Muscling in: Gene therapies for muscular dystrophy target RNA

Nature Medicine

Volumn 16, Issue 2, 2010, Pages 170-171

  Chamberlain, Joel R ^a   Chamberlain, Jeffrey S ^b  

^a UNIVERSITY OF WASHINGTON SCHOOL OF MEDICINE   (United States)

^b UNIVERSITY OF WASHINGTON   (United States)

Author keywords

[No Author keywords available]

Indexed keywords

2' O METHYL PHOSPHOROTHIOATE ANTISENSE OLIGONUCLEOTIDE; ADENOVIRUS VECTOR; ANTISENSE OLIGONUCLEOTIDE; ATAXIN 3; BETA GLOBIN; DYSTROPHIN; MESSENGER RNA PRECURSOR; RNA; UNCLASSIFIED DRUG;

ANIMAL EXPERIMENT; ANIMAL MODEL; BETA THALASSEMIA; DEGENERATIVE DISEASE; DUCHENNE MUSCULAR DYSTROPHY; FACIOSCAPULOHUMERAL MUSCULAR DYSTROPHY; GENE EXPRESSION; GENE THERAPY; GENETIC DISORDER; HUMAN; MOUSE; MUSCLE DISEASE; MUSCULAR DYSTROPHY; MYOTONIC DYSTROPHY; NEUROLOGIC DISEASE; NONHUMAN; PRIORITY JOURNAL; PROTEIN EXPRESSION; RNA INTERFERENCE; RNA SPLICING; SHORT SURVEY; SPINOCEREBELLAR DEGENERATION; VIRAL GENE DELIVERY SYSTEM;

ANIMALS; DISEASE MODELS, ANIMAL; GENE THERAPY; MICE; MUSCULAR DYSTROPHIES; OLIGONUCLEOTIDES, ANTISENSE; RNA;

EID: 76249084121     PISSN: 10788956     EISSN: 1546170X     Source Type: Journal    
DOI: 10.1038/nm0210-170     Document Type: Short Survey

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