Retrovirus-mediated enzymatic correction of Tay-Sachs defect in transduced and non-transduced cells

Human Molecular Genetics

Volumn 7, Issue 5, 1998, Pages 831-838

  Guidotti, J E ^a   Akli, S ^b   Castelnau Ptakhine, L ^a   Kahn, A ^a   Poenaru, L ^a,c  

^a CHU Cochin Port Royal ^*  (France)

^b BAYLOR COLLEGE OF MEDICINE   (United States)

^c UNIVERSITÉ PARIS DESCARTES   (France)

Author keywords

[No Author keywords available]

Indexed keywords

BETA N ACETYLHEXOSAMINIDASE A; LYSOSOME ENZYME;

ARTICLE; CLONING VECTOR; ENZYME DEFICIENCY; FIBROBLAST; GENE TRANSFER; GENETIC TRANSDUCTION; HUMAN; MOUSE; NONHUMAN; PLASMID; PRIORITY JOURNAL; RETROVIRUS; TAY SACHS DISEASE;

3T3 CELLS; ANIMALS; BETA-N-ACETYLHEXOSAMINIDASE; CLONING, MOLECULAR; ENZYME ACTIVATION; FIBROBLASTS; GENE EXPRESSION REGULATION, ENZYMOLOGIC; GENE TRANSFER TECHNIQUES; GENETIC VECTORS; HUMANS; ISOENZYMES; MICE; MICE, INBRED C57BL; RETROVIRIDAE; TAY-SACHS DISEASE; TRANSFECTION;

MURINAE; RNA VIRUSES; UNIDENTIFIED RETROVIRUS;

EID: 0031944718     PISSN: 09646906     EISSN: None     Source Type: Journal    
DOI: 10.1093/hmg/7.5.831     Document Type: Article

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