Feasibility of gene therapy in Gaucher disease using an adeno-associated virus vector

Journal of Human Genetics

Volumn 49, Issue 10, 2004, Pages 536-543

  Hong, Young Bin ^a   Kim, Eun Young ^a   Yoo, Han Wook ^b   Jung, Sung Chul ^a,c  

^a Korea National Institute of Health   (South Korea)

^b University of Ulsan College of Medicine   (South Korea)

^c Ewha Womans University School of Medicine   (South Korea)

Author keywords

AAV vector; Adeno associated virus; Gaucher disease; Gene therapy; Glucocerebrosidase

Indexed keywords

COMPLEMENTARY DNA; ELONGATION FACTOR 1ALPHA; GLUCOSYLCERAMIDASE; PARVOVIRUS VECTOR;

ANIMAL EXPERIMENT; ARTICLE; CONTROLLED STUDY; EMBRYO; ENZYME ACTIVITY; FIBROBLAST; GAUCHER DISEASE; GENE THERAPY; GENE TRANSFER; HUMAN; HUMAN CELL; LIVER; LUNG; MOUSE; NONHUMAN; PORTAL VEIN; PROMOTER REGION; PROTEIN EXPRESSION; SIGNAL TRANSDUCTION; SPLEEN; VIRUS RECOMBINANT; WILD TYPE;

ANIMALS; BASE SEQUENCE; CELL LINE; DEPENDOVIRUS; DNA PRIMERS; ENDOCYTOSIS; FEASIBILITY STUDIES; GAUCHER DISEASE; GENE THERAPY; GENETIC VECTORS; HUMANS; MICE; MICE, INBRED C57BL;

ADENO-ASSOCIATED VIRUS;

EID: 8644286142     PISSN: 14345161     EISSN: None     Source Type: Journal    
DOI: 10.1007/s10038-004-0186-8     Document Type: Article

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