Preclinical studies for gene therapy of Duchenne muscular dystrophy

Journal of Child Neurology

Volumn 25, Issue 9, 2010, Pages 1149-1157

  Odom, Guy L ^a   Banks, Glen B ^a   Schultz, Brian R ^a   Gregorevic, Paul ^a   Chamberlain, Jeffrey S ^a  

^a UNIVERSITY OF WASHINGTON SCHOOL OF MEDICINE   (United States)

Author keywords

adeno associated virus; Duchenne muscular dystrophy; dystrophin; gene therapy; micro dystrophin

Indexed keywords

ADENOVIRUS VECTOR; DYSTROBREVIN; DYSTROPHIN; MICRO DYSTROPHIN; MICRO UTROPHIN; PARVOVIRUS VECTOR; SYNTROPHIN; UNCLASSIFIED DRUG; UTROPHIN;

ADENO ASSOCIATED VIRUS; CARBOXY TERMINAL SEQUENCE; DRUG EFFECT; DRUG MECHANISM; DUCHENNE MUSCULAR DYSTROPHY; GENE CASSETTE; GENE EXPRESSION; GENETIC VARIABILITY; HETEROZYGOTE; HUMAN; IMMUNE RESPONSE; IMMUNOSUPPRESSIVE TREATMENT; NONHUMAN; PRIORITY JOURNAL; PROTEIN BINDING; REVIEW; TREATMENT OUTCOME; VIRAL GENE DELIVERY SYSTEM; VIRAL GENE THERAPY;

ANIMALS; DISEASE MODELS, ANIMAL; GENE THERAPY; GENETIC VECTORS; HUMANS; MUSCULAR DYSTROPHY, DUCHENNE;

EID: 77956330692     PISSN: 08830738     EISSN: 17088283     Source Type: Journal    
DOI: 10.1177/0883073810371006     Document Type: Review

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