Cone specific promoter for use in gene therapy of retinal degenerative diseases

Advances in Experimental Medicine and Biology

Volumn 801, Issue , 2014, Pages 695-701

  Dyka, Frank M ^a   Boye, Sanford L ^a   Ryals, Renee C ^a   Chiodo, Vince A ^a   Boye, Shannon E ^a   Hauswirth, William W ^a  

^a UNIVERSITY OF FLORIDA COLLEGE OF MEDICINE   (United States)

Author keywords

Achromatopsia; Adeno associated virus; Chimeric promoter; Cone photoreceptors; Gene replacement therapy; Targeted expression

Indexed keywords

GENE THERAPY AGENT; GREEN FLUORESCENT PROTEIN; INTERPHOTORECEPTOR RETINOID BINDING PROTEIN CHIMERIC TRANSDUCIN ALPHA SUBUNIT PROMOTER; MOLECULAR THERAPY AGENT; PARVOVIRUS VECTOR; RETINA S ANTIGEN; SYNTHETIC TRANSDUCIN ALPHA SUBUNIT PROMOTER; UNCLASSIFIED DRUG; EYE PROTEIN; HYBRID PROTEIN; INTERPHOTORECEPTOR RETINOID BINDING PROTEIN; INTERSTITIAL RETINOL-BINDING PROTEIN; RETINOL BINDING PROTEIN; TRANSDUCIN;

ANIMAL CELL; ANIMAL EXPERIMENT; ANIMAL TISSUE; ARTICLE; COLOR BLINDNESS; CONTROLLED STUDY; DRUG SELECTIVITY; DRUG SPECIFICITY; ENHANCER REGION; GENE SEQUENCE; GENE TARGETING; GENE THERAPY; GENETIC CONSERVATION; HISTOPATHOLOGY; IMMUNOHISTOCHEMISTRY; NONHUMAN; OUTCOME ASSESSMENT; PIGMENT EPITHELIUM; PRIORITY JOURNAL; PROMOTER REGION; PROTEIN EXPRESSION; RETINA CONE; RETINA DEGENERATION; SEQUENCE ALIGNMENT; TRANSCRIPTION INITIATION SITE; VALIDATION PROCESS; ADENO ASSOCIATED VIRUS; ANIMAL; COLOR VISION DEFECT; DOG; GENE EXPRESSION REGULATION; GENETICS; HUMAN; METHODOLOGY; MOUSE; PATHOLOGY; PHYSIOLOGY; RAT;

ADENO-ASSOCIATED VIRUS; ANIMALIA; MIRIDAE; MURINAE;

ANIMALS; COLOR VISION DEFECTS; DEPENDOVIRUS; DOGS; EYE PROTEINS; GENE EXPRESSION REGULATION; GENETIC THERAPY; HUMANS; MICE; PROMOTER REGIONS, GENETIC; RATS; RECOMBINANT FUSION PROTEINS; RETINAL CONE PHOTORECEPTOR CELLS; RETINOL-BINDING PROTEINS; TRANSDUCIN;

EID: 84904808981     PISSN: 00652598     EISSN: 22148019     Source Type: Book Series    
DOI: 10.1007/978-1-4614-3209-8_87     Document Type: Article

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