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Volumn 16, Issue 2, 2010, Pages 170-171
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Muscling in: Gene therapies for muscular dystrophy target RNA
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Author keywords
[No Author keywords available]
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Indexed keywords
2' O METHYL PHOSPHOROTHIOATE ANTISENSE OLIGONUCLEOTIDE;
ADENOVIRUS VECTOR;
ANTISENSE OLIGONUCLEOTIDE;
ATAXIN 3;
BETA GLOBIN;
DYSTROPHIN;
MESSENGER RNA PRECURSOR;
RNA;
UNCLASSIFIED DRUG;
ANIMAL EXPERIMENT;
ANIMAL MODEL;
BETA THALASSEMIA;
DEGENERATIVE DISEASE;
DUCHENNE MUSCULAR DYSTROPHY;
FACIOSCAPULOHUMERAL MUSCULAR DYSTROPHY;
GENE EXPRESSION;
GENE THERAPY;
GENETIC DISORDER;
HUMAN;
MOUSE;
MUSCLE DISEASE;
MUSCULAR DYSTROPHY;
MYOTONIC DYSTROPHY;
NEUROLOGIC DISEASE;
NONHUMAN;
PRIORITY JOURNAL;
PROTEIN EXPRESSION;
RNA INTERFERENCE;
RNA SPLICING;
SHORT SURVEY;
SPINOCEREBELLAR DEGENERATION;
VIRAL GENE DELIVERY SYSTEM;
ANIMALS;
DISEASE MODELS, ANIMAL;
GENE THERAPY;
MICE;
MUSCULAR DYSTROPHIES;
OLIGONUCLEOTIDES, ANTISENSE;
RNA;
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EID: 76249084121
PISSN: 10788956
EISSN: 1546170X
Source Type: Journal
DOI: 10.1038/nm0210-170 Document Type: Short Survey |
Times cited : (8)
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References (14)
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