Transduction characteristics of adeno-associated virus vectors expressing cap serotypes 7, 8, 9, and Rh10 in the mouse brain

Molecular Therapy

Volumn 13, Issue 3, 2006, Pages 528-537

  Cearley, Cassia N ^a,b   Wolfe, John H ^a,b  

^a UNIVERSITY OF PENNSYLVANIA   (United States)

^b CHILDREN S HOSPITAL OF PHILADELPHIA   (United States)

Author keywords

glucuronidase; Capsid; Lysosomal storage disease; MPS VII; Serotype; Vector transport

Indexed keywords

CAPSID PROTEIN; COMPLEMENTARY DNA; LYSOSOME ENZYME; VIRUS VECTOR;

ADENO ASSOCIATED VIRUS; ANIMAL CELL; ANIMAL EXPERIMENT; ANIMAL MODEL; ANIMAL TISSUE; ARTICLE; ASTROCYTE; BRAIN CORTEX; BRAIN DISEASE; BRAIN NERVE CELL; CELL TRANSPORT; CENTRAL NERVOUS SYSTEM; CONTROLLED STUDY; CORPUS STRIATUM; ENZYME LOCALIZATION; EXPRESSION VECTOR; GENE VECTOR; HIPPOCAMPUS; LYSOSOME STORAGE DISEASE; MOUSE; NERVE FIBER; NONHUMAN; OLIGODENDROGLIA; SEROTYPE; SIGNAL TRANSDUCTION; THALAMUS; VIRAL GENE DELIVERY SYSTEM;

ANIMALS; AXONS; BRAIN; CAPSID; CAPSID PROTEINS; DEPENDOVIRUS; DISEASE MODELS, ANIMAL; GENE THERAPY; GENETIC VECTORS; GLUCURONIDASE; HUMANS; MICE; MICE, INBRED C3H; MUCOPOLYSACCHARIDOSIS VII; RNA, MESSENGER; SEROTYPING; TRANSDUCTION, GENETIC; VIRUS ASSEMBLY;

ADENO-ASSOCIATED VIRUS; ANIMALIA; MIRIDAE;

EID: 32944459983     PISSN: 15250016     EISSN: None     Source Type: Journal    
DOI: 10.1016/j.ymthe.2005.11.015     Document Type: Article

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