene Med , vol.8 , Issue.2 , pp. 207-216
    • Fletcher, S.1    Honeyman, K.2
  • 17
    • 33745894322 scopus 로고    scopus 로고
    • rAAV6-microdystrophin preserves muscle function and extends lifespan in severely dystrophic mice
    • Gregorevic P., Allen J.M., et al. rAAV6-microdystrophin preserves muscle function and extends lifespan in severely dystrophic mice. Nat Med 12 7 (2006) 787-789
    • (2006) Nat Med , vol.12 , Issue.7 , pp. 787-789
    • Gregorevic, P.1    Allen, J.M.2
  • 18
    • 33751064254 scopus 로고    scopus 로고
    • Drug evaluation: PTC-124 - a potential treatment of cystic fibrosis and Duchenne muscular dystrophy
    • Hamed S.A. Drug evaluation: PTC-124 - a potential treatment of cystic fibrosis and Duchenne muscular dystrophy. IDrugs 9 11 (2006) 783-789
    • (2006) IDrugs , vol.9 , Issue.11 , pp. 783-789
    • Hamed, S.A.1
  • 19
    • 33644975603 scopus 로고    scopus 로고
    • Utrophin upregulation for treating Duchenne or Becker muscular dystrophy: how close are we?
    • Miura P., and Jasmin B.J. Utrophin upregulation for treating Duchenne or Becker muscular dystrophy: how close are we?. Trends Mol Med 12 3 (2006) 122-129
    • (2006) Trends Mol Med , vol.12 , Issue.3 , pp. 122-129
    • Miura, P.1    Jasmin, B.J.2
  • 20
    • 33845257119 scopus 로고    scopus 로고
    • Mesoangioblast stem cells ameliorate muscle function in dystrophic dogs
    • Sampaolesi M., Blot S., et al. Mesoangioblast stem cells ameliorate muscle function in dystrophic dogs. Nature (2006)
    • (2006) Nature
    • Sampaolesi, M.1    Blot, S.2
  • 21
    • 34247585376 scopus 로고    scopus 로고
    • Redirecting splicing to address dystrophin mutations: molecular by-pass surgery
    • Wilton S.D., and Fletcher S. Redirecting splicing to address dystrophin mutations: molecular by-pass surgery. Prog Mol Subcell Biol 44 (2006) 161-197
    • (2006) Prog Mol Subcell Biol , vol.44 , pp. 161-197
    • Wilton, S.D.1    Fletcher, S.2
  • 22
    • 0037191752 scopus 로고    scopus 로고
    • Functional improvement of dystrophic muscle by myostatin blockade
    • Bogdanovich S., Krag T.O., et al. Functional improvement of dystrophic muscle by myostatin blockade. Nature 420 6914 (2002) 418-421
    • (2002) Nature , vol.420 , Issue.6914 , pp. 418-421
    • Bogdanovich, S.1    Krag, T.O.2
  • 23
    • 16344375071 scopus 로고    scopus 로고
    • Myostatin propeptide-mediated amelioration of dystrophic pathophysiology
    • Bogdanovich S., Perkins K.J., et al. Myostatin propeptide-mediated amelioration of dystrophic pathophysiology. FASEB J 19 6 (2005) 543-549
    • (2005) FASEB J , vol.19 , Issue.6 , pp. 543-549
    • Bogdanovich, S.1    Perkins, K.J.2
  • 24
    • 0037462964 scopus 로고    scopus 로고
    • Inhibition of myostatin in adult mice increases skeletal muscle mass and strength
    • Whittemore L.A., Song K., et al. Inhibition of myostatin in adult mice increases skeletal muscle mass and strength. Biochem Biophys Res Commun 300 4 (2003) 965-971
    • (2003) Biochem Biophys Res Commun , vol.300 , Issue.4 , pp. 965-971
    • Whittemore, L.A.1    Song, K.2
  • 25
    • 4243119542 scopus 로고    scopus 로고
    • Validation of a general measure of treatment satisfaction, the Treatment Satisfaction Questionnaire for Medication (TSQM), using a national panel study of chronic disease
    • Atkinson M.J., Sinah A., et al. Validation of a general measure of treatment satisfaction, the Treatment Satisfaction Questionnaire for Medication (TSQM), using a national panel study of chronic disease. Health Quality Life Outcomes 2 12 (2004)
    • (2004) Health Quality Life Outcomes , vol.2 , Issue.12
    • Atkinson, M.J.1    Sinah, A.2
  • 26
    • 33646672126 scopus 로고    scopus 로고
    • Measurement in Duchenne muscular dystrophy: considerations in the development of a neuromuscular assessment tool
    • Scott E., and Mawson S.J. Measurement in Duchenne muscular dystrophy: considerations in the development of a neuromuscular assessment tool. Dev Med Child Neurol 48 6 (2006) 540-544
    • (2006) Dev Med Child Neurol , vol.48 , Issue.6 , pp. 540-544
    • Scott, E.1    Mawson, S.J.2
  • 27
    • 0142055132 scopus 로고    scopus 로고
    • Bone mineral density in Duchenne muscular dystrophy
    • Bianchi M.L., Mazzanti A., et al. Bone mineral density in Duchenne muscular dystrophy. Osteoporosis Int 14 (2003) 761-767
    • (2003) Osteoporosis Int , vol.14 , pp. 761-767
    • Bianchi, M.L.1    Mazzanti, A.2
  • 28
    • 15044356774 scopus 로고    scopus 로고
    • Biggar LK, Bachrach RC, et al. (2005). Bone health in Duchenne muscular dystrophy: a workshop report from the meeting in Cincinnati, Ohio, July 8, 2004. Neuromuscul Disord 15(1):80-5.
  • 29
    • 15044360059 scopus 로고    scopus 로고
    • Report of a Muscular Dystrophy Campaign funded workshop Birmingham, UK, January 16th 2004. Osteoporosis in Duchenne muscular dystrophy; its prevalence, treatment and prevention. [see comment]
    • Quinlivan R., Roper H., et al. Report of a Muscular Dystrophy Campaign funded workshop Birmingham, UK, January 16th 2004. Osteoporosis in Duchenne muscular dystrophy; its prevalence, treatment and prevention. [see comment]. Neuromuscul Disord 15 1 (2005) 72-79
    • (2005) Neuromuscul Disord , vol.15 , Issue.1 , pp. 72-79
    • Quinlivan, R.1    Roper, H.2
  • 30
    • 0037304994 scopus 로고    scopus 로고
    • Bushby KMD, Muntoni F, et al. (2003). The management of cardiac complications in muscular dystrophy and myotonic dystrophy. In: Proceedings of 107th ENMC Workshop, Neuromuscul Disord, vol. 13. p. 166-172.
  • 31
    • 4544272373 scopus 로고    scopus 로고
    • Respiratory care of the patient with Duchenne muscular dystrophy: ATS consensus statement
    • Finder J.D., Birnkrant D., et al. Respiratory care of the patient with Duchenne muscular dystrophy: ATS consensus statement. Am J Respir Crit Care Med 170 4 (2004) 456-465
    • (2004) Am J Respir Crit Care Med , vol.170 , Issue.4 , pp. 456-465
    • Finder, J.D.1    Birnkrant, D.2


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