Integration-specific in vitro evaluation of lentivirally transduced rhesus CD34+ cells correlates with in vivo vector copy number

Molecular Therapy Nucleic Acids

Volumn 2, Issue SEP, 2013, Pages e122-

  Uchida, Naoya ^a   Evans, Molly E ^a   Hsieh, Matthew M ^a   Bonifacino, Aylin C ^a   Krouse, Allen E ^a   Metzger, Mark E ^a   Sellers, Stephanie E ^a   Dunbar, Cynthia E ^a   Donahue, Robert E ^a   Tisdale, John F ^a  

^a NATIONAL HEART LUNG AND BLOOD INSTITUTE   (United States)

Author keywords

Hematopoietic stem cell transplantation; Large animal model; Lentiviral vector

Indexed keywords

GREEN FLUORESCENT PROTEIN; LENTIVIRUS VECTOR; YELLOW FLUORESCENT PROTEIN;

ANIMAL CELL; ANIMAL EXPERIMENT; ANIMAL MODEL; ARTICLE; CD34 SELECTION; CD34+ CELL; CONTROLLED STUDY; GENE DOSAGE; GENE EXPRESSION; GENE THERAPY; GENETIC TRANSDUCTION; GRANULOCYTE; HEMATOPOIETIC STEM CELL; HEMATOPOIETIC STEM CELL TRANSPLANTATION; IN VITRO STUDY; IN VIVO STUDY; LONG TERMINAL REPEAT; LYMPHOCYTE; NONHUMAN; PLASMID; PRIORITY JOURNAL; PROVIRUS; REAL TIME POLYMERASE CHAIN REACTION; RHESUS MONKEY; TRANSGENE;

EID: 84903843476     PISSN: None     EISSN: 21622531     Source Type: Journal    
DOI: 10.1038/mtna.2013.49     Document Type: Article

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