Mechanism of Action and Clinical Application of Tafamidis in Hereditary Transthyretin Amyloidosis

Neurology and Therapy

Volumn 5, Issue 1, 2016, Pages

  Coelho, Teresa ^a   Merlini, Giampaolo ^b   Bulawa, Christine E ^c   Fleming, James A ^c   Judge, Daniel P ^d   Kelly, Jeffery W ^e   Maurer, Mathew S ^f   Planté Bordeneuve, Violaine ^g   Labaudinière, Richard ^h   Mundayat, Rajiv ^c   Riley, Steve ^c   Lombardo, Ilise ^j   Huertas, Pedro ⁱ  

^a HOSPITAL DE SANTO ANTÓNIO   (Portugal)

^b UNIVERSITY OF PAVIA   (Italy)

^c PFIZER INC   (United States)

^d JOHNS HOPKINS UNIVERSITY SCHOOL OF MEDICINE   (United States)

^e SCRIPPS RESEARCH INSTITUTE   (United States)

^f Columbia University College of Physicians and Surgeons ^*  (United States)

^g HENRI MONDOR HOSPITAL   (France)

^h Labaudiniere Consulting LLC   (United States)

ⁱ HARVARD MEDICAL SCHOOL   (United States)

^j FORUM Pharmaceuticals   (United States)

more..

Author keywords

Familial amyloid cardiomyopathy; Familial amyloid polyneuropathy; Hereditary TTR amyloid cardiomyopathy; Pharmacology; Senile systemic amyloidosis; Therapeutic use; Wild type TTR amyloidosis

Indexed keywords

DIFLUNISAL; NONSTEROID ANTIINFLAMMATORY AGENT; TAFAMIDIS;

AMYLOIDOSIS; ATRIAL FIBRILLATION; BRAIN HEMORRHAGE; CHILD PUGH SCORE; CREATININE CLEARANCE; CRYSTAL STRUCTURE; DIARRHEA; DRUG BIOAVAILABILITY; FAINTNESS; GENE MUTATION; GENE SEQUENCE; GENOTYPE PHENOTYPE CORRELATION; HEART EJECTION FRACTION; HEART FAILURE; HUMAN; POLYNEUROPATHY; PRIORITY JOURNAL; QUALITY OF LIFE; RANDOMIZED CONTROLLED TRIAL (TOPIC); REVIEW; SEQUENCE ANALYSIS; URINARY TRACT INFECTION;

EID: 85006228054     PISSN: 21938253     EISSN: 21936536     Source Type: Journal    
DOI: 10.1007/s40120-016-0040-x     Document Type: Review

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