메뉴 건너뛰기




Volumn 1, Issue 6, 2000, Pages 501-505

Gene therapy for ocular disease

Author keywords

[No Author keywords available]

Indexed keywords

NERVE GROWTH FACTOR;

EID: 0034200932     PISSN: 15250016     EISSN: None     Source Type: Journal    
DOI: 10.1006/mthe.2000.0080     Document Type: Review
Times cited : (61)

References (55)
  • 1
    • 0031684801 scopus 로고    scopus 로고
    • Analysis of immune deviation elicited by antigens injected into the subretinal space
    • Wenkel, H., and Streilein, J. W. (1998). Analysis of immune deviation elicited by antigens injected into the subretinal space. Invest. Ophthalmol. Vis. Sci. 39: 1823-1834.
    • (1998) Invest. Ophthalmol. Vis. Sci. , vol.39 , pp. 1823-1834
    • Wenkel, H.1    Streilein, J.W.2
  • 2
    • 0028791690 scopus 로고
    • Enhanced perspective: Unraveling immune privilege
    • Streilein, J. (1995). Enhanced perspective: Unraveling immune privilege. Science 270: 1158.
    • (1995) Science , vol.270 , pp. 1158
    • Streilein, J.1
  • 3
    • 0025791004 scopus 로고
    • Studies on the induction of anterior chamber-associated immune deviation (ACAID). 1. Evidence that an antigen-specific, ACAID-inducing, cell-associated signal exists in the peripheral blood
    • Wilbanks, G. A., and Streilein, J. W. (1991). Studies on the induction of anterior chamber-associated immune deviation (ACAID). 1. Evidence that an antigen-specific, ACAID-inducing, cell-associated signal exists in the peripheral blood. J. Immunol. 146: 2610-2617.
    • (1991) J. Immunol. , vol.146 , pp. 2610-2617
    • Wilbanks, G.A.1    Streilein, J.W.2
  • 4
    • 0028136394 scopus 로고
    • Epidermal growth factor, transforming growth factor alpha, transforming growth factor beta, acidic fibroblast growth factor, basic fibroblast growth factor, and interleukin-1 proteins in the cornea
    • Wilson, S. E., Schultz, G. S., Chegini, N., Weng, J., and He, Y. (1994). Epidermal growth factor, transforming growth factor alpha, transforming growth factor beta, acidic fibroblast growth factor, basic fibroblast growth factor, and interleukin-1 proteins in the cornea. Exp. Eye Res. 59: 63-71.
    • (1994) Exp. Eye Res. , vol.59 , pp. 63-71
    • Wilson, S.E.1    Schultz, G.S.2    Chegini, N.3    Weng, J.4    He, Y.5
  • 7
    • 0028297518 scopus 로고
    • In vivo transfer of a reporter gene to the retina mediated by an adenoviral vector
    • Li, T., et al. (1994). In vivo transfer of a reporter gene to the retina mediated by an adenoviral vector. Invest. Ophthalmol. Vis. Sci. 35: 2543-2549.
    • (1994) Invest. Ophthalmol. Vis. Sci. , vol.35 , pp. 2543-2549
    • Li, T.1
  • 8
    • 0031455575 scopus 로고    scopus 로고
    • Real-time non-invasive in vivo assessment of adeno-associated virus-mediated retinal transduction
    • Bennett, J., Duan, D., Engelhardt, J., and Maguire, A. M. (1997). Real-time non-invasive in vivo assessment of adeno-associated virus-mediated retinal transduction. Invest. Ophthalmol. Vis. Sci. 38: 2857-2863.
    • (1997) Invest. Ophthalmol. Vis. Sci. , vol.38 , pp. 2857-2863
    • Bennett, J.1    Duan, D.2    Engelhardt, J.3    Maguire, A.M.4
  • 9
    • 0030924589 scopus 로고    scopus 로고
    • Evaluation of recombinant adeno-associated virus as a gene transfer vector for the retina
    • Grant, C., Ponnazhagan, S., Wang, X.-S., Srivastava, A., and Li, T. (1997). Evaluation of recombinant adeno-associated virus as a gene transfer vector for the retina. Curr. Eye Res. 16: 949-956.
    • (1997) Curr. Eye Res. , vol.16 , pp. 949-956
    • Grant, C.1    Ponnazhagan, S.2    Wang, X.-S.3    Srivastava, A.4    Li, T.5
  • 10
    • 0031011667 scopus 로고    scopus 로고
    • Efficient photoreceptor-targeted gene expression in vivo by recombinant adeno-associated virus
    • Flannery, J., et al. (1997). Efficient photoreceptor-targeted gene expression in vivo by recombinant adeno-associated virus. Proc. Natl. Acad. Sci. USA 94: 6916-6921.
    • (1997) Proc. Natl. Acad. Sci. USA , vol.94 , pp. 6916-6921
    • Flannery, J.1
  • 11
    • 0030819379 scopus 로고    scopus 로고
    • Multiply attenuated lentiviral vector achieves efficient gene delivery in vivo
    • Zufferey, R., Nagy, D., Mandel, R.J., Naldini, L., and Trono, D. (1997). Multiply attenuated lentiviral vector achieves efficient gene delivery in vivo. Nat. Biotech. 15: 871-875.
    • (1997) Nat. Biotech. , vol.15 , pp. 871-875
    • Zufferey, R.1    Nagy, D.2    Mandel, R.J.3    Naldini, L.4    Trono, D.5
  • 12
    • 0030931963 scopus 로고    scopus 로고
    • Stable and efficient gene transfer into the retina using an HIV-based lentiviral vector
    • Miyoshi, H., Takahashi, M., Gage, F., and Verma, I. (1997). Stable and efficient gene transfer into the retina using an HIV-based lentiviral vector. Proc. Natt. Acad. Sci. USA 94: 10319-10323.
    • (1997) Proc. Natt. Acad. Sci. USA , vol.94 , pp. 10319-10323
    • Miyoshi, H.1    Takahashi, M.2    Gage, F.3    Verma, I.4
  • 14
    • 0030874508 scopus 로고    scopus 로고
    • Cell-mediated immune response and stability of intraocular transgene expression after adenovirus-mediated delivery
    • Hoffman, L. M., Maguire, A. M., and Bennett, J. (1997). Cell-mediated immune response and stability of intraocular transgene expression after adenovirus-mediated delivery. Invest. Ophthalmol. Vis. Sci. 38: 2224-2233.
    • (1997) Invest. Ophthalmol. Vis. Sci. , vol.38 , pp. 2224-2233
    • Hoffman, L.M.1    Maguire, A.M.2    Bennett, J.3
  • 15
    • 0029887454 scopus 로고    scopus 로고
    • Ocular adenovirus gene transfer varies in efficiency and inflammatory response
    • Borras, T., Tamm, E. R., and Zigler, J. S., Jr. (1996). Ocular adenovirus gene transfer varies in efficiency and inflammatory response. Invest. Ophthalmol. Vis. Sci. 37: 1282-1293.
    • (1996) Invest. Ophthalmol. Vis. Sci. , vol.37 , pp. 1282-1293
    • Borras, T.1    Tamm, E.R.2    Zigler J.S., Jr.3
  • 16
    • 0032413204 scopus 로고    scopus 로고
    • Adenovirus-mediated gene transfer to the ocular surface epithelium
    • Tsubota, K., et al. (1998). Adenovirus-mediated gene transfer to the ocular surface epithelium. Exp. Eye Res. 67: 531-538.
    • (1998) Exp. Eye Res. , vol.67 , pp. 531-538
    • Tsubota, K.1
  • 18
    • 0030840092 scopus 로고    scopus 로고
    • Ex vivo adenovirus-mediated gene transfer and immunomodulatory protein production in human cornea
    • Oral, H. B., et al. (1997). Ex vivo adenovirus-mediated gene transfer and immunomodulatory protein production in human cornea. Gene Ther. 4: 639-647.
    • (1997) Gene Ther. , vol.4 , pp. 639-647
    • Oral, H.B.1
  • 20
    • 0032584228 scopus 로고    scopus 로고
    • Prolonged delivery of brain-derived neurotrophic factor by adenovirus-infected Muller cells temporarily rescues injured retinal ganglion cells
    • Di Polo, A., Aigner, L. J., Dunn, R. J., Bray, G. M., and Aguayo, A. J. (1998). Prolonged delivery of brain-derived neurotrophic factor by adenovirus-infected Muller cells temporarily rescues injured retinal ganglion cells. Proc. Natl. Acad. Sci. USA 95: 3978-3983.
    • (1998) Proc. Natl. Acad. Sci. USA , vol.95 , pp. 3978-3983
    • Di Polo, A.1    Aigner, L.J.2    Dunn, R.J.3    Bray, G.M.4    Aguayo, A.J.5
  • 21
    • 0032952793 scopus 로고    scopus 로고
    • Persistent transgene product in retina, optic nerve and brain after intraocular injection of rAAV
    • Dudus, L., et al. (1999). Persistent transgene product in retina, optic nerve and brain after intraocular injection of rAAV. Vis. Res. 39: 2545-2554.
    • (1999) Vis. Res. , vol.39 , pp. 2545-2554
    • Dudus, L.1
  • 22
    • 0033166476 scopus 로고    scopus 로고
    • Bcl-2 gene therapy exacerbates excitotoxicity
    • Simon, P., et al. (1999). Bcl-2 gene therapy exacerbates excitotoxicity. Hum. Gene Ther. 10: 1715-1720.
    • (1999) Hum. Gene Ther. , vol.10 , pp. 1715-1720
    • Simon, P.1
  • 23
    • 0040286047 scopus 로고    scopus 로고
    • In vivo gene therapy with AAV-bFGF protects against excitotoxicity
    • in press
    • Vorwerk, C. K., et al. (2000). In vivo gene therapy with AAV-bFGF protects against excitotoxicity. Invest. Ophthalmol. Vis. Sci.: in press.
    • (2000) Invest. Ophthalmol. Vis. Sci.
    • Vorwerk, C.K.1
  • 24
    • 0024996675 scopus 로고
    • Clinical and genetic heterogeneity in retinitis pigmentosa
    • Kaplan, J., Bonneau, D., Frezal, J., Munnich, A., and Dufier, J. L. (1990). Clinical and genetic heterogeneity in retinitis pigmentosa. Hum. Genet. 85: 635-642.
    • (1990) Hum. Genet. , vol.85 , pp. 635-642
    • Kaplan, J.1    Bonneau, D.2    Frezal, J.3    Munnich, A.4    Dufier, J.L.5
  • 26
    • 0027270053 scopus 로고
    • Recessive mutations in the gene encoding the beta subunit of rod phosphodiesterase in patients with retinitis pigmentosa
    • McLaughlin, M. E., Sandberg, M. A., Berson, E. L., and Dryja, T. P. (1993). Recessive mutations in the gene encoding the beta subunit of rod phosphodiesterase in patients with retinitis pigmentosa. Nat. Genet. 4: 130-134.
    • (1993) Nat. Genet. , vol.4 , pp. 130-134
    • McLaughlin, M.E.1    Sandberg, M.A.2    Berson, E.L.3    Dryja, T.P.4
  • 27
    • 0026072333 scopus 로고
    • Identification of a nonsense mutation in the rod photoreceptor cGMP-phosphodiesterase beta subunit gene of the rd mouse
    • Pittler, S. J., and Baehr, W. (1991). Identification of a nonsense mutation in the rod photoreceptor cGMP-phosphodiesterase beta subunit gene of the rd mouse. Proc. Natl. Acad. Sci. USA 88: 8322-8326.
    • (1991) Proc. Natl. Acad. Sci. USA , vol.88 , pp. 8322-8326
    • Pittler, S.J.1    Baehr, W.2
  • 28
    • 0027262347 scopus 로고
    • Irish setter dogs affected with rod/cone dysplasia contain a nonsense mutation in the rod cGMP phosphodiesterase b-subunit gene
    • Suber, M. L., et al. (1993). Irish setter dogs affected with rod/cone dysplasia contain a nonsense mutation in the rod cGMP phosphodiesterase b-subunit gene. Proc. Natl. Acad. Sci. USA 90: 3968-3972.
    • (1993) Proc. Natl. Acad. Sci. USA , vol.90 , pp. 3968-3972
    • Suber, M.L.1
  • 29
    • 0026591170 scopus 로고
    • Retinal degeneration is rescued in transgenic rd mice by expression of the cGMP phosphodiesterase and β subunit
    • Lem, J., et al. (1992). Retinal degeneration is rescued in transgenic rd mice by expression of the cGMP phosphodiesterase and β subunit. Proc. Natl. Acad. Sci. USA 89: 4422-4426.
    • (1992) Proc. Natl. Acad. Sci. USA , vol.89 , pp. 4422-4426
    • Lem, J.1
  • 30
    • 0029893012 scopus 로고    scopus 로고
    • Photoreceptor cell rescue in retinal degeneration (rd) mice by in vivo gene therapy
    • Bennett, J., et al. (1996). Photoreceptor cell rescue in retinal degeneration (rd) mice by in vivo gene therapy. Nat. Med. 2: 649-654.
    • (1996) Nat. Med. , vol.2 , pp. 649-654
    • Bennett, J.1
  • 31
    • 0030759730 scopus 로고    scopus 로고
    • Rescue of photoreceptor function by AAV-mediated gene transfer in a mouse model of inherited retinal degeneration
    • Jomary, C., Vincent, K., Grist, J., Neal, M., and Jones, S. (1997). Rescue of photoreceptor function by AAV-mediated gene transfer in a mouse model of inherited retinal degeneration. Gene Ther. 4: 683-690.
    • (1997) Gene Ther. , vol.4 , pp. 683-690
    • Jomary, C.1    Vincent, K.2    Grist, J.3    Neal, M.4    Jones, S.5
  • 32
    • 0008937542 scopus 로고    scopus 로고
    • Cross-species comparison of in vivo reporter gene expression after rAAV-mediated retinal transduction
    • in press.
    • Bennett, J., Anand, V., Acland, G. M., and Maguire, A. M. (2000). Cross-species comparison of in vivo reporter gene expression after rAAV-mediated retinal transduction. Methods Enzymol.: in press.
    • (2000) Methods Enzymol.
    • Bennett, J.1    Anand, V.2    Acland, G.M.3    Maguire, A.M.4
  • 33
    • 0031795296 scopus 로고    scopus 로고
    • Encapsidated adenovirus mini-chromosome-mediated delivery of genes to the retina: Application to the rescue of photoreceptor degeneration
    • Kumar-Singh, R., and Farber, D. (1998). Encapsidated adenovirus mini-chromosome-mediated delivery of genes to the retina: Application to the rescue of photoreceptor degeneration. Hum. Mol. Genet. 7: 1893-1900.
    • (1998) Hum. Mol. Genet. , vol.7 , pp. 1893-1900
    • Kumar-Singh, R.1    Farber, D.2
  • 34
    • 0032816002 scopus 로고    scopus 로고
    • Rescue from photoreceptor degeneration in the rd mouse by human immunodeficiency virus vector-mediated gene transfer
    • Takahashi, M., Miyoshi, H., Verma, I. M., and Gage, F. H. (1999). Rescue from photoreceptor degeneration in the rd mouse by human immunodeficiency virus vector-mediated gene transfer. J. Virol. 73: 7812-7816.
    • (1999) J. Virol. , vol.73 , pp. 7812-7816
    • Takahashi, M.1    Miyoshi, H.2    Verma, I.M.3    Gage, F.H.4
  • 35
    • 0026058548 scopus 로고
    • Functional heterogeneity of mutant rhodopsins responsible for autosomal dominant retinitis pigmentosa
    • Sung, C.-H., Schneider, B. G., Papermaster, D., and Nathans, J. (1991). Functional heterogeneity of mutant rhodopsins responsible for autosomal dominant retinitis pigmentosa. Proc. Natl. Acad. Sci. USA 88: 8840-8844.
    • (1991) Proc. Natl. Acad. Sci. USA , vol.88 , pp. 8840-8844
    • Sung, C.-H.1    Schneider, B.G.2    Papermaster, D.3    Nathans, J.4
  • 36
    • 0028287273 scopus 로고
    • Structure and function in rhodopsin. Point mutations associated with autosomal dominant retinitis pigmentosa
    • Kaushal, S., and Khorana, H. (1994). Structure and function in rhodopsin. Point mutations associated with autosomal dominant retinitis pigmentosa. Biochemistry 33: 6121-6128.
    • (1994) Biochemistry , vol.33 , pp. 6121-6128
    • Kaushal, S.1    Khorana, H.2
  • 37
    • 0027987902 scopus 로고
    • Ribozyme-mediated repair of defective mRNA by targeted trans-splicing
    • Sullenger, B., and Cech, T. (1994). Ribozyme-mediated repair of defective mRNA by targeted trans-splicing. Nature 371: 619.
    • (1994) Nature , vol.371 , pp. 619
    • Sullenger, B.1    Cech, T.2
  • 38
    • 0031880563 scopus 로고    scopus 로고
    • Ribozyme rescue of photoreceptor cells in a transgenic rat model of autosomal dominant retinitis pigmentosa
    • Lewin, A. S., et al. (1998). Ribozyme rescue of photoreceptor cells in a transgenic rat model of autosomal dominant retinitis pigmentosa. Nat. Med. 4: 967-971.
    • (1998) Nat. Med. , vol.4 , pp. 967-971
    • Lewin, A.S.1
  • 39
    • 0030069494 scopus 로고    scopus 로고
    • Mechanisms of photoreceptor death in retinal degenerations
    • Adler, R. (1996). Mechanisms of photoreceptor death in retinal degenerations. Arch. Ophthalmol. 114: 79-83.
    • (1996) Arch. Ophthalmol. , vol.114 , pp. 79-83
    • Adler, R.1
  • 41
    • 0028331785 scopus 로고
    • Apoptosis leads to photoreceptor degeneration in inherited retinal dystrophy of RCS rats
    • Tso, M. O. M., et al. (1994). Apoptosis leads to photoreceptor degeneration in inherited retinal dystrophy of RCS rats. Invest. Ophthalmol. Vis. Sci. 36: 2693-2699.
    • (1994) Invest. Ophthalmol. Vis. Sci. , vol.36 , pp. 2693-2699
    • Tso, M.O.M.1
  • 42
    • 0027521914 scopus 로고
    • Apoptosis: Final common pathway of photoreceptor death in rd, rds and rhodopsin mutant mice
    • Chang, G.-Q., Hao, Y., and Wong, F. (1993). Apoptosis: Final common pathway of photoreceptor death in rd, rds and rhodopsin mutant mice. Neuron 11: 595-605.
    • (1993) Neuron , vol.11 , pp. 595-605
    • Chang, G.-Q.1    Hao, Y.2    Wong, F.3
  • 43
    • 0028223006 scopus 로고
    • Linkage of photoreceptor degeneration by apoptosis with inherited defect in phototransduction
    • Lolley, I. R. N., Rong, H., and Craft, C. M. (1994). Linkage of photoreceptor degeneration by apoptosis with inherited defect in phototransduction. Invest. Ophthalmol. Vis. Sci. 35: 358-362.
    • (1994) Invest. Ophthalmol. Vis. Sci. , vol.35 , pp. 358-362
    • Lolley, I.R.N.1    Rong, H.2    Craft, C.M.3
  • 45
    • 0029949082 scopus 로고    scopus 로고
    • bcl-2 overexpression reduces apoptotic photoreceptor cell death in three different retinal degenerations
    • Chen, J., et al. (1996). bcl-2 overexpression reduces apoptotic photoreceptor cell death in three different retinal degenerations. Proc. Natl. Acad. Sci. USA 93: 7042-7047.
    • (1996) Proc. Natl. Acad. Sci. USA , vol.93 , pp. 7042-7047
    • Chen, J.1
  • 46
    • 85037750403 scopus 로고    scopus 로고
    • Genomic and somatic delivery of rhodopsin-promoted bcl-2 results in a mild delay in photoreceptor cell death in the rd/rd mouse
    • Zeng, Y., et al. (1997). Genomic and somatic delivery of rhodopsin-promoted bcl-2 results in a mild delay in photoreceptor cell death in the rd/rd mouse. Invest. Ophthalmol. Vis. Sci. 38: S1133.
    • (1997) Invest. Ophthalmol. Vis. Sci. , vol.38
    • Zeng, Y.1
  • 47
    • 0031713983 scopus 로고    scopus 로고
    • Adenovirus-mediated delivery of rhodopsin-promoted bcl-2 results in a delay in photoreceptor cell death in the rd/rd mouse
    • Bennett, J., et al. (1998). Adenovirus-mediated delivery of rhodopsin-promoted bcl-2 results in a delay in photoreceptor cell death in the rd/rd mouse. Gene Ther. 5: 1156-1164.
    • (1998) Gene Ther. , vol.5 , pp. 1156-1164
    • Bennett, J.1
  • 48
    • 0030997980 scopus 로고    scopus 로고
    • Adenovirus-mediated gene transfer of ciliary neurotrophic factor can prevent photoreceptor degeneration in the retinal degeneration (rd) mouse
    • Cayouette, M., and Gravel, C. (1997). Adenovirus-mediated gene transfer of ciliary neurotrophic factor can prevent photoreceptor degeneration in the retinal degeneration (rd) mouse. Hum. Gene Ther. 8: 423-430.
    • (1997) Hum. Gene Ther. , vol.8 , pp. 423-430
    • Cayouette, M.1    Gravel, C.2
  • 49
    • 0032533962 scopus 로고    scopus 로고
    • Intraocular gene transfer of ciliary neurotrophic factor prevents death and increases responsiveness of rod photoreceptors in the retinal degeneration slow mouse
    • Cayouette, M., Behn, D., Sendtner, M., Lachapelle, P., and Gravel, C. (1998). Intraocular gene transfer of ciliary neurotrophic factor prevents death and increases responsiveness of rod photoreceptors in the retinal degeneration slow mouse. J. Neurosci. 18: 9282-9293.
    • (1998) J. Neurosci. , vol.18 , pp. 9282-9293
    • Cayouette, M.1    Behn, D.2    Sendtner, M.3    Lachapelle, P.4    Gravel, C.5
  • 50
    • 0032917801 scopus 로고    scopus 로고
    • Adenovirally expressed basic fibroblast growth factor rescues photoreceptor cells in RCS rats
    • Akimoto, M., et al. (1999). Adenovirally expressed basic fibroblast growth factor rescues photoreceptor cells in RCS rats. Invest. Ophthalmol. Vis. Sci. 40: 273-279.
    • (1999) Invest. Ophthalmol. Vis. Sci. , vol.40 , pp. 273-279
    • Akimoto, M.1
  • 51
    • 0008158116 scopus 로고    scopus 로고
    • Rescue of photoreceptor degeneration in S334ter(4) mutant rhodopsin transgenic rats by adeno-associated virus (AAV)-mediated delivery of basic fibroblast growth factor
    • McGee, L. H., et al. (1999). Rescue of photoreceptor degeneration in S334ter(4) mutant rhodopsin transgenic rats by adeno-associated virus (AAV)-mediated delivery of basic fibroblast growth factor. Invest. Ophthalmol. Vis. Sci. 40: S936.
    • (1999) Invest. Ophthalmol. Vis. Sci. , vol.40
    • McGee, L.H.1
  • 52
    • 13044263133 scopus 로고    scopus 로고
    • Intravitreous transplantation of encapsulated fibroblasts secreting the human fibroblast growth factor 2 delays photoreceptor cell degeneration in Royal College of Surgeons rats
    • Utteza, Y., et al. (1999). Intravitreous transplantation of encapsulated fibroblasts secreting the human fibroblast growth factor 2 delays photoreceptor cell degeneration in Royal College of Surgeons rats. Proc. Natl. Acad. Sci. USA 96: 3126-3131.
    • (1999) Proc. Natl. Acad. Sci. USA , vol.96 , pp. 3126-3131
    • Utteza, Y.1
  • 53
    • 0029928282 scopus 로고    scopus 로고
    • Retrovirus-mediated suicide gene transduction in the vitreous cavity of the eye: Feasibility in prevention of proliferative vitreoretinopathy
    • Kimura, H., et al. (1996). Retrovirus-mediated suicide gene transduction in the vitreous cavity of the eye: Feasibility in prevention of proliferative vitreoretinopathy. Hum. Gene Ther. 7: 799-808.
    • (1996) Hum. Gene Ther. , vol.7 , pp. 799-808
    • Kimura, H.1
  • 54
    • 0030761353 scopus 로고    scopus 로고
    • Ocular gene therapy: Experimental studies and clinical possibilities
    • Murata, T., et al. (1997). Ocular gene therapy: Experimental studies and clinical possibilities. Ophthalmol. Res. 29: 242-251.
    • (1997) Ophthalmol. Res. , vol.29 , pp. 242-251
    • Murata, T.1


* 이 정보는 Elsevier사의 SCOPUS DB에서 KISTI가 분석하여 추출한 것입니다.