Therapeutic antisense-induced exon skipping in cultured muscle cells from six different DMD patients

Human Molecular Genetics

Volumn 12, Issue 8, 2003, Pages 907-914

  Aartsma Rus, Annemieke ^a   Janson, Anneke A M ^a   Kaman, Wendy E ^a   Bremmer Bout, Mattie ^a   den Dunnen T , Johan ^a   Baas, Frank ^b   van Ommen, Gert Jan B ^a   van Deutekom, Judith C T ^a  

^a LEIDEN UNIVERSITY MEDICAL CENTER   (Netherlands)

^b ACADEMIC MEDICAL CENTER   (Netherlands)

Author keywords

[No Author keywords available]

Indexed keywords

ANTISENSE OLIGONUCLEOTIDE; DYSTROPHIN; MEMBRANE PROTEIN; MESSENGER RNA;

ARTICLE; BECKER MUSCULAR DYSTROPHY; CELL CULTURE; CONTROLLED STUDY; DATA BASE; DISEASE COURSE; DISEASE SEVERITY; DUCHENNE MUSCULAR DYSTROPHY; EXON; FRAMESHIFT MUTATION; GENE DELETION; GENE MUTATION; GENE TARGETING; GENE THERAPY; GENETIC TRANSCRIPTION; HUMAN; HUMAN CELL; MUSCLE ATROPHY; MUSCLE CELL; NONSENSE MUTATION; PRIORITY JOURNAL; PROTEIN ANALYSIS; PROTEIN EXPRESSION; PROTEIN FUNCTION; PROTEIN SYNTHESIS;

BLOTTING, WESTERN; CELLS, CULTURED; DYSTROPHIN; EXONS; HUMANS; IMMUNOHISTOCHEMISTRY; MUSCLE CELLS; MUSCULAR DYSTROPHY, DUCHENNE; MUTATION; OLIGORIBONUCLEOTIDES, ANTISENSE; REVERSE TRANSCRIPTASE POLYMERASE CHAIN REACTION; TIME FACTORS;

EID: 0037447517     PISSN: 09646906     EISSN: None     Source Type: Journal    
DOI: 10.1093/hmg/ddg100     Document Type: Article

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