Anti-β(s)-ribozyme reduces β(s) mRNA levels in transgenic mice: Potential application to the gene therapy of sickle cell anemia

Blood Cells, Molecules, and Diseases

Volumn 25, Issue 2, 1999, Pages 110-119

  Alami, Raouf ^a   Gilman, John G ^a   Feng, Y Q ^a   Marmorato, Antonietta ^a   Rochlin, Ilia ^a   Suzuka, Sandra M ^a   Fabry, Mary E ^a   Nagel, Ronald L ^a   Bouhassira, Eric E ^a  

^a ALBERT EINSTEIN COLLEGE OF MEDICINE   (United States)

Author keywords

Beta globin; Gene therapy; Hammerhead ribozyme; Mouse model; Sickle cell anemia

Indexed keywords

ANTIBODY; MESSENGER RNA; RIBOZYME;

ANIMAL EXPERIMENT; ARTICLE; CONTROLLED STUDY; GENE EXPRESSION; GENE THERAPY; HIGH PERFORMANCE LIQUID CHROMATOGRAPHY; MOUSE; NONHUMAN; PRIORITY JOURNAL; PROMOTER REGION; REPORTER GENE; RETICULOCYTE; SICKLE CELL ANEMIA; TRANSGENIC MOUSE;

ANIMALIA; MUS MUSCULUS;

EID: 0033027061     PISSN: 10799796     EISSN: None     Source Type: Journal    
DOI: 10.1006/bcmd.1999.0235     Document Type: Article

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