Cystic fibrosis in young children: A review of disease manifestation, progression, and response to early treatment

Journal of Cystic Fibrosis

Volumn 15, Issue 2, 2016, Pages 147-157

  VanDevanter, Donald R ^a   Kahle, Jennifer S ^b   O'Sullivan, Amy K ^c   Sikirica, Slaven ^c   Hodgkins, Paul S ^c  

^a CASE WESTERN RESERVE UNIVERSITY SCHOOL OF MEDICINE   (United States)

^b BPS International   (United States)

^c VERTEX PHARMACEUTICALS   (United States)

Author keywords

Child; Comprehensive survey; Data collection; Disease progression; Health status; Infant; Preschool

Indexed keywords

CYSTIC FIBROSIS TRANSMEMBRANE CONDUCTANCE REGULATOR;

CHILD; CHILDHOOD DISEASE; CYSTIC FIBROSIS; DIGESTIVE SYSTEM; DISEASE COURSE; EARLY DIAGNOSIS; HUMAN; META ANALYSIS; MORBIDITY; NEWBORN SCREENING; PRESCHOOL CHILD; PROTEIN EXPRESSION; RESPIRATORY SYSTEM; REVIEW; SYSTEMATIC REVIEW; TREATMENT RESPONSE; DISEASE MANAGEMENT; GLOBAL HEALTH; PREVALENCE; TIME FACTOR;

CHILD; CYSTIC FIBROSIS; DISEASE MANAGEMENT; DISEASE PROGRESSION; GLOBAL HEALTH; HUMANS; PREVALENCE; TIME FACTORS;

EID: 84951064471     PISSN: 15691993     EISSN: 18735010     Source Type: Journal    
DOI: 10.1016/j.jcf.2015.09.008     Document Type: Review

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