Plasmid-based gene transfer ameliorates visceral storage in a mouse model of Sandhoff disease

Journal of Molecular Medicine

Volumn 81, Issue 3, 2003, Pages 185-193

  Yamaguchi, Akira ^a   Katsuyama, Kayoko ^a   Suzuki, Kyoko ^a   Kosaka, Kenji ^a   Aoki, Ichiro ^a   Yamanaka, Shoji ^a  

^a YOKOHAMA CITY UNIVERSITY   (Japan)

Author keywords

Cationic liposome; GM2 gangliosidoses; Lysosomal storage disorder; Plasmid gene therapy; Sandhoff disease

Indexed keywords

BETA N ACETYLHEXOSAMINIDASE; GANGLIOSIDE; GANGLIOSIDE GM2; LIPOSOME; RECOMBINANT ENZYME;

ADOLESCENT; ANIMAL; ANIMAL MODEL; ANIMAL TISSUE; ARTICLE; CELL LINE; CONTROLLED STUDY; DISEASE MODEL; ENZYME ACTIVITY; GENE EXPRESSION; GENE MUTATION; GENE THERAPY; GENE TRANSFER; GENETICS; GM2 GANGLIOSIDOSIS; HISTOCHEMISTRY; HUMAN; LIPID DEGRADATION; LIVER; LYSOSOME STORAGE DISEASE; MALE; METABOLISM; MOUSE; MOUSE MUTANT; NONHUMAN; PATHOLOGY; PLASMID; SANDHOFF DISEASE; TISSUE DISTRIBUTION; VISCERA;

EID: 0037365217     PISSN: 09462716     EISSN: None     Source Type: Journal    
DOI: 10.1007/s00109-002-0410-y     Document Type: Article

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