메뉴 건너뛰기




Volumn 7, Issue 4, 1999, Pages 269-283

Gene transfer into the CNS using recombinant adeno-associated virus: Analysis of vector DNA forms resulting in sustained expression

Author keywords

AAV; Brain; Episome; Integration; rAAV

Indexed keywords

BETA GALACTOSIDASE; VIRUS DNA; VIRUS VECTOR;

EID: 0033389722     PISSN: 1061186X     EISSN: None     Source Type: Journal    
DOI: 10.3109/10611869909085510     Document Type: Article
Times cited : (19)

References (45)
  • 2
    • 0029883821 scopus 로고    scopus 로고
    • Effects of gamma irradiation on the transduction of dividing and nondividing cells in brain and muscle of rats by adeno-associated virus vectors
    • Alexander, I.E., Russell, D.W., Spence, A.M. and Miller, A.D. (1996) Effects of gamma irradiation on the transduction of dividing and nondividing cells in brain and muscle of rats by adeno-associated virus vectors. Hum. Gene Ther., 7, 841-850.
    • (1996) Hum. Gene Ther. , vol.7 , pp. 841-850
    • Alexander, I.E.1    Russell, D.W.2    Spence, A.M.3    Miller, A.D.4
  • 4
    • 0014799307 scopus 로고
    • Evidence for a single-stranded adenovirus-associated virus genome: Isolation and separation of complementary single strands
    • Berns, K.I. and Rose, J.A. (1970) Evidence for a single-stranded adenovirus-associated virus genome: isolation and separation of complementary single strands. J. Virol., 5, 693-699.
    • (1970) J. Virol. , vol.5 , pp. 693-699
    • Berns, K.I.1    Rose, J.A.2
  • 6
    • 0030970938 scopus 로고    scopus 로고
    • Recombinant adeno-associated viral vectors mediate long-term transgene expression in muscle
    • Clark, K.R., Sferra, T.J. and Johnson, P.R. (1997) Recombinant adeno-associated viral vectors mediate long-term transgene expression in muscle. Hum. Gene Ther., 8, 659-669.
    • (1997) Hum. Gene Ther. , vol.8 , pp. 659-669
    • Clark, K.R.1    Sferra, T.J.2    Johnson, P.R.3
  • 7
    • 0030458783 scopus 로고    scopus 로고
    • A stable cell line carrying adenovirus-inducible rep and cap genes allows for infectivity titration of adeno-associated virus vectors
    • Clark, K.R., Voulgaropoulou, F. and Johnson, P.R. (1996) A stable cell line carrying adenovirus-inducible rep and cap genes allows for infectivity titration of adeno-associated virus vectors. Gene Therapy, 3, 1124-1132.
    • (1996) Gene Therapy , vol.3 , pp. 1124-1132
    • Clark, K.R.1    Voulgaropoulou, F.2    Johnson, P.R.3
  • 8
    • 0028889443 scopus 로고
    • Cell lines for the production of recombinant adeno-associated virus
    • Clark, K.R., Voulgaropoulou, F., Fraley, D.M. and Johnson, P.R. (1995) Cell lines for the production of recombinant adeno-associated virus. Hum. Gene Ther., 6, 1329-1341.
    • (1995) Hum. Gene Ther. , vol.6 , pp. 1329-1341
    • Clark, K.R.1    Voulgaropoulou, F.2    Fraley, D.M.3    Johnson, P.R.4
  • 9
    • 0033541640 scopus 로고    scopus 로고
    • Highly purified recombinant adeno-assotiated virus vectors are biologically active and free of detectable helper and wild-type viruses
    • Clark, K.R., Liu, X., McGrath, J. and Johnson, P.R. (1999) Highly purified recombinant adeno-assotiated virus vectors are biologically active and free of detectable helper and wild-type viruses. Hum. Gene Ther., 10, 1031-1039.
    • (1999) Hum. Gene Ther. , vol.10 , pp. 1031-1039
    • Clark, K.R.1    Liu, X.2    McGrath, J.3    Johnson, P.R.4
  • 10
    • 0029944989 scopus 로고    scopus 로고
    • Comparison of promoter strengths on gene delivery into mammalian brain cells using AAV vectors
    • Doll, R.F., Crandall, J.E., Dyer, C.A., Aucoin, J.M. and Smith, F.I. (1996) Comparison of promoter strengths on gene delivery into mammalian brain cells using AAV vectors. Gene Therapy, 3, 437-447.
    • (1996) Gene Therapy , vol.3 , pp. 437-447
    • Doll, R.F.1    Crandall, J.E.2    Dyer, C.A.3    Aucoin, J.M.4    Smith, F.I.5
  • 11
    • 0030000767 scopus 로고    scopus 로고
    • Efficient transduction of human neurons with an adeno-associated virus vector
    • Du, B., Wu, P., Boldt-Houle, D.M. and Terwilliger, E.F. (1996) Efficient transduction of human neurons with an adeno-associated virus vector. Gene Therapy, 3, 254-261.
    • (1996) Gene Therapy , vol.3 , pp. 254-261
    • Du, B.1    Wu, P.2    Boldt-Houle, D.M.3    Terwilliger, E.F.4
  • 12
    • 0031691257 scopus 로고    scopus 로고
    • Circular intermediates of recombinant adeno-associated virus have defined structural characteristics responsible for long-term episomal persistence in muscle tissue
    • Duan, D., Sharma, P., Yang, J., Yue, Y., Dudus, L., Zhang, Y., Fisher, K.J. and Engelhardt, J.F. (1998) Circular intermediates of recombinant adeno-associated virus have defined structural characteristics responsible for long-term episomal persistence in muscle tissue. J. Virol., 72, 8568-8577.
    • (1998) J. Virol. , vol.72 , pp. 8568-8577
    • Duan, D.1    Sharma, P.2    Yang, J.3    Yue, Y.4    Dudus, L.5    Zhang, Y.6    Fisher, K.J.7    Engelhardt, J.F.8
  • 17
    • 0028783719 scopus 로고
    • Recombinant junctions formed by site-specific integration of adeno-associated virus into an episome
    • Giraud, C., Winocour, E. and Berns, K.I. (1995) Recombinant junctions formed by site-specific integration of adeno-associated virus into an episome. J. Virol., 69, 6917-6924.
    • (1995) J. Virol. , vol.69 , pp. 6917-6924
    • Giraud, C.1    Winocour, E.2    Berns, K.I.3
  • 18
    • 0028789833 scopus 로고
    • Development and application of herpes simplex virus vectors for human gene therapy
    • Glorioso, J.C., DeLuca, N.A. and Fink, D.J. (1995) Development and application of herpes simplex virus vectors for human gene therapy. Annu. Rev. Microbiol., 49, 675-710.
    • (1995) Annu. Rev. Microbiol. , vol.49 , pp. 675-710
    • Glorioso, J.C.1    DeLuca, N.A.2    Fink, D.J.3
  • 19
    • 0014202537 scopus 로고
    • Selective extraction of polyoma DNA from infected mouse cell cultures
    • Hirt, B. (1967) Selective extraction of polyoma DNA from infected mouse cell cultures. J. Mol. Biol., 26, 365-369.
    • (1967) J. Mol. Biol. , vol.26 , pp. 365-369
    • Hirt, B.1
  • 20
    • 0028169741 scopus 로고
    • Long-term gene expression and phenotypic correction using adeno-associated virus vectors in the mammalian brain
    • Kaplitt, M.G., Leone, P., Samulski, R.J., Xiao, X., Pfaff, D.W., O'Malley, K.L. and During, M.J. (1994) Long-term gene expression and phenotypic correction using adeno-associated virus vectors in the mammalian brain. Nature Genet., 8, 148-154.
    • (1994) Nature Genet. , vol.8 , pp. 148-154
    • Kaplitt, M.G.1    Leone, P.2    Samulski, R.J.3    Xiao, X.4    Pfaff, D.W.5    O'Malley, K.L.6    During, M.J.7
  • 21
    • 0343807515 scopus 로고    scopus 로고
    • The principles of gene therapy for the nervous system
    • Karpati, G., Lochmuller, H.J.N. and Durham, H. (1996) The principles of gene therapy for the nervous system. TINS, 19, 49-54.
    • (1996) TINS , vol.19 , pp. 49-54
    • Karpati, G.1    Lochmuller, H.J.N.2    Durham, H.3
  • 23
    • 0033583937 scopus 로고    scopus 로고
    • Generation of aberrant sprouting in the adult rat brain by GAP-43 somatic gene transfer
    • Klein, R.L., McNamara, R.K., King, M.A., Lenox, R.H., Muzyczka, N. and Meyer, E.M. (1999) Generation of aberrant sprouting in the adult rat brain by GAP-43 somatic gene transfer. Brain Res., 832, 136-144.
    • (1999) Brain Res. , vol.832 , pp. 136-144
    • Klein, R.L.1    McNamara, R.K.2    King, M.A.3    Lenox, R.H.4    Muzyczka, N.5    Meyer, E.M.6
  • 26
    • 0033585514 scopus 로고    scopus 로고
    • Adeno-associated virus-mediated gene transfer to the brain: Duration and modulation of expression
    • Lo, W.D., Qu, G., Sierra, T.J., Clark, R., Chen, R. and Johnson, P.R. (1999) Adeno-associated virus-mediated gene transfer to the brain: duration and modulation of expression. Hum. Gene Ther., 10, 201-213.
    • (1999) Hum. Gene Ther. , vol.10 , pp. 201-213
    • Lo, W.D.1    Qu, G.2    Sierra, T.J.3    Clark, R.4    Chen, R.5    Johnson, P.R.6
  • 27
    • 0031456051 scopus 로고    scopus 로고
    • Midbrain injection of recombinant adeno-associated virus encoding rat glial cell line-derived neurotrophic factor protects nigral neurons in a progressive 6-hydroxydopamine-induced degeneration model of Parkinson's disease in rats
    • Mandel, R.J., Spratt, S.K., Snyder, R.O. and Leff, S.E. (1997) Midbrain injection of recombinant adeno-associated virus encoding rat glial cell line-derived neurotrophic factor protects nigral neurons in a progressive 6-hydroxydopamine-induced degeneration model of Parkinson's disease in rats. Proc. Natl. Acad. Sci. USA, 94, 14 083-14 088.
    • (1997) Proc. Natl. Acad. Sci. USA , vol.94 , pp. 14083-14088
    • Mandel, R.J.1    Spratt, S.K.2    Snyder, R.O.3    Leff, S.E.4
  • 28
    • 0030003480 scopus 로고    scopus 로고
    • Differential and persistent expression patterns of CNS gene transfer by an adeno-associated virus (AAV) vector
    • McCown, T.J., Xiao, X., Li, J., Breese, G.R. and Sumulski, R.J. (1996) Differential and persistent expression patterns of CNS gene transfer by an adeno-associated virus (AAV) vector. Brain Res., 713, 99-107.
    • (1996) Brain Res. , vol.713 , pp. 99-107
    • McCown, T.J.1    Xiao, X.2    Li, J.3    Breese, G.R.4    Sumulski, R.J.5
  • 29
    • 0023889191 scopus 로고
    • Adeno-associated virus general transduction vectors: Analysis of proviral structures
    • McLaughlin, S.K., Collis, P., Hermonat, P.L. and Muzyczka, N. (1988) Adeno-associated virus general transduction vectors: analysis of proviral structures. J. Virol., 62, 1963-1973.
    • (1988) J. Virol. , vol.62 , pp. 1963-1973
    • McLaughlin, S.K.1    Collis, P.2    Hermonat, P.L.3    Muzyczka, N.4
  • 31
    • 0032990410 scopus 로고    scopus 로고
    • Isolation of recombinant adeno-associated virus vector-cellular DNA junctions from mouse liver
    • Nakai, H., Iwaki, Y., Kay, M.A. and Couto, L.B. (1999) Isolation of recombinant adeno-associated virus vector-cellular DNA junctions from mouse liver. J. Virol., 73, 5438-5447.
    • (1999) J. Virol. , vol.73 , pp. 5438-5447
    • Nakai, H.1    Iwaki, Y.2    Kay, M.A.3    Couto, L.B.4
  • 32
    • 0031014887 scopus 로고    scopus 로고
    • Efficient transduction of green fluorescent protein in spinal cord neurons using adeno-associated virus vectors containing cell type-specific promoters
    • Pecl, A.L., Zolotukhin, S., Schrimsher, G.W., Muzyczka, N. and Reier, P.J. (1997) Efficient transduction of green fluorescent protein in spinal cord neurons using adeno-associated virus vectors containing cell type-specific promoters. Gene Therapy, 4, 16-24.
    • (1997) Gene Therapy , vol.4 , pp. 16-24
    • Pecl, A.L.1    Zolotukhin, S.2    Schrimsher, G.W.3    Muzyczka, N.4    Reier, P.J.5
  • 33
    • 0033106311 scopus 로고    scopus 로고
    • Evaluation of adeno-associated virus-mediated gene transfer into the rat retina by clinical fluorescence photography
    • Rolling, F., Shen, W.Y., Tabarias, H., Constable, I., Kanagasingam, Y., Barry, C.J. and Rakoczy, P.E. (1999) Evaluation of adeno-associated virus-mediated gene transfer into the rat retina by clinical fluorescence photography. Hum. Gene Ther., 10, 641-648.
    • (1999) Hum. Gene Ther. , vol.10 , pp. 641-648
    • Rolling, F.1    Shen, W.Y.2    Tabarias, H.3    Constable, I.4    Kanagasingam, Y.5    Barry, C.J.6    Rakoczy, P.E.7
  • 34
    • 0028577595 scopus 로고
    • Adeno-associated virus vectors preferentially transduce cells in S phase
    • Russell, D.W., Miller, A.D. and Alexander, I.A. (1994) Adeno-associated virus vectors preferentially transduce cells in S phase. Proc. Natl. Acad. Sci. USA, 91, 8915-8919.
    • (1994) Proc. Natl. Acad. Sci. USA , vol.91 , pp. 8915-8919
    • Russell, D.W.1    Miller, A.D.2    Alexander, I.A.3
  • 36
    • 0024311525 scopus 로고
    • Helper-free stocks of recombinant adeno-associated viruses: Normal integration does not require viral gene expression
    • Samulski, R.J., Chang, L.S. and Shenk, T. (1989) Helper-free stocks of recombinant adeno-associated viruses: normal integration does not require viral gene expression. J. Virol., 63, 3822-3828.
    • (1989) J. Virol. , vol.63 , pp. 3822-3828
    • Samulski, R.J.1    Chang, L.S.2    Shenk, T.3
  • 37
    • 0023216839 scopus 로고
    • A recombinant plasmid from which an infectious adeno-associated virus genome can be excised in vitro and its use to study viral replication
    • Samulski, R.J., Long-Sheng, C. and Shenk, T. (1987) A recombinant plasmid from which an infectious adeno-associated virus genome can be excised in vitro and its use to study viral replication. J. Virol., 61, 3096-3101.
    • (1987) J. Virol. , vol.61 , pp. 3096-3101
    • Samulski, R.J.1    Long-Sheng, C.2    Shenk, T.3
  • 38
  • 40
    • 0033030906 scopus 로고    scopus 로고
    • Gene therapy in the central nervous system: The use of recombinant retroviruses
    • Suhr, S.T. and Gage, F.H. (1999) Gene therapy in the central nervous system: the use of recombinant retroviruses. Arch. Neurol., 56, 287-292.
    • (1999) Arch. Neurol. , vol.56 , pp. 287-292
    • Suhr, S.T.1    Gage, F.H.2
  • 41
    • 0023552653 scopus 로고
    • Oligonucleotide probes for the screening of recombinant DNA libraries
    • S.L. Berger and A.R. Kimmel (Eds.) (Harcourt Brace Jovanovich Publishers, San Diego, CA)
    • Wallace, R.B. and Miyada, C.G. (1987) Oligonucleotide probes for the screening of recombinant DNA libraries. In Guide to Molecular Cloning Techniques, S.L. Berger and A.R. Kimmel (Eds.) (Harcourt Brace Jovanovich Publishers, San Diego, CA) pp. 432-442.
    • (1987) Guide to Molecular Cloning Techniques , pp. 432-442
    • Wallace, R.B.1    Miyada, C.G.2
  • 42
    • 0028307303 scopus 로고
    • Adeno-associated virus (AAV) Rep proteins mediate complex formation between AAV DNA and its integration site in human DNA
    • Weitzman, M.D., Kyostio, S.R., Kotin, R.M. and Owens, R.A. (1994) Adeno-associated virus (AAV) Rep proteins mediate complex formation between AAV DNA and its integration site in human DNA. Proc. Natl. Acad. Sci. USA, 91, 5808-5812.
    • (1994) Proc. Natl. Acad. Sci. USA , vol.91 , pp. 5808-5812
    • Weitzman, M.D.1    Kyostio, S.R.2    Kotin, R.M.3    Owens, R.A.4
  • 43
    • 0031779697 scopus 로고    scopus 로고
    • Adeno-associated virus vector-mediated transgene integration into neurons and other nondividing cell targets
    • Wu, P., Phillips, M.I., Bui, J. and Terwilliger, E.F. (1998) Adeno-associated virus vector-mediated transgene integration into neurons and other nondividing cell targets. J. Virol., 72, 5919-5926.
    • (1998) J. Virol. , vol.72 , pp. 5919-5926
    • Wu, P.1    Phillips, M.I.2    Bui, J.3    Terwilliger, E.F.4
  • 44
    • 0031016643 scopus 로고    scopus 로고
    • A novel 165-base-pair terminal repeat sequence is the sole cis requirement for the adeno-associated virus life cycle
    • Xiao, X., Xiao, W., Li, J. and Samulski, R.J. (1997) A novel 165-base-pair terminal repeat sequence is the sole cis requirement for the adeno-associated virus life cycle. J. Virol., 71, 941-948.
    • (1997) J. Virol. , vol.71 , pp. 941-948
    • Xiao, X.1    Xiao, W.2    Li, J.3    Samulski, R.J.4
  • 45
    • 0029843596 scopus 로고    scopus 로고
    • Efficient long-term gene transfer into muscle tissue of immunocompetent mice by adeno-associated virus vector
    • Xiao, X., Li, J. and Samulski, R.J. (1996) Efficient long-term gene transfer into muscle tissue of immunocompetent mice by adeno-associated virus vector. J. Virol., 70, 8098-8108.
    • (1996) J. Virol. , vol.70 , pp. 8098-8108
    • Xiao, X.1    Li, J.2    Samulski, R.J.3


* 이 정보는 Elsevier사의 SCOPUS DB에서 KISTI가 분석하여 추출한 것입니다.