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Volumn 102, Issue 3, 2003, Pages 843-848

In vivo retroviral gene transfer by direct intrafemoral injection results in correction of the SCID phenotype in Jak3 knock-out animals

Author keywords

[No Author keywords available]

Indexed keywords

ADENOVIRUS VECTOR; GENE PRODUCT; GREEN FLUORESCENT PROTEIN; HEMOPOIETIC GROWTH FACTOR; JANUS KINASE 3; RETROVIRUS VECTOR; UNCLASSIFIED DRUG;

EID: 0042243666     PISSN: 00064971     EISSN: None     Source Type: Journal    
DOI: 10.1182/blood-2002-12-3859     Document Type: Article
Times cited : (29)

References (37)
  • 1
    • 0021758970 scopus 로고
    • Introduction of new genetic material into pluripotent haematopoietic stem cells of the mouse
    • Williams DA, Lemischka IR, Nathan DG, Mulligan RC. Introduction of new genetic material into pluripotent haematopoietic stem cells of the mouse. Nature. 1984;310:476-480.
    • (1984) Nature , vol.310 , pp. 476-480
    • Williams, D.A.1    Lemischka, I.R.2    Nathan, D.G.3    Mulligan, R.C.4
  • 2
    • 0022355684 scopus 로고
    • Introduction of a selectable gene into primitive stem cells capable of long term reconstruction of the hemopoietic system of W/Wv mice
    • Dick JE, Magli MC, Huszar D, Phillips RA, Bernstein A. Introduction of a selectable gene into primitive stem cells capable of long term reconstruction of the hemopoietic system of W/Wv mice. Cell. 1985;42:71-79.
    • (1985) Cell , vol.42 , pp. 71-79
    • Dick, J.E.1    Magli, M.C.2    Huszar, D.3    Phillips, R.A.4    Bernstein, A.5
  • 3
    • 0022365333 scopus 로고
    • Expression of a foreign gene in myeloid and lymphoid cells derived from multipotent haematopoietic precursors
    • Keller G, Paige C, Gilboa E, Wagner EF. Expression of a foreign gene in myeloid and lymphoid cells derived from multipotent haematopoietic precursors. Nature. 1985;318:149-154.
    • (1985) Nature , vol.318 , pp. 149-154
    • Keller, G.1    Paige, C.2    Gilboa, E.3    Wagner, E.F.4
  • 4
    • 0027158091 scopus 로고
    • Integration of murine leukemia virus DNA depends on mitosis
    • Roe T, Reynolds TC, Yu G, Brown PO. Integration of murine leukemia virus DNA depends on mitosis. EMBO J. 1993;12:2099-2108.
    • (1993) EMBO J , vol.12 , pp. 2099-2108
    • Roe, T.1    Reynolds, T.C.2    Yu, G.3    Brown, P.O.4
  • 5
    • 0026725231 scopus 로고
    • The renewal and differentiation of hemopoietic stem cells
    • Zipori D. The renewal and differentiation of hemopoietic stem cells. FASEB J. 1992;6:2691-2697.
    • (1992) FASEB J , vol.6 , pp. 2691-2697
    • Zipori, D.1
  • 6
    • 0027325195 scopus 로고
    • Differentiation and proliferation of hematopoietic stem cells
    • Ogawa M. Differentiation and proliferation of hematopoietic stem cells. Blood. 1993;81:2844-2853.
    • (1993) Blood , vol.81 , pp. 2844-2853
    • Ogawa, M.1
  • 7
    • 0028332764 scopus 로고
    • Efficient retrovirus mediated gene transduction into murine hematopoietic stem cells and long lasting expression using a transwell co-culture system
    • Germeraad WTV, Asami N, Fujimoto S, Mazda O, Katsura Y. Efficient retrovirus mediated gene transduction into murine hematopoietic stem cells and long lasting expression using a transwell co-culture system. Blood. 1994;84:780-788.
    • (1994) Blood , vol.84 , pp. 780-788
    • Germeraad, W.T.V.1    Asami, N.2    Fujimoto, S.3    Mazda, O.4    Katsura, Y.5
  • 8
    • 0033571561 scopus 로고    scopus 로고
    • Improved expression in hematopoietic and lymphoid cells in mice after transplantation of bone marrow transduced with a modified retroviral vector
    • Halene S, Wang L, Cooper RM, Bockstoce DC, Robbins PB, Kohn DB. Improved expression in hematopoietic and lymphoid cells in mice after transplantation of bone marrow transduced with a modified retroviral vector. Blood. 1999;94:3349-3357.
    • (1999) Blood , vol.94 , pp. 3349-3357
    • Halene, S.1    Wang, L.2    Cooper, R.M.3    Bockstoce, D.C.4    Robbins, P.B.5    Kohn, D.B.6
  • 9
    • 0034724857 scopus 로고    scopus 로고
    • Gene therapy of human severe combined immunodeficiency (SCID)-X1 disease
    • Cavazzana-Calvo M, Hacein-Bey S, Basile GDS, et al. Gene therapy of human severe combined immunodeficiency (SCID)-X1 disease. Science. 2000;288:669-672.
    • (2000) Science , vol.288 , pp. 669-672
    • Cavazzana-Calvo, M.1    Hacein-Bey, S.2    Basile, G.D.S.3
  • 10
    • 0034131481 scopus 로고    scopus 로고
    • Efficient retrovirus mediated transfer of the multidrug resistance 1 gene into autologous human long term repopulating hematopoietic stem cells
    • Abonour R, Williams DA, Einhorn L, et al. Efficient retrovirus mediated transfer of the multidrug resistance 1 gene into autologous human long term repopulating hematopoietic stem cells. Nat Med. 2000;6:652-658.
    • (2000) Nat Med , vol.6 , pp. 652-658
    • Abonour, R.1    Williams, D.A.2    Einhorn, L.3
  • 11
    • 0025163797 scopus 로고
    • Molecular basis of homing of intravenously transplanted stem cells to the marrow
    • Tavassoli M, Hardy CL. Molecular basis of homing of intravenously transplanted stem cells to the marrow. Blood. 1990;76:1059-1070.
    • (1990) Blood , vol.76 , pp. 1059-1070
    • Tavassoli, M.1    Hardy, C.L.2
  • 12
    • 0029016628 scopus 로고
    • Murine marrow cells expanded in culture with IL-3, IL-6, and SCF acquire an engraftment defect in normal hosts
    • Peters SO, Kittler ELW, Ramshaw HS, Quesenberry PJ. Murine marrow cells expanded in culture with IL-3, IL-6, and SCF acquire an engraftment defect in normal hosts. Exp Hematol. 1995; 23:461-469.
    • (1995) Exp Hematol , vol.23 , pp. 461-469
    • Peters, S.O.1    Kittler, E.L.W.2    Ramshaw, H.S.3    Quesenberry, P.J.4
  • 13
    • 0029923437 scopus 로고    scopus 로고
    • Interleukin 3 or interleukin 1 abrogates the reconstituting ability of hematopoietic stem cells
    • Yonemura Y, Ku H, Hairayama F, Souza LM, Ogawa M. Interleukin 3 or interleukin 1 abrogates the reconstituting ability of hematopoietic stem cells. Proc Natl Acad Sci U S A. 1996;93:4040-4044.
    • (1996) Proc Natl Acad Sci U S A , vol.93 , pp. 4040-4044
    • Yonemura, Y.1    Ku, H.2    Hairayama, F.3    Souza, L.M.4    Ogawa, M.5
  • 14
    • 0030920565 scopus 로고    scopus 로고
    • CD34 positive PBPC expanded ex vivo may not provide durable engraftment following myeloablative chemoradiotherapy regimens
    • Holyoake TL, Alcorn MJ, Richmond L, et al. CD34 positive PBPC expanded ex vivo may not provide durable engraftment following myeloablative chemoradiotherapy regimens. Bone Marrow Transplant. 1997;19:1095-1101.
    • (1997) Bone Marrow Transplant , vol.19 , pp. 1095-1101
    • Holyoake, T.L.1    Alcorn, M.J.2    Richmond, L.3
  • 15
    • 0031936092 scopus 로고    scopus 로고
    • Restrictions in stem cell function of murine bone marrow grafts after ex vivo expansion of short term repopulating progenitors
    • Varas F, Bernad A, Bueren JA. Restrictions in stem cell function of murine bone marrow grafts after ex vivo expansion of short term repopulating progenitors. Exp Hematol. 1998;26:100-109.
    • (1998) Exp Hematol , vol.26 , pp. 100-109
    • Varas, F.1    Bernad, A.2    Bueren, J.A.3
  • 16
    • 0033104947 scopus 로고    scopus 로고
    • Organ selective homing defines engraftment kinetics of murine hematopoietic stem cells and is compromised by ex vivo expansion
    • Szilvassy SJ, Bass MJ, Zant GV, Grimes B. Organ selective homing defines engraftment kinetics of murine hematopoietic stem cells and is compromised by ex vivo expansion. Blood. 1999; 93:1557-1566.
    • (1999) Blood , vol.93 , pp. 1557-1566
    • Szilvassy, S.J.1    Bass, M.J.2    Zant, G.V.3    Grimes, B.4
  • 17
    • 0032227546 scopus 로고    scopus 로고
    • Retroviral vectors containing a variant dihydrofolate reductase gene for drug protection and in vivo selection of hematopoietic cells
    • Allay JA, Galipeau J, Blakley RL, Sorrentino BP. Retroviral vectors containing a variant dihydrofolate reductase gene for drug protection and in vivo selection of hematopoietic cells. Stem Cells. 1998;16:223-233.
    • (1998) Stem Cells , vol.16 , pp. 223-233
    • Allay, J.A.1    Galipeau, J.2    Blakley, R.L.3    Sorrentino, B.P.4
  • 18
    • 0033567909 scopus 로고    scopus 로고
    • In vivo selection of wild-type hematopoietic stem cells in a murine model of Fanconi anemia
    • Battaile KP, Bateman RL, Mortimer D, et al. In vivo selection of wild-type hematopoietic stem cells in a murine model of Fanconi anemia. Blood. 1999;94:2151-2158.
    • (1999) Blood , vol.94 , pp. 2151-2158
    • Battaile, K.P.1    Bateman, R.L.2    Mortimer, D.3
  • 19
    • 0034694076 scopus 로고    scopus 로고
    • Self selection by genetically modified committed lymphocyte precursors reverses the phenotype of JAK3-deficient mice without myeloablation
    • Bunting KD, Lu T, Kelly PF, Sorrentino BP. Self selection by genetically modified committed lymphocyte precursors reverses the phenotype of JAK3-deficient mice without myeloablation. Hum Gene Ther. 2000;11:2353-2364.
    • (2000) Hum Gene Ther , vol.11 , pp. 2353-2364
    • Bunting, K.D.1    Lu, T.2    Kelly, P.F.3    Sorrentino, B.P.4
  • 20
    • 0031890632 scopus 로고    scopus 로고
    • Restoration of lymphocyte function in Janus kinase 3-deficient mice by retroviral mediated gene transfer
    • Bunting KD, Sangster MY, Ihle JN, Sorrentino BP. Restoration of lymphocyte function in Janus kinase 3-deficient mice by retroviral mediated gene transfer. Nat Med. 1998;4:58-64.
    • (1998) Nat Med , vol.4 , pp. 58-64
    • Bunting, K.D.1    Sangster, M.Y.2    Ihle, J.N.3    Sorrentino, B.P.4
  • 22
    • 0035869530 scopus 로고    scopus 로고
    • Lack of dominant-negative effects of a truncated gamma(c) on retroviral-mediated gene correction of immunodeficient mice
    • Otsu M, Sugamura K, Candotti F. Lack of dominant-negative effects of a truncated gamma(c) on retroviral-mediated gene correction of immunodeficient mice. Blood 2001;97:1618-1624.
    • (2001) Blood , vol.97 , pp. 1618-1624
    • Otsu, M.1    Sugamura, K.2    Candotti, F.3
  • 23
    • 0028840706 scopus 로고
    • Defective lymphoid development in mice lacking Jak3
    • Nosaka T, Deursen JMAV, Tripp TA, et al. Defective lymphoid development in mice lacking Jak3. Science. 1995;270:800-802.
    • (1995) Science , vol.270 , pp. 800-802
    • Nosaka, T.1    Deursen, J.M.A.V.2    Tripp, T.A.3
  • 24
    • 0029550822 scopus 로고
    • Developmental defects of lymphoid cells in Jak3 kinase deficient mice
    • Park SY, Saijo K, Takeahashi T, et al. Developmental defects of lymphoid cells in Jak3 kinase deficient mice. Immunity. 1995;3:771-782.
    • (1995) Immunity , vol.3 , pp. 771-782
    • Park, S.Y.1    Saijo, K.2    Takeahashi, T.3
  • 25
    • 0027751556 scopus 로고
    • Interleukin-2 receptor gamma chain: A functional com ponent of the interleukin-7 receptor
    • Noguchi M, Nakamura Y, Russell SM, et al. Interleukin-2 receptor gamma chain: a functional com ponent of the interleukin-7 receptor. Science. 1993;262:1877-1880.
    • (1993) Science , vol.262 , pp. 1877-1880
    • Noguchi, M.1    Nakamura, Y.2    Russell, S.M.3
  • 26
    • 0031749260 scopus 로고    scopus 로고
    • T cell development and activation in Jak3-deficient mice
    • Baird AM, Thomis DC, Berg LJ. T cell development and activation in Jak3-deficient mice. J Leukoc Biol. 1998;63:669-677.
    • (1998) J Leukoc Biol , vol.63 , pp. 669-677
    • Baird, A.M.1    Thomis, D.C.2    Berg, L.J.3
  • 27
    • 0029164841 scopus 로고
    • Mutations of Jak-3 gene in patients with autosomal severe combined immune deficiency (SCID)
    • Macchi P, Villa A, Giliani S, et al. Mutations of Jak-3 gene in patients with autosomal severe combined immune deficiency (SCID). Nature. 1995;377:65-68.
    • (1995) Nature , vol.377 , pp. 65-68
    • Macchi, P.1    Villa, A.2    Giliani, S.3
  • 28
    • 0024239024 scopus 로고
    • Construction and use of a safe and efficient amphotropic packaging cell line
    • Markowitz D, Goff S, Bank A. Construction and use of a safe and efficient amphotropic packaging cell line. Virology. 1988;167:400-406.
    • (1988) Virology , vol.167 , pp. 400-406
    • Markowitz, D.1    Goff, S.2    Bank, A.3
  • 29
    • 0030775308 scopus 로고    scopus 로고
    • A GFP reporter system to assess gene transfer and expression in human hematopoietic progenitor cells
    • Cheng L, Du C, Murray D, et al. A GFP reporter system to assess gene transfer and expression in human hematopoietic progenitor cells. Gene Ther. 1997;4:1013-1022.
    • (1997) Gene Ther , vol.4 , pp. 1013-1022
    • Cheng, L.1    Du, C.2    Murray, D.3
  • 30
    • 0028095137 scopus 로고
    • Enrichment for primitive hemopoietic progenitors of marrow cells from 5-fluorouracil treated mice and normal mice
    • Ogawa M, Shih JP, Katayama N. Enrichment for primitive hemopoietic progenitors of marrow cells from 5-fluorouracil treated mice and normal mice. Blood Cells. 1994;20:7-13.
    • (1994) Blood Cells , vol.20 , pp. 7-13
    • Ogawa, M.1    Shih, J.P.2    Katayama, N.3
  • 31
    • 0025992197 scopus 로고
    • Most primitive hematopoietic stem cells are stimulated to cycle rapidly after treatment with 5-fluorouracil
    • Harrison DE, Lerner CP. Most primitive hematopoietic stem cells are stimulated to cycle rapidly after treatment with 5-fluorouracil. Blood. 1991; 78:1237-1240.
    • (1991) Blood , vol.78 , pp. 1237-1240
    • Harrison, D.E.1    Lerner, C.P.2
  • 32
    • 0032544024 scopus 로고    scopus 로고
    • Consistent, persistent expression from modified retroviral vectors in murine hematopoietic stem cells
    • Robbins PB, Skelton DC, Yu X-J, Halen S, Leonard EH. Consistent, persistent expression from modified retroviral vectors in murine hematopoietic stem cells. Proc Natl Acad Sci U S A. 1998;95:10182-10187.
    • (1998) Proc Natl Acad Sci U S A , vol.95 , pp. 10182-10187
    • Robbins, P.B.1    Skelton, D.C.2    Yu, X.-J.3    Halen, S.4    Leonard, E.H.5
  • 33
    • 0030920096 scopus 로고    scopus 로고
    • In vivo retrovirus mediated gene transfer into multiple hematopoietic lineages in rabbits without preconditioning
    • Nelson DM, Metzger ME, Donahue RE, Morgan RA. In vivo retrovirus mediated gene transfer into multiple hematopoietic lineages in rabbits without preconditioning. Hum Gene Ther. 1997;8:747-754.
    • (1997) Hum Gene Ther , vol.8 , pp. 747-754
    • Nelson, D.M.1    Metzger, M.E.2    Donahue, R.E.3    Morgan, R.A.4
  • 34
    • 0033624048 scopus 로고    scopus 로고
    • Neonatal gene therapy: Transfer and expression of exogenous genes in neonatal sheep following direct injection of retroviral vectors into the bone marrow space
    • Porada CD, Tran ND, Zhao Y, Anderson WF, Zanjani ED. Neonatal gene therapy: transfer and expression of exogenous genes in neonatal sheep following direct injection of retroviral vectors into the bone marrow space. Exp Hematol. 2000;28:642-650.
    • (2000) Exp Hematol , vol.28 , pp. 642-650
    • Porada, C.D.1    Tran, N.D.2    Zhao, Y.3    Anderson, W.F.4    Zanjani, E.D.5
  • 35
    • 0033214219 scopus 로고    scopus 로고
    • Efficient and durable gene marking of hematopoietic progenitor cells in nonhuman primates after nonablative conditioning
    • Rosenzweig M, MacVittie TJ, Harper D, et al. Efficient and durable gene marking of hematopoietic progenitor cells in nonhuman primates after nonablative conditioning. Blood. 1999;94:2271-2286.
    • (1999) Blood , vol.94 , pp. 2271-2286
    • Rosenzweig, M.1    MacVittie, T.J.2    Harper, D.3
  • 36
    • 0032529523 scopus 로고    scopus 로고
    • Ex vivo expansion of genetically marked rhesus peripheral blood progenitor cells results in diminished long term repopulating ability
    • Tisdale JF, Hanazono Y, Sellers SE, et al. Ex vivo expansion of genetically marked rhesus peripheral blood progenitor cells results in diminished long term repopulating ability. Blood. 1998;92:1131-1141.
    • (1998) Blood , vol.92 , pp. 1131-1141
    • Tisdale, J.F.1    Hanazono, Y.2    Sellers, S.E.3
  • 37
    • 0037020112 scopus 로고    scopus 로고
    • News: Gene therapy a suspect in leukemia-like disease
    • Marshall E. News: gene therapy a suspect in leukemia-like disease. Science. 2002;298:34-35.
    • (2002) Science , vol.298 , pp. 34-35
    • Marshall, E.1


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