Stem cell and genetic therapies for the fetus

Seminars in Fetal and Neonatal Medicine

Volumn 15, Issue 1, 2010, Pages 46-51

  Roybal, Jessica L ^a   Santore, Matthew T ^a,b   Flake, Alan W ^a,b  

^a CHILDREN S HOSPITAL OF PHILADELPHIA   (United States)

^b UNIVERSITY OF PENNSYLVANIA   (United States)

Author keywords

Fetal therapy; Gene therapy; Hematopoietic stem cell transplantation; Prenatal treatment

Indexed keywords

ADENOVIRUS VECTOR; LENTIVIRUS VECTOR; PARVOVIRUS VECTOR; RETROVIRUS VECTOR;

ARTICLE; CHIMERA; CRIGLER NAJJAR SYNDROME; CYSTIC FIBROSIS; DUCHENNE MUSCULAR DYSTROPHY; FETAL THERAPY; FETUS GENE THERAPY; FETUS STEM CELL TRANSPLANTATION; GENE EXPRESSION; GENE INSERTION; GENE TARGETING; GENE THERAPY; GENE TRANSFER; GENETIC TRANSDUCTION; GESTATION PERIOD; GLYCOGEN STORAGE DISEASE TYPE 2; GRAFT VERSUS HOST REACTION; HEMATOPOIETIC STEM CELL TRANSPLANTATION; HUMAN; IMMUNE SYSTEM; LEBER CONGENITAL AMAUROSIS; LEUKOCYTE ADHESION DEFICIENCY; MEDICAL ETHICS; MUCOPOLYSACCHARIDOSIS TYPE 7; MUTAGENESIS; MYELOABLATIVE CONDITIONING; NONHUMAN; PERINATAL PERIOD; RISK ASSESSMENT; RISK FACTOR; STEM CELL TRANSPLANTATION; T LYMPHOCYTE; TRANSGENE; TRANSPLANTATION TOLERANCE; VIRAL GENE DELIVERY SYSTEM; VIRUS REPLICATION;

ANIMALS; FETAL DISEASES; GENE THERAPY; GENE TRANSFER TECHNIQUES; HEMATOPOIETIC STEM CELL TRANSPLANTATION; HUMANS; IMMUNE TOLERANCE;

EID: 74449088264     PISSN: 1744165X     EISSN: None     Source Type: Journal    
DOI: 10.1016/j.siny.2009.05.005     Document Type: Article

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