Targeted gene therapy and cell reprogramming in Fanconi anemia

EMBO Molecular Medicine

Volumn 6, Issue 6, 2014, Pages 835-848

  Rio, Paula ^a,b   Baños, Rocio ^a,b   Lombardo, Angelo ^c   Quintana Bustamante, Oscar ^a,b   Alvarez, Lara ^a,b   Garate, Zita ^a,b   Genovese, Pietro ^c   Almarza, Elena ^a,b   Valeri, Antonio ^a,b   Díez, Begoña ^a,b   Navarro, Susana ^a,b   Torres, Yaima ^d   Trujillo, Juan P ^b,e   Murillas, Rodolfo ^a   Segovia, Jose C ^a,b   Samper, Enrique ^d   Surralles, Jordi ^e   Gregory, Philip D ^f   Holmes, Michael C ^f   Naldini, Luigi ^c,g   Bueren, Juan A ^a,b   more..

^a CIEMAT   (Spain)

^b UAM)   (Spain)

^c SAN RAFFAELE SCIENTIFIC INSTITUTE   (Italy)

^d NIMGenetics   (Spain)

^e UNIVERSITAT AUTÒNOMA DE BARCELONA   (Spain)

^f SANGAMO BIOSCIENCES INC   (United States)

^g VITA SALUTE SAN RAFFAELE UNIVERSITY   (Italy)

Author keywords

Cell reprogramming; Fanconi anemia; Gene targeting; IPSCs; Zinc finger nucleases

Indexed keywords

GENOMIC DNA; INTEGRASE; LENTIVIRUS VECTOR; ZINC FINGER NUCLEASE; FANCONI ANEMIA GROUP A PROTEIN;

ARTICLE; CELL LINEAGE; CHROMOSOMAL INSTABILITY; CHROMOSOME 5; CHROMOSOME ABERRATION; CONTROLLED STUDY; DNA CROSS LINKING; DNA DAMAGE; FANCONI ANEMIA; FIBROBLAST; FLOW CYTOMETRY; GENE LOCUS; GENE TARGETING; GENETIC STABILITY; HEMATOPOIETIC CELL; HEMATOPOIETIC STEM CELL; HUMAN; HUMAN CELL; HUMAN TISSUE; IMMUNOFLUORESCENCE; IMMUNOHISTOCHEMISTRY; MOLECULARLY TARGETED THERAPY; MOUSE; NONHUMAN; NONVIRAL GENE THERAPY; NUCLEAR REPROGRAMMING; PLURIPOTENT STEM CELL; PRIORITY JOURNAL; SOUTHERN BLOTTING; VIRAL GENE DELIVERY SYSTEM; WESTERN BLOTTING; CELL CULTURE; CYTOLOGY; GENE THERAPY; GENETICS; HEMATOPOIESIS; METABOLISM; PROCEDURES;

CELLS, CULTURED; CELLULAR REPROGRAMMING; FANCONI ANEMIA; FANCONI ANEMIA COMPLEMENTATION GROUP A PROTEIN; FIBROBLASTS; GENE TARGETING; GENETIC THERAPY; HEMATOPOIESIS; HUMANS; INDUCED PLURIPOTENT STEM CELLS;

EID: 84901791385     PISSN: 17574676     EISSN: 17574684     Source Type: Journal    
DOI: 10.15252/emmm.201303374     Document Type: Article

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