-
1
-
-
0025887093
-
Human dystrophin expression in mdx mice after intramuscular injection of DNA constructs
-
Acsadi G, Dickson G, Love DR, Jani A, Walsh FS, Gurusinghe A, et al. Human dystrophin expression in mdx mice after intramuscular injection of DNA constructs. Nature 1991;352:815-818.
-
(1991)
Nature
, vol.352
, pp. 815-818
-
-
Acsadi, G.1
Dickson, G.2
Love, D.R.3
Jani, A.4
Walsh, F.S.5
Gurusinghe, A.6
-
2
-
-
0031753867
-
Gene transfer into muscle by electroporation in vivo
-
Aihara H, Miyazaki J. Gene transfer into muscle by electroporation in vivo. Nat Biotechnol 1998;16:867-870.
-
(1998)
Nat Biotechnol
, vol.16
, pp. 867-870
-
-
Aihara, H.1
Miyazaki, J.2
-
3
-
-
13044257108
-
High-efficiency gene transfer into skeletal muscle mediated by electric pulses
-
Mir LM, Bureau MF, Gehl J, Rangara R, Rouy D, Caillaud JM, et al. High-efficiency gene transfer into skeletal muscle mediated by electric pulses. Proc Natl Acad Sci U S A 1999;96:4262-4267.
-
(1999)
Proc Natl Acad Sci U S A
, vol.96
, pp. 4262-4267
-
-
Mir, L.M.1
Bureau, M.F.2
Gehl, J.3
Rangara, R.4
Rouy, D.5
Caillaud, J.M.6
-
4
-
-
4644275773
-
In vivo gene electrotransfer into skeletal muscle: Effects of plasmid DNA on the occurrence and extent of muscle damage
-
Durieux AC, Bonnefoy R, Busso T, Freyssenet D. In vivo gene electrotransfer into skeletal muscle: effects of plasmid DNA on the occurrence and extent of muscle damage. J Gene Med 2004;6:809-816.
-
(2004)
J Gene Med
, vol.6
, pp. 809-816
-
-
Durieux, A.C.1
Bonnefoy, R.2
Busso, T.3
Freyssenet, D.4
-
5
-
-
4444279151
-
Factors influencing the efficacy, longevity, and safety of electroporation-assisted plasmid-based gene transfer into mouse muscles
-
Molnar MJ, Gilbert R, Lu Y, Liu AB, Guo A, Larochelle N, et al. Factors influencing the efficacy, longevity, and safety of electroporation-assisted plasmid-based gene transfer into mouse muscles. Mol Ther 2004;10:447-455.
-
(2004)
Mol Ther
, vol.10
, pp. 447-455
-
-
Molnar, M.J.1
Gilbert, R.2
Lu, Y.3
Liu, A.B.4
Guo, A.5
Larochelle, N.6
-
6
-
-
0034787753
-
Electrotransfer of naked DNA in the skeletal muscles of animal models of muscular dystrophies
-
Vilquin JT, Kennel PF, Paturneau-Jouas M, Chapdelaine P, Boissel N, Delaère P, et al. Electrotransfer of naked DNA in the skeletal muscles of animal models of muscular dystrophies. Gene Ther 2001;8:1097-1107.
-
(2001)
Gene Ther
, vol.8
, pp. 1097-1107
-
-
Vilquin, J.T.1
Kennel, P.F.2
Paturneau-Jouas, M.3
Chapdelaine, P.4
Boissel, N.5
Delaère, P.6
-
7
-
-
0037309533
-
Full-length dystrophin cDNA transfer into skeletal muscle of adult mdx mice by electroporation
-
Murakami T, Nishi T, Kimura E, Goto T, Maeda Y, Ushio Y, et al. Full-length dystrophin cDNA transfer into skeletal muscle of adult mdx mice by electroporation. Muscle Nerve 2003;27:237-241.
-
(2003)
Muscle Nerve
, vol.27
, pp. 237-241
-
-
Murakami, T.1
Nishi, T.2
Kimura, E.3
Goto, T.4
Maeda, Y.5
Ushio, Y.6
-
8
-
-
0034893580
-
Optimisation of electrotransfer of plasmid into skeletal muscle by pretreatment with hyaluronidase--increased expression with reduced muscle damage
-
McMahon JM, Signori E, Wells KE, Fazio VM, Wells DJ. Optimisation of electrotransfer of plasmid into skeletal muscle by pretreatment with hyaluronidase--increased expression with reduced muscle damage. Gene Ther 2001;8:1264-1270.
-
(2001)
Gene Ther
, vol.8
, pp. 1264-1270
-
-
McMahon, J.M.1
Signori, E.2
Wells, K.E.3
Fazio, V.M.4
Wells, D.J.5
-
9
-
-
0036207351
-
Hyaluronidase increases electrogene transfer efficiency in skeletal muscle
-
Mennuni C, Calvaruso F, Zampaglione I, Rizzuto G, Rinaudo D, Dammassa E, et al. Hyaluronidase increases electrogene transfer efficiency in skeletal muscle. Hum Gene Ther 2002;13:355-365.
-
(2002)
Hum Gene Ther
, vol.13
, pp. 355-365
-
-
Mennuni, C.1
Calvaruso, F.2
Zampaglione, I.3
Rizzuto, G.4
Rinaudo, D.5
Dammassa, E.6
-
10
-
-
0031935395
-
The efficient expression of intravascularly delivered DNA in rat muscle
-
Budker V, Zhang G, Danko I, Williams P, Wolff J. The efficient expression of intravascularly delivered DNA in rat muscle. Gene Ther 1998; 5:272-276.
-
(1998)
Gene Ther
, vol.5
, pp. 272-276
-
-
Budker, V.1
Zhang, G.2
Danko, I.3
Williams, P.4
Wolff, J.5
-
11
-
-
4143091589
-
Intraarterial delivery of naked plasmid DNA expressing full-length mouse dystrophin in the mdx mouse model of duchenne muscular dystrophy
-
Zhang G, Ludtke JJ, Thioudellet C, Kleinpeter P, Antoniou M, Herweijer H, et al. Intraarterial delivery of naked plasmid DNA expressing full-length mouse dystrophin in the mdx mouse model of duchenne muscular dystrophy. Hum Gene Ther 2004;15:770-782.
-
(2004)
Hum Gene Ther
, vol.15
, pp. 770-782
-
-
Zhang, G.1
Ludtke, J.J.2
Thioudellet, C.3
Kleinpeter, P.4
Antoniou, M.5
Herweijer, H.6
-
12
-
-
4344715026
-
A facile nonviral method for delivering genes and siRNAs to skeletal muscle of mammalian limbs
-
Hagstrom JE, Hegge J, Zhang G, Noble M, Budker V, Lewis DL, et al. A facile nonviral method for delivering genes and siRNAs to skeletal muscle of mammalian limbs. Mol Ther 2004;10:386-398.
-
(2004)
Mol Ther
, vol.10
, pp. 386-398
-
-
Hagstrom, J.E.1
Hegge, J.2
Zhang, G.3
Noble, M.4
Budker, V.5
Lewis, D.L.6
-
13
-
-
6344263893
-
Phase I study of dystrophin plasmid-based gene therapy in Duchenne/Becker muscular dystrophy
-
Romero NB, Braun S, Benveniste O, Leturcq F, Hogrel JY, Morris GE, et al. Phase I study of dystrophin plasmid-based gene therapy in Duchenne/Becker muscular dystrophy. Hum Gene Ther 2004;15: 1065-1076.
-
(2004)
Hum Gene Ther
, vol.15
, pp. 1065-1076
-
-
Romero, N.B.1
Braun, S.2
Benveniste, O.3
Leturcq, F.4
Hogrel, J.Y.5
Morris, G.E.6
-
14
-
-
0036790998
-
Functional correction of adult mdx mouse muscle using gutted adenoviral vectors expressing fulll-ength dystrophin
-
DelloRusso C, Scott JM, Hartigan-O'Connor D, Salvatori G, Barjot C, Robinson AS, et al. Functional correction of adult mdx mouse muscle using gutted adenoviral vectors expressing fulll-ength dystrophin. Proc Natl Acad Sci U S A 2002;99:12979-12984.
-
(2002)
Proc Natl Acad Sci U S A
, vol.99
, pp. 12979-12984
-
-
DelloRusso, C.1
Scott, J.M.2
Hartigan-O'Connor, D.3
Salvatori, G.4
Barjot, C.5
Robinson, A.S.6
-
15
-
-
0033543994
-
Gene transfer into the liver of nonhuman primates with E1-deleted recombinant adenoviral vectors: Safety of readministration
-
Nunes FA, Furth EE, Wilson JM, Raper SE. Gene transfer into the liver of nonhuman primates with E1-deleted recombinant adenoviral vectors: safety of readministration. Hum Gene Ther 1999;10:2515-2526.
-
(1999)
Hum Gene Ther
, vol.10
, pp. 2515-2526
-
-
Nunes, F.A.1
Furth, E.E.2
Wilson, J.M.3
Raper, S.E.4
-
16
-
-
0031969428
-
Transduction of dendritic cells by DNA viral vectors directs the immune response to transgene products in muscle fibers
-
Jooss K, Yang Y, Fisher KJ, Wilson JM. Transduction of dendritic cells by DNA viral vectors directs the immune response to transgene products in muscle fibers. J Virol 1998;72:4212-4223.
-
(1998)
J Virol
, vol.72
, pp. 4212-4223
-
-
Jooss, K.1
Yang, Y.2
Fisher, K.J.3
Wilson, J.M.4
-
17
-
-
0034610364
-
Adeno-associated virus vector carrying human minidystrophin genes effectively ameliorates muscular dystrophy in mdx mouse model
-
Wang B, Li J, Xiao X. Adeno-associated virus vector carrying human minidystrophin genes effectively ameliorates muscular dystrophy in mdx mouse model. Proc Natl Acad Sci U S A 2000;97:13714-13719.
-
(2000)
Proc Natl Acad Sci U S A
, vol.97
, pp. 13714-13719
-
-
Wang, B.1
Li, J.2
Xiao, X.3
-
18
-
-
7044253593
-
AAV vector-mediated microdystrophin expression in a relatively small percentage of mdx myofibers improved the mdx phenotype
-
Yoshimura M, Sakamoto M, Ikemoto M, Mochizuki Y, Yuasa K, Miyagoe-Suzuki Y, et al. AAV vector-mediated microdystrophin expression in a relatively small percentage of mdx myofibers improved the mdx phenotype. Mol Ther 2004;10:821-828.
-
(2004)
Mol Ther
, vol.10
, pp. 821-828
-
-
Yoshimura, M.1
Sakamoto, M.2
Ikemoto, M.3
Mochizuki, Y.4
Yuasa, K.5
Miyagoe-Suzuki, Y.6
-
19
-
-
4043092073
-
Systemic delivery of genes to striated muscles using adeno-associated viral vectors
-
Gregorevic P, Blankinship MJ, Allen JM, Crawford RW, Meuse L, Miller DG, et al. Systemic delivery of genes to striated muscles using adeno-associated viral vectors. Nat Med 2004;10:828-834.
-
(2004)
Nat Med
, vol.10
, pp. 828-834
-
-
Gregorevic, P.1
Blankinship, M.J.2
Allen, J.M.3
Crawford, R.W.4
Meuse, L.5
Miller, D.G.6
-
20
-
-
50549085053
-
Lack of toxicity of alpha-sarcoglycan overexpression supports clinical gene transfer trial in LGMD2D
-
Rodino-Klapac LR, Lee JS, Mulligan RC, Clark KR, Mendell JR. Lack of toxicity of alpha-sarcoglycan overexpression supports clinical gene transfer trial in LGMD2D. Neurology 2008;71:240-247.
-
(2008)
Neurology
, vol.71
, pp. 240-247
-
-
Rodino-Klapac, L.R.1
Lee, J.S.2
Mulligan, R.C.3
Clark, K.R.4
Mendell, J.R.5
-
21
-
-
0036892308
-
Adeno-associated virus vector-mediated gene transfer into dystrophin-deficient skeletal muscles evokes enhanced immune response against the transgene product
-
Yuasa K, Sakamoto M, Miyagoe-Suzuki Y, Tanouchi A, Yamamoto H, Li J, et al. Adeno-associated virus vector-mediated gene transfer into dystrophin-deficient skeletal muscles evokes enhanced immune response against the transgene product. Gene Ther 2002;9:1576-1588.
-
(2002)
Gene Ther
, vol.9
, pp. 1576-1588
-
-
Yuasa, K.1
Sakamoto, M.2
Miyagoe-Suzuki, Y.3
Tanouchi, A.4
Yamamoto, H.5
Li, J.6
-
22
-
-
33747584384
-
Long-term expression and repeated administration of AAV type 1, 2 and 5 vectors in skeletal muscle of immunocompetent adult mice
-
Rivière C, Danos O, Douar AM. Long-term expression and repeated administration of AAV type 1, 2 and 5 vectors in skeletal muscle of immunocompetent adult mice. Gene Ther 2006;13:1300-1308.
-
(2006)
Gene Ther
, vol.13
, pp. 1300-1308
-
-
Rivière, C.1
Danos, O.2
Douar, A.M.3
-
23
-
-
33745894322
-
RAAV6-microdystrophin preserves muscle function and extends lifespan in severely dystrophic mice
-
Gregorevic P, Allen JM, Minami E, Blankinship MJ, Haraguchi M, Meuse L, et al. rAAV6-microdystrophin preserves muscle function and extends lifespan in severely dystrophic mice. Nat Med 2006;12:787-789.
-
(2006)
Nat Med
, vol.12
, pp. 787-789
-
-
Gregorevic, P.1
Allen, J.M.2
Minami, E.3
Blankinship, M.J.4
Haraguchi, M.5
Meuse, L.6
-
24
-
-
33745143956
-
Robust systemic transduction with AAV9 vectors in mice: Efficient global cardiac gene transfer superior to that of AAV8
-
Inagaki K, Fuess S, Storm TA, Gibson GA, Mctiernan CF, Kay MA, et al. Robust systemic transduction with AAV9 vectors in mice: efficient global cardiac gene transfer superior to that of AAV8. Mol Ther 2006;14:45-53.
-
(2006)
Mol Ther
, vol.14
, pp. 45-53
-
-
Inagaki, K.1
Fuess, S.2
Storm, T.A.3
Gibson, G.A.4
McTiernan, C.F.5
Kay, M.A.6
-
25
-
-
70350067897
-
Limb-girdle muscular dystrophy type 2D gene therapy restores alpha-sarcoglycan and associated proteins
-
Mendell JR, Rodino-Klapac LR, Rosales-Quintero X, Kota J, Coley BD, Galloway G, et al. Limb-girdle muscular dystrophy type 2D gene therapy restores alpha-sarcoglycan and associated proteins. Ann Neurol 2009;66:290-297.
-
(2009)
Ann Neurol
, vol.66
, pp. 290-297
-
-
Mendell, J.R.1
Rodino-Klapac, L.R.2
Rosales-Quintero, X.3
Kota, J.4
Coley, B.D.5
Galloway, G.6
-
26
-
-
0032924996
-
rAAV vector-mediated sarcogylcan gene transfer in a hamster model for limb girdle muscular dystrophy
-
Li J, Dressman D, Tsao YP, Sakamoto A, Hoffman EP, Xiao X. rAAV vector-mediated sarcogylcan gene transfer in a hamster model for limb girdle muscular dystrophy. Gene Ther 1999;6:74-82.
-
(1999)
Gene Ther
, vol.6
, pp. 74-82
-
-
Li, J.1
Dressman, D.2
Tsao, Y.P.3
Sakamoto, A.4
Hoffman, E.P.5
Xiao, X.6
-
27
-
-
0023718118
-
An explanation for the phenotypic differences between patients bearing partial deletions of the DMD locus
-
Monaco AP, Bertelson CJ, Liechti-Gallati S, Moser H, Kunkel LM. An explanation for the phenotypic differences between patients bearing partial deletions of the DMD locus. Genomics 1988;2:90-95.
-
(1988)
Genomics
, vol.2
, pp. 90-95
-
-
Monaco, A.P.1
Bertelson, C.J.2
Liechti-Gallati, S.3
Moser, H.4
Kunkel, L.M.5
-
28
-
-
0031800293
-
Modification of splicing in the dystrophin gene in cultured Mdx muscle cells by antisense oligoribonucleotides
-
Dunckley MG, Manoharan M, Villiet P, Eperon IC, Dickson G. Modification of splicing in the dystrophin gene in cultured Mdx muscle cells by antisense oligoribonucleotides. Hum Mol Genet 1998;7: 1083-1090.
-
(1998)
Hum Mol Genet
, vol.7
, pp. 1083-1090
-
-
Dunckley, M.G.1
Manoharan, M.2
Villiet, P.3
Eperon, I.C.4
Dickson, G.5
-
29
-
-
0035793047
-
Antisense-induced exon skipping and synthesis of dystrophin in the mdx mouse
-
Mann CJ, Honeyman K, Cheng AJ, Ly T, Lloyd F, Fletcher S, et al. Antisense-induced exon skipping and synthesis of dystrophin in the mdx mouse. Proc Natl Acad Sci U S A 2001;98:42-47.
-
(2001)
Proc Natl Acad Sci U S A
, vol.98
, pp. 42-47
-
-
Mann, C.J.1
Honeyman, K.2
Cheng, A.J.3
Ly, T.4
Lloyd, F.5
Fletcher, S.6
-
30
-
-
32244443828
-
Systemic delivery of morpholino oligonucleotide restores dystrophin expression bodywide and improves dystrophic pathology
-
Alter J, Lou F, Rabinowitz A, Yin H, Rosenfeld J, Wilton SD, et al. Systemic delivery of morpholino oligonucleotide restores dystrophin expression bodywide and improves dystrophic pathology. Nat Med 2006;12:175-177.
-
(2006)
Nat Med
, vol.12
, pp. 175-177
-
-
Alter, J.1
Lou, F.2
Rabinowitz, A.3
Yin, H.4
Rosenfeld, J.5
Wilton, S.D.6
-
31
-
-
0042536463
-
Functional amounts of dystrophin produced by skipping the mutated exon in the mdx dystrophic mouse
-
Lu QL, Mann CJ, Lou F, Bou-Gharios G, Morris GE, Xue SA, et al. Functional amounts of dystrophin produced by skipping the mutated exon in the mdx dystrophic mouse. Nat Med 2003;9:1009-1014.
-
(2003)
Nat Med
, vol.9
, pp. 1009-1014
-
-
Lu, Q.L.1
Mann, C.J.2
Lou, F.3
Bou-Gharios, G.4
Morris, G.E.5
Xue, S.A.6
-
32
-
-
0141760549
-
Enhanced in vivo delivery of antisense oligonucleotides to restore dystrophin expression in adult mdx mouse muscle
-
Wells KE, Fletcher S, Mann CJ, Wilton SD, Wells DJ. Enhanced in vivo delivery of antisense oligonucleotides to restore dystrophin expression in adult mdx mouse muscle. FEBS Lett 2003;552:145-149.
-
(2003)
FEBS Lett
, vol.552
, pp. 145-149
-
-
Wells, K.E.1
Fletcher, S.2
Mann, C.J.3
Wilton, S.D.4
Wells, D.J.5
-
33
-
-
4344693568
-
Targeted exon skipping in transgenic hDMD mice: A model for direct preclinical screening of human-specific antisense oligonucleotides
-
Bremmer-Bout M, Aartsma-Rus A, de Meijer EJ, Kaman WE, Janson AA, Vossen RH, et al. Targeted exon skipping in transgenic hDMD mice: a model for direct preclinical screening of human-specific antisense oligonucleotides. Mol Ther 2004;10:232-240.
-
(2004)
Mol Ther
, vol.10
, pp. 232-240
-
-
Bremmer-Bout, M.1
Aartsma-Rus, A.2
de Meijer, E.J.3
Kaman, W.E.4
Janson, A.A.5
Vossen, R.H.6
-
34
-
-
33646671717
-
Intravenous infusion of an antisense oligonucleotide results in exon skipping in muscle dystrophin mRNA of Duchenne muscular dystrophy
-
Takeshima Y, Yagi M, Wada H, Ishibashi K, Nishiyama A, Kakumoto M, et al. Intravenous infusion of an antisense oligonucleotide results in exon skipping in muscle dystrophin mRNA of Duchenne muscular dystrophy. Pediatr Res 2006;59:690-694.
-
(2006)
Pediatr Res
, vol.59
, pp. 690-694
-
-
Takeshima, Y.1
Yagi, M.2
Wada, H.3
Ishibashi, K.4
Nishiyama, A.5
Kakumoto, M.6
-
35
-
-
37549034298
-
Local dystrophin restoration with antisense oligonucleotide PRO051
-
van Deutekom JC, Janson AA, Ginjaar IB, Frankhuizen WS, Aartsma-Rus A, Bremmer-Bout M, et al. Local dystrophin restoration with antisense oligonucleotide PRO051. N Engl J Med 2007;357:2677-2686.
-
(2007)
N Engl J Med
, vol.357
, pp. 2677-2686
-
-
van Deutekom, J.C.1
Janson, A.A.2
Ginjaar, I.B.3
Frankhuizen, W.S.4
Aartsma-Rus, A.5
Bremmer-Bout, M.6
-
36
-
-
0032720705
-
Aminoglycoside antibiotics restore dystrophin function to skeletal muscles of mdx mice
-
Barton-Davis ER, Cordier L, Shoturma DI, Leland SE, Sweeney HL. Aminoglycoside antibiotics restore dystrophin function to skeletal muscles of mdx mice. J Clin Invest 1999;104:375-381.
-
(1999)
J Clin Invest
, vol.104
, pp. 375-381
-
-
Barton-Davis, E.R.1
Cordier, L.2
Shoturma, D.I.3
Leland, S.E.4
Sweeney, H.L.5
-
37
-
-
0034982292
-
Gentamicin treatment of Duchenne and Becker muscular dystrophy due to nonsense mutations
-
Wagner KR, Hamed S, Hadley DW, Gropman AL, Burstein AH, Escolar DM, et al. Gentamicin treatment of Duchenne and Becker muscular dystrophy due to nonsense mutations. Ann Neurol 2001;49:706-711.
-
(2001)
Ann Neurol
, vol.49
, pp. 706-711
-
-
Wagner, K.R.1
Hamed, S.2
Hadley, D.W.3
Gropman, A.L.4
Burstein, A.H.5
Escolar, D.M.6
-
38
-
-
0043092426
-
Gentamicin administration in Duchenne patients with premature stop codon. Preliminary results
-
Politano L, Nigro G, Nigro V, Piluso G, Papparella S, Paciello O, et al. Gentamicin administration in Duchenne patients with premature stop codon. Preliminary results. Acta Myol 2003;22:15-21.
-
(2003)
Acta Myol
, vol.22
, pp. 15-21
-
-
Politano, L.1
Nigro, G.2
Nigro, V.3
Piluso, G.4
Papparella, S.5
Paciello, O.6
-
39
-
-
0033854425
-
Sequence specificity of aminoglycoside-induced stop condon readthrough: Potential implications for treatment of Duchenne muscular dystrophy
-
Howard MT, Shirts BH, Petros LM, Flanigan KM, Gesteland RF, Atkins JF. Sequence specificity of aminoglycoside-induced stop condon readthrough: potential implications for treatment of Duchenne muscular dystrophy. Ann Neurol 2000;48:164-169.
-
(2000)
Ann Neurol
, vol.48
, pp. 164-169
-
-
Howard, M.T.1
Shirts, B.H.2
Petros, L.M.3
Flanigan, K.M.4
Gesteland, R.F.5
Atkins, J.F.6
-
40
-
-
34247588271
-
PTC124 targets genetic disorders caused by nonsense mutations
-
Welch EM, Barton ER, Zhuo J, Tomizawa Y, Friesen WJ, Trifillis P, et al. PTC124 targets genetic disorders caused by nonsense mutations. Nature 2007;447:87-91.
-
(2007)
Nature
, vol.447
, pp. 87-91
-
-
Welch, E.M.1
Barton, E.R.2
Zhuo, J.3
Tomizawa, Y.4
Friesen, W.J.5
Trifillis, P.6
-
41
-
-
33947529670
-
Safety, tolerability, and pharmacokinetics of PTC124, a nonaminoglycoside nonsense mutation suppressor, following single- and multiple-dose administration to healthy male and female adult volunteers
-
Hirawat S, Welch EM, Elfring GL, Northcutt VJ, Paushkin S, Hwang S, et al. Safety, tolerability, and pharmacokinetics of PTC124, a nonaminoglycoside nonsense mutation suppressor, following single- and multiple-dose administration to healthy male and female adult volunteers. J Clin Pharmacol 2007;47:430-444.
-
(2007)
J Clin Pharmacol
, vol.47
, pp. 430-444
-
-
Hirawat, S.1
Welch, E.M.2
Elfring, G.L.3
Northcutt, V.J.4
Paushkin, S.5
Hwang, S.6
-
42
-
-
33847789357
-
Dystrophin expression in host muscle following transplantation of muscle precursor cells modified with the phiC31 integrase
-
Quenneville SP, Chapdelaine P, Rousseau J, Tremblay JP. Dystrophin expression in host muscle following transplantation of muscle precursor cells modified with the phiC31 integrase. Gene Ther 2007;14: 514-522.
-
(2007)
Gene Ther
, vol.14
, pp. 514-522
-
-
Quenneville, S.P.1
Chapdelaine, P.2
Rousseau, J.3
Tremblay, J.P.4
-
43
-
-
36349034522
-
Autologous transplantation of SM/C-2.6(+) satellite cells transduced with micro-dystrophin CS1 cDNA by lentiviral vector into mdx mice
-
Ikemoto M, Fukada S, Uezumi A, Masuda S, Miyoshi H, Yamamoto H, et al. Autologous transplantation of SM/C-2.6(+) satellite cells transduced with micro-dystrophin CS1 cDNA by lentiviral vector into mdx mice. Mol Ther 2007;15:2178-2185.
-
(2007)
Mol Ther
, vol.15
, pp. 2178-2185
-
-
Ikemoto, M.1
Fukada, S.2
Uezumi, A.3
Masuda, S.4
Miyoshi, H.5
Yamamoto, H.6
-
44
-
-
36749032678
-
Restoration of human dystrophin following transplantation of exon-skipping-engineered DMD patient stem cells into dystrophic mice
-
Benchaouir R, Meregalli M, Farini A, D'Antona G, Belicchi M, Goyenvalle A, et al. Restoration of human dystrophin following transplantation of exon-skipping-engineered DMD patient stem cells into dystrophic mice. Cell Stem Cell 2007;1:646-657.
-
(2007)
Cell Stem Cell
, vol.1
, pp. 646-657
-
-
Benchaouir, R.1
Meregalli, M.2
Farini, A.3
D'Antona, G.4
Belicchi, M.5
Goyenvalle, A.6
-
45
-
-
33845257119
-
Mesoangioblast stem cells ameliorate muscle function in dystrophic dogs
-
Sampaolesi M, Blot S, D'Antona G, Granger N, Tonlorenzi R, Innocenzi A, et al. Mesoangioblast stem cells ameliorate muscle function in dystrophic dogs. Nature 2006;444:574-579.
-
(2006)
Nature
, vol.444
, pp. 574-579
-
-
Sampaolesi, M.1
Blot, S.2
D'Antona, G.3
Granger, N.4
Tonlorenzi, R.5
Innocenzi, A.6
-
46
-
-
36248950999
-
Autologous transplantation of muscle-derived CD133+ stem cells in Duchenne muscle patients
-
Torrente Y, Belicchi M, Marchesi C, Dantona G, Cogiamanian F, Pisati F, et al. Autologous transplantation of muscle-derived CD133+ stem cells in Duchenne muscle patients. Cell Transplant 2007;16: 563-577.
-
(2007)
Cell Transplant
, vol.16
, pp. 563-577
-
-
Torrente, Y.1
Belicchi, M.2
Marchesi, C.3
Dantona, G.4
Cogiamanian, F.5
Pisati, F.6
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