-
1
-
-
9244234931
-
In vivo model of adeno-associated virus vector persistence and rescue
-
AFIONE, S.A., CONRAD, C.K., KEARNS, W.G., CHUNDURU, S., ADAMS, R., REYNOLDS, T.C., GUGGINO, W.B. CUTTING, G.R., CARTER, B.J., and FLOTTE, T.R. (1996). In vivo model of adeno-associated virus vector persistence and rescue. J. Virol. 70, 3235-3241.
-
(1996)
J. Virol.
, vol.70
, pp. 3235-3241
-
-
Afione, S.A.1
Conrad, C.K.2
Kearns, W.G.3
Chunduru, S.4
Adams, R.5
Reynolds, T.C.6
Guggino, W.B.7
Cutting, G.R.8
Carter, B.J.9
Flotte, T.R.10
-
2
-
-
0031985556
-
Adeno-associated virus gene transfer to mouse retina
-
ALI, R.R., REICHEL, M.B., DEALWIS, M., KANUGA, N., KINNON, C., LEVINSKY, R.J., HUNT, D.M., BHATTACHARYA, S.S., and THRASHER, A.J. (1998). Adeno-associated virus gene transfer to mouse retina. Hum. Gene Ther. 9, 81-86.
-
(1998)
Hum. Gene Ther.
, vol.9
, pp. 81-86
-
-
Ali, R.R.1
Reichel, M.B.2
Dealwis, M.3
Kanuga, N.4
Kinnon, C.5
Levinsky, R.J.6
Hunt, D.M.7
Bhattacharya, S.S.8
Thrasher, A.J.9
-
3
-
-
0031455575
-
Real-time, noninvasive in vivo assessment of adeno-associated virus-mediated retinal transduction
-
BENNETT, J., DUAN, D.S., ENGELHARDT J.F., and MAGUIRE, A.M. (1997). Real-time, noninvasive in vivo assessment of adeno-associated virus-mediated retinal transduction. Invest. Ophthalmol. Vis. Sci. 38, 2857-2863.
-
(1997)
Invest. Ophthalmol. Vis. Sci.
, vol.38
, pp. 2857-2863
-
-
Bennett, J.1
Duan, D.S.2
Engelhardt, J.F.3
Maguire, A.M.4
-
4
-
-
0029768758
-
Biology of adeno-associated virus
-
K. Berns and C. Giraud, eds. (Springer-Verlag, Berlin)
-
BERNS, K., and GIRAUD, C. (1996). Biology of adeno-associated virus. In Adeno-Associated Virus (AAV) Vectors in Gene Therapy. K. Berns and C. Giraud, eds. (Springer-Verlag, Berlin) pp. 1-24.
-
(1996)
Adeno-Associated Virus (AAV) Vectors in Gene Therapy
, pp. 1-24
-
-
Berns, K.1
Giraud, C.2
-
5
-
-
0029741735
-
Safety of single-dose administration of an adenoassociated virus (AAV)-CFTR vector in the primate lung
-
CONRAD, C.K., ALLEN, S.S., AFIONE, S.A., REYNOLDS, T.C., BECK, S.E., FEEMAKI, M., BARRAZZAORTIZ, X., ADAMS, R., ASKIN, F.B., CARTER, B.J., GUGGINO, W.B., and FLOTTE, T.R. (1996). Safety of single-dose administration of an adenoassociated virus (AAV)-CFTR vector in the primate lung. Gene Ther. 3, 658-668.
-
(1996)
Gene Ther.
, vol.3
, pp. 658-668
-
-
Conrad, C.K.1
Allen, S.S.2
Afione, S.A.3
Reynolds, T.C.4
Beck, S.E.5
Feemaki, M.6
Barrazzaortiz, X.7
Adams, R.8
Askin, F.B.9
Carter, B.J.10
Guggino, W.B.11
Flotte, T.R.12
-
6
-
-
0028903353
-
A human retinal pigment epithelial cell line that retains epithelial characteristics after prolonged culture
-
DAVIS, A., BERNSTEIN, P., BOK, D., TURNER, J., NACHTIGAL, M., and HUNT, R. (1995). A human retinal pigment epithelial cell line that retains epithelial characteristics after prolonged culture. Invest. Ophthalmol. Vis. Sci. 36, 955-964.
-
(1995)
Invest. Ophthalmol. Vis. Sci.
, vol.36
, pp. 955-964
-
-
Davis, A.1
Bernstein, P.2
Bok, D.3
Turner, J.4
Nachtigal, M.5
Hunt, R.6
-
7
-
-
0029849257
-
Quantitative analysis of the packaging capacity of recombinant adeno-associated virus
-
DONC, J.Y., FAN, P.D., and FRIZZELL, R.A. (1996). Quantitative analysis of the packaging capacity of recombinant adeno-associated virus. Hum. Gene Ther. 7, 2101-2112.
-
(1996)
Hum. Gene Ther.
, vol.7
, pp. 2101-2112
-
-
Donc, J.Y.1
Fan, P.D.2
Frizzell, R.A.3
-
8
-
-
0031058024
-
Recombinant adeno-associated virus for muscle directed gene therapy
-
FISHER, K.J., JOOSS, K., ALSTON, J., YANG, Y.P., HAECKER, S.E., HIGH, K., PATHAK, R., RAPER, S.E., and WILSON, J.M. (1997). Recombinant adeno-associated virus for muscle directed gene therapy. Nature Med. 3, 306-312.
-
(1997)
Nature Med.
, vol.3
, pp. 306-312
-
-
Fisher, K.J.1
Jooss, K.2
Alston, J.3
Yang, Y.P.4
Haecker, S.E.5
High, K.6
Pathak, R.7
Raper, S.E.8
Wilson, J.M.9
-
9
-
-
0031011667
-
Efficient photoreceptor-targeted gene expression in vivo by recombinant adeno-associated virus
-
FLANNERY, J.G., ZOLOTUKHIN, S., VAQUERO, M.I., LAVAIL, M.M., MUZYCZKA, N., and HAUSWIRTH, W.W. (1997). Efficient photoreceptor-targeted gene expression in vivo by recombinant adeno-associated virus. Proc. Natl. Acad. Sci. U.S.A. 94, 6916-6921.
-
(1997)
Proc. Natl. Acad. Sci. U.S.A.
, vol.94
, pp. 6916-6921
-
-
Flannery, J.G.1
Zolotukhin, S.2
Vaquero, M.I.3
Lavail, M.M.4
Muzyczka, N.5
Hauswirth, W.W.6
-
10
-
-
0031909281
-
A fluorescence video-endoscopy technique for detection of gene transfer and expression
-
FLOTTE, T.R., BECK, S.E., CHESNUT, K., POTTER, M., POIRIER, A., and ZOLOTUKHIN, S. (1998). A fluorescence video-endoscopy technique for detection of gene transfer and expression. Gene Ther. 5, 166-173.
-
(1998)
Gene Ther.
, vol.5
, pp. 166-173
-
-
Flotte, T.R.1
Beck, S.E.2
Chesnut, K.3
Potter, M.4
Poirier, A.5
Zolotukhin, S.6
-
11
-
-
0030924589
-
Evaluation of recombinant adeno-associated virus as a gene transfer vector for the retina
-
GRANT, C.A., PONNAZHAGAN, S., WANG, X.S., SRIVASTAVA, A., and LI, T.S. (1997). Evaluation of recombinant adeno-associated virus as a gene transfer vector for the retina. Curr. Eye Res. 16, 949-956.
-
(1997)
Curr. Eye Res.
, vol.16
, pp. 949-956
-
-
Grant, C.A.1
Ponnazhagan, S.2
Wang, X.S.3
Srivastava, A.4
Li, T.S.5
-
12
-
-
0031255068
-
Mutations in RPE65 cause autosomal recessive childhood-onset severe retinal dystrophy
-
GU, S., THOMPSON, D., SRIKUMARI, S., LORENZ, B., FINCKH, U., NICOLETTI, A., MURTHY, K.R., RATHMANN, M., KUMARAMANICKAVEL, G., DENTON, M.J., and GAL., A. (1997). Mutations in RPE65 cause autosomal recessive childhood-onset severe retinal dystrophy. Nature Genet. 17, 194-197.
-
(1997)
Nature Genet.
, vol.17
, pp. 194-197
-
-
Gu, S.1
Thompson, D.2
Srikumari, S.3
Lorenz, B.4
Finckh, U.5
Nicoletti, A.6
Murthy, K.R.7
Rathmann, M.8
Kumaramanickavel, G.9
Denton, M.J.10
Gal, A.11
-
13
-
-
0030874508
-
Cell-mediated immune response and stability of intraocular transgene expression after adenovirus-mediated delivery
-
HOFFMAN, L.M., MAGUIRE, A.M., and BENNETT, J. (1997). Cell-mediated immune response and stability of intraocular transgene expression after adenovirus-mediated delivery. Invest. Ophthalmol. Vis. Sci. 38, 2224-2233.
-
(1997)
Invest. Ophthalmol. Vis. Sci.
, vol.38
, pp. 2224-2233
-
-
Hoffman, L.M.1
Maguire, A.M.2
Bennett, J.3
-
14
-
-
0028169741
-
Long-term gene expression and phenotypic correction using adeno-associated virus vectors in the mammalian brain
-
KAPLITT, M.G., LEONE, P., SAMULSKI, R.J., XIAO, X., PFAFF, D.W., OMALLEY, K.L., and DURING, M.J. (1994). Long-term gene expression and phenotypic correction using adeno-associated virus vectors in the mammalian brain. Nature Genet. 8, 148-154.
-
(1994)
Nature Genet.
, vol.8
, pp. 148-154
-
-
Kaplitt, M.G.1
Leone, P.2
Samulski, R.J.3
Xiao, X.4
Pfaff, D.W.5
Omalley, K.L.6
During, M.J.7
-
15
-
-
84984763750
-
Mutation of the gene encoding cellular retinaldehyde-binding protein in autosomal recessive retinitis pigmentosa
-
MAW, M.A., KENNEDY, B., KNIGHT, A., BRIDGES, R., ROTH, K.E., MANI, E.J., MUKKADAN, J.K., NANCARROW, D., CRABB, J.W., and DENTON, M.J. (1997). Mutation of the gene encoding cellular retinaldehyde-binding protein in autosomal recessive retinitis pigmentosa. Nature Genet. 17, 198-200.
-
(1997)
Nature Genet.
, vol.17
, pp. 198-200
-
-
Maw, M.A.1
Kennedy, B.2
Knight, A.3
Bridges, R.4
Roth, K.E.5
Mani, E.J.6
Mukkadan, J.K.7
Nancarrow, D.8
Crabb, J.W.9
Denton, M.J.10
-
16
-
-
0030003480
-
Differential and persistent expression patterns of CNS gene transfer by an adeno-associated virus (AAV) vector
-
McCOWN, T.J., XIAO, X., LI, J., BREESE, G.R., and SAMULSKI, R.J. (1996). Differential and persistent expression patterns of CNS gene transfer by an adeno-associated virus (AAV) vector. Brain Res. 713, 99-107.
-
(1996)
Brain Res.
, vol.713
, pp. 99-107
-
-
McCown, T.J.1
Xiao, X.2
Li, J.3
Breese, G.R.4
Samulski, R.J.5
-
17
-
-
0031983639
-
Direct intramuscular injection with recombinant AAV vectors results in sustained expression in a dog model of hemophilia
-
MONAHAN, P.E., SAMULSKI, R.J., TAZELAAR, J., XIAO, X., NICHOLS, T.C., BELLINGER, D.A., READ, M.S., and WALSH, C.E. (1998). Direct intramuscular injection with recombinant AAV vectors results in sustained expression in a dog model of hemophilia. Gene Ther. 5, 40-49.
-
(1998)
Gene Ther.
, vol.5
, pp. 40-49
-
-
Monahan, P.E.1
Samulski, R.J.2
Tazelaar, J.3
Xiao, X.4
Nichols, T.C.5
Bellinger, D.A.6
Read, M.S.7
Walsh, C.E.8
-
18
-
-
0029990867
-
Gene therapy against an experimental glioma using adeno-associated virus vectors
-
OKADA, H., MIYAMURA, K., ITOH, T., HAGIWARA, M., WAKABAYASHI, T., MIZUNO, M., COLOSI, P., KURTZMAN, G., and YOSHIDA, J. (1996). Gene therapy against an experimental glioma using adeno-associated virus vectors. Gene Ther. 3, 957-964.
-
(1996)
Gene Ther.
, vol.3
, pp. 957-964
-
-
Okada, H.1
Miyamura, K.2
Itoh, T.3
Hagiwara, M.4
Wakabayashi, T.5
Mizuno, M.6
Colosi, P.7
Kurtzman, G.8
Yoshida, J.9
-
19
-
-
0028060363
-
Efficient gene transfer into nondividing cells by adeno-associated virus-based vectors
-
PODSAKOFF, G., WONG, K.K., and CHATTERJEE, S. (1994). Efficient gene transfer into nondividing cells by adeno-associated virus-based vectors. J. Virol. 68, 5656-5666.
-
(1994)
J. Virol.
, vol.68
, pp. 5656-5666
-
-
Podsakoff, G.1
Wong, K.K.2
Chatterjee, S.3
-
20
-
-
0030772504
-
Gene therapy for retinal degeneration
-
REICHEL, M.B., ALI, R.R., HUNT, D.M., and BHATTACHARYA, S.S. (1997). Gene therapy for retinal degeneration. Ophthalmic Res. 29. 261-268.
-
(1997)
Ophthalmic Res.
, vol.29
, pp. 261-268
-
-
Reichel, M.B.1
Ali, R.R.2
Hunt, D.M.3
Bhattacharya, S.S.4
-
21
-
-
0030866312
-
Adeno-associated virus-mediated gene transfer into rat carotid arterie
-
ROLLING, F., NONG, Z., PISVIN, S., and COLLEN, D. (1997). Adeno-associated virus-mediated gene transfer into rat carotid arterie. Gene Ther. 4, 757-761.
-
(1997)
Gene Ther.
, vol.4
, pp. 757-761
-
-
Rolling, F.1
Nong, Z.2
Pisvin, S.3
Collen, D.4
-
22
-
-
0024311525
-
Helper-free stocks of recombinant adeno-associated viruses: Normal integration does not require viral gene expression
-
SAMULSKI, R.J., CHANG, L.S., and SHENK, T. (1989). Helper-free stocks of recombinant adeno-associated viruses: Normal integration does not require viral gene expression. J. Virol. 63, 3822-3828.
-
(1989)
J. Virol.
, vol.63
, pp. 3822-3828
-
-
Samulski, R.J.1
Chang, L.S.2
Shenk, T.3
-
23
-
-
0031657921
-
Expression of cell adhesion molecules and vascular endothelial growth factor in experimental choroidal neovascularisation in the rat
-
SHEN, W.Y., YU, M., BARRY, C.J., CONSTABLE, I.J., and RAKOCZY, P.E. (1999). Expression of cell adhesion molecules and vascular endothelial growth factor in experimental choroidal neovascularisation in the rat. Br. J. Ophthalmol 82, 1063-1071.
-
(1999)
Br. J. Ophthalmol
, vol.82
, pp. 1063-1071
-
-
Shen, W.Y.1
Yu, M.2
Barry, C.J.3
Constable, I.J.4
Rakoczy, P.E.5
-
24
-
-
0031746558
-
Characterization of wild-type adeno-associated virus type 2-like particles generated during recombinant viral vector production and strategies for their elimination
-
WANG, X.S., KHUNTIRAT, B., QING, K., PONNAZHAGAN, S., KUBE, D.M., ZHOU, S., DWARKI, V.J., and SRIVASTAVA, A. (1998). Characterization of wild-type adeno-associated virus type 2-like particles generated during recombinant viral vector production and strategies for their elimination. J. Virol. 72, 5472-5480.
-
(1998)
J. Virol.
, vol.72
, pp. 5472-5480
-
-
Wang, X.S.1
Khuntirat, B.2
Qing, K.3
Ponnazhagan, S.4
Kube, D.M.5
Zhou, S.6
Dwarki, V.J.7
Srivastava, A.8
-
25
-
-
0029843596
-
Long-term and efficient in vivo gene transfer into muscle tissue of immunocompetent mice with an rAAV vector
-
XIAO, X., LI, J., and SAMULSKI, R.J. (1996). Long-term and efficient in vivo gene transfer into muscle tissue of immunocompetent mice with an rAAV vector. J. Virol. 70, 8098-8108.
-
(1996)
J. Virol.
, vol.70
, pp. 8098-8108
-
-
Xiao, X.1
Li, J.2
Samulski, R.J.3
-
26
-
-
0031104792
-
Gene transfer by adeno-associated virus vectors into the central nervous system
-
XIAO, X., LI, J., McCOWN, T.J., and SAMULSKI, R.J. (1997). Gene transfer by adeno-associated virus vectors into the central nervous system. Exp. Neurol. 144, 113-124.
-
(1997)
Exp. Neurol.
, vol.144
, pp. 113-124
-
-
Xiao, X.1
Li, J.2
McCown, T.J.3
Samulski, R.J.4
-
27
-
-
2642642141
-
Production of high-titer recombinant adeno-associated virus vectors in the absence of helper adenovirus
-
XIAO, X., LI, J., and SAMULSKI, R.J. (1998). Production of high-titer recombinant adeno-associated virus vectors in the absence of helper adenovirus. J. Virol. 72, 2224-2232.
-
(1998)
J. Virol.
, vol.72
, pp. 2224-2232
-
-
Xiao, X.1
Li, J.2
Samulski, R.J.3
|