Manufacturing and characterization of a recombinant adeno-associated virus type 8 reference standard material

Human Gene Therapy

Volumn 25, Issue 11, 2014, Pages 977-987

  Ayuso, Eduard ^a   Blouin, Véronique ^b,c   Lock, Martin ^d   Mcgorray, Susan ^e   Leon, Xavier ^a   Alvira, Mauricio R ^d   Auricchio, Alberto ^f,g   Bucher, Stephanie ^h   Chtarto, Abdelwahed ⁱ   Clark, K Reed ^j,k   Darmon, Christophe ^b,c,l   Doria, Monica ^g   Fountain, Will ^j,k   Gao, Guangping ^m   Gao, Kai ^m,n   Giacca, Mauro ^o   Kleinschmidt, Juergen ^p   Leuchs, Barbara ^p   Melas, Catherine ⁱ   Mizukami, Hiroaki ^q   Müller, Marcus ^p   Noordman, Yvet ^r   Bockstael, Olivier ⁱ   Ozawa, Keiya ^q   Pythoud, Catherine ^s   Sumaroka, Marina ^t   Surosky, Richard ^u   Tenenbaum, Liliane ^s   Van Der Linden, Inge ^r   Weins, Brigitte ^v   Wright, J Fraser ^t,w   Zhang, Xinhua ^t   Zentilin, Lorena ^o   Bosch, Fatima ^a   Snyder, Richard O ^e,x   Moullier, Philippe ^b,c,e   more..

^a UNIVERSITAT AUTÒNOMA DE BARCELONA   (Spain)

^b NANTES UNIVERSITY HOSPITAL   (France)

^c Atlantic Gene Therapies   (France)

^d UNIVERSITY OF PENNSYLVANIA   (United States)

^e UNIVERSITY OF FLORIDA COLLEGE OF MEDICINE   (United States)

^f UNIVERSITY OF NAPLES FEDERICO II   (Italy)

^g TELETHON INSTITUTE OF GENETICS AND MEDICINE TIGEM   (Italy)

^h GÉNÉTHON   (France)

ⁱ FREE UNIVERSITY OF BRUSSELS   (Belgium)

^j THE RESEARCH INSTITUTE AT NATIONWIDE CHILDREN S HOSPITAL   (United States)

^k OHIO STATE UNIVERSITY   (United States)

^l EFS Atlantic BioGMP   (France)

^m UNIVERSITY OF MASSACHUSETTS MEDICAL SCHOOL   (United States)

ⁿ NATIONAL INSTITUTES FOR FOOD AND DRUG CONTROL   (China)

^o INTERNATIONAL CENTRE FOR GENETIC ENGINEERING AND BIOTECHNOLOGY   (Italy)

^p GERMAN CANCER RESEARCH CENTER DKFZ   (Germany)

^q JICHI MEDICAL UNIVERSITY   (Japan)

^r UNIQURE   (Netherlands)

^s LAUSANNE UNIVERSITY HOSPITAL   (Switzerland)

^t CHILDREN S HOSPITAL OF PHILADELPHIA   (United States)

^u SANGAMO BIOSCIENCES INC   (United States)

^v Progen Biotechnik   (Germany)

^w UNIVERSITY OF PENNSYLVANIA   (United States)

^x UNIVERSITY OF FLORIDA   (United States)

more..

Author keywords

[No Author keywords available]

Indexed keywords

ENDOTOXIN; PARVOVIRUS VECTOR; PLASMID VECTOR;

ARTICLE; DENSITY GRADIENT CENTRIFUGATION; EMBRYO; GENOME; HEK293 CELL LINE; HUMAN; HUMAN CELL; LABORATORY; MYCOPLASMA; POLYMERASE CHAIN REACTION; SEROTYPE; TRANSIENT TRANSFECTION; VIRAL GENE THERAPY; VIRUS CAPSID; VIRUS PURIFICATION; DEPENDOPARVOVIRUS; GENE THERAPY; GENETIC TRANSFORMATION; GENETICS; STANDARD; STANDARDS; VIRION; VIRUS CULTURE; VIRUS GENOME;

DEPENDOVIRUS; GENETIC THERAPY; GENOME, VIRAL; HEK293 CELLS; HUMANS; REFERENCE STANDARDS; TRANSFORMATION, GENETIC; VIRION; VIRUS CULTIVATION;

EID: 84910600504     PISSN: 10430342     EISSN: 15577422     Source Type: Journal    
DOI: 10.1089/hum.2014.057     Document Type: Article

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