Regulated and multiple miRNA and siRNA delivery into primary cells by a lentiviral platform

Molecular Therapy

Volumn 17, Issue 6, 2009, Pages 1039-1052

  Amendola, Mario ^a,b   Passerini, Laura ^a,b   Pucci, Ferdinando ^a,b   Gentner, Bernhard ^a   Bacchetta, Rosa ^a   Naldini, Luigi ^a,b  

^a SAN RAFFAELE SCIENTIFIC INSTITUTE   (Italy)

^b VITA SALUTE SAN RAFFAELE UNIVERSITY   (Italy)

Author keywords

[No Author keywords available]

Indexed keywords

LENTIVIRUS VECTOR; MICRORNA; RNA POLYMERASE II; SMALL INTERFERING RNA; TRANSCRIPTION FACTOR FOXP3;

ARTICLE; CD4+ CD25+ T LYMPHOCYTE; CONTROLLED STUDY; GENE ACTIVITY; GENE CONTROL; GENE EXPRESSION; GENE REPRESSION; GENE TARGETING; GENETIC ENGINEERING; HETEROLOGOUS EXPRESSION; HUMAN; HUMAN CELL; INTRON; LYMPHOCYTE PROLIFERATION; PHENOTYPE; PLASMID; PROMOTER REGION; REGULATORY T LYMPHOCYTE; RNA SPLICING; VIRAL GENE DELIVERY SYSTEM; VIRUS TITRATION;

BLOTTING, WESTERN; CD4-POSITIVE T-LYMPHOCYTES; CELL LINE; CELLS, CULTURED; FLOW CYTOMETRY; FORKHEAD TRANSCRIPTION FACTORS; GENETIC VECTORS; HELA CELLS; HUMANS; INTERLEUKIN-2 RECEPTOR ALPHA SUBUNIT; LENTIVIRUS; MICRORNAS; POLYMERASE CHAIN REACTION; RNA, SMALL INTERFERING; T-LYMPHOCYTES, REGULATORY; TRANSDUCTION, GENETIC;

EID: 67349250445     PISSN: 15250016     EISSN: 15250024     Source Type: Journal    
DOI: 10.1038/mt.2009.48     Document Type: Article

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