Gene therapy for leber congenital amaurosis

Advances in Experimental Medicine and Biology

Volumn 533, Issue , 2003, Pages 415-422

  Dejneka, Nadine S ^b   Surace, Enrico M ^b   Bennett, Jean ^a  

^a UNIVERSITY OF PENNSYLVANIA   (United States)

^b NONE

Author keywords

[No Author keywords available]

Indexed keywords

AROMATIC HYDROCARBON RECEPTOR; ARYL HYDROCARBON RECEPTOR INTERACTING PROTEIN LIKE 1; COMPLEMENTARY DNA; CRUMBS HOMOLOG 1 PROTEIN; GUANOSINE TRIPHOSPHATASE; GUANYLATE CYCLASE; PROTEIN; RHODOPSIN; TRANSCRIPTION FACTOR; UNCLASSIFIED DRUG; VIRUS VECTOR;

ADENO ASSOCIATED VIRUS; AIPL1 GENE; ANIMAL MODEL; CONE ROD HOMEOBOX; CONFERENCE PAPER; CRB1 GENE; CRX GENE; ELECTRORETINOGRAM; GENE; GENE EXPRESSION; GENE MUTATION; GENE THERAPY; GENETIC TRANSCRIPTION; GUCY2D GENE; HOMEOBOX; HUMAN; LEBER CONGENITAL AMAUROSIS; NONHUMAN; PIGMENT EPITHELIUM; PRIORITY JOURNAL; PROMOTER REGION; RETGC1 GENE; RETINA CONE; RETINA DISEASE; RETINA DYSTROPHY; RETINA ROD; RPE65 GENE; RPGRIP1 GENE; VIRAL GENE DELIVERY SYSTEM; VIRAL GENE THERAPY; VIRUS RECOMBINANT;

ADENO-ASSOCIATED VIRUS; ANIMALIA;

EID: 0346271741     PISSN: 00652598     EISSN: None     Source Type: Book Series    
DOI: 10.1007/978-1-4615-0067-4_53     Document Type: Conference Paper

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