RNA repair for haemophilia A

Expert Reviews in Molecular Medicine

Volumn 8, Issue 1, 2006, Pages 1-8

  Chao, Hengjun ^a   Walsh, Christopher E ^a  

^a MOUNT SINAI SCHOOL OF MEDICINE   (United States)

Author keywords

[No Author keywords available]

Indexed keywords

BLOOD CLOTTING FACTOR 8; COMPLEMENTARY DNA; MESSENGER RNA; PARVOVIRUS VECTOR; PLASMID DNA; RNA; TRANSFER RNA;

CONSENSUS SEQUENCE; EXON; FEASIBILITY STUDY; GENE CONTROL; GENE MUTATION; GENE TARGETING; GENE TRANSFER; GENETIC CODE; GENETIC DISORDER; HEMOPHILIA A; HUMAN; INTRON; MAMMAL CELL; NONHUMAN; PHENOTYPE; PRIORITY JOURNAL; REVERSE TRANSCRIPTION POLYMERASE CHAIN REACTION; REVIEW; RNA SPLICING; SPLICEOSOME; TRANS SPLICING; VIRAL GENE DELIVERY SYSTEM; VIRAL GENE THERAPY; VIRUS RECOMBINANT; WILD TYPE;

ANIMALS; GENE THERAPY; HEMOPHILIA A; HUMANS; MICE; RNA PRECURSORS; SPLICEOSOMES; TRANS-SPLICING;

MAMMALIA; PARVOVIRUS;

EID: 33645829317     PISSN: 14623994     EISSN: 14623994     Source Type: Journal    
DOI: 10.1017/S1462399406010337     Document Type: Review

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