Design of shRNA and miRNA for delivery to the CNS

Methods in Molecular Biology

Volumn 1382, Issue , 2016, Pages 67-80

  Cabrera, Gabriela Toro ^a   Mueller, Christian ^a  

^a NONE

Author keywords

AAV; Knockdown; MiRNA; RNAi; ShRNA

Indexed keywords

DNA DIRECTED DNA POLYMERASE ALPHA; DNA DIRECTED RNA POLYMERASE III; LENTIVIRUS VECTOR; MICRORNA; PARVOVIRUS VECTOR; RNA INDUCED SILENCING COMPLEX; SHORT HAIRPIN RNA; VIRUS VECTOR; SMALL INTERFERING RNA;

CELL NUCLEUS; CENTRAL NERVOUS SYSTEM; CYTOPLASM; GENE REPRESSION; GENE SILENCING; GENETIC COMPLEMENTATION; GENETIC SCREENING; NONHUMAN; PROMOTER REGION; RNA CLEAVAGE; RNA INTERFERENCE; VIRAL GENE DELIVERY SYSTEM; VIRAL GENE THERAPY; ADMINISTRATION AND DOSAGE; ADVERSE EFFECTS; DEPENDOPARVOVIRUS; GENE THERAPY; GENE VECTOR; GENETIC ENGINEERING; GENETICS; HEK293 CELL LINE; HUMAN; METABOLISM; PROCEDURES;

CENTRAL NERVOUS SYSTEM; DEPENDOVIRUS; DNA POLYMERASE II; GENE SILENCING; GENETIC ENGINEERING; GENETIC THERAPY; GENETIC VECTORS; HEK293 CELLS; HUMANS; MICRORNAS; PROMOTER REGIONS, GENETIC; RNA, SMALL INTERFERING;

EID: 84948784193     PISSN: 10643745     EISSN: None     Source Type: Book Series    
DOI: 10.1007/978-1-4939-3271-9_5     Document Type: Chapter

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