Genetic correction of HAX1 in induced pluripotent stem cells from a patient with severe congenital neutropenia improves defective granulopoiesis

Haematologica

Volumn 99, Issue 1, 2014, Pages 19-27

  Morishima, Tatsuya ^a   Watanabe, Ken ichiro ^a   Niwa, Akira ^b   Hirai, Hideyo ^c   Saida, Satoshi ^a   Tanaka, Takayuki ^b   Kato, Itaru ^a   Umeda, Katsutsugu ^a   Hiramatsu, Hidefumi ^a   Saito, Megumu K ^b   Matsubara, Kousaku ^d   Adachi, Souichi ^a   Kobayashi, Masao ^e   Nakahata, Tatsutoshi ^b   Heike, Toshio ^a  

^a KYOTO UNIVERSITY   (Japan)

^b KYOTO UNIVERSITY   (Japan)

^c KYOTO UNIVERSITY HOSPITAL   (Japan)

^d NISHI KOBE MEDICAL CENTER   (Japan)

^e HIROSHIMA UNIVERSITY   (Japan)

Author keywords

[No Author keywords available]

Indexed keywords

ADAPTOR PROTEINS, SIGNAL TRANSDUCING; APOPTOSIS; CELL CULTURE TECHNIQUES; CELL DIFFERENTIATION; CELL LINE; CHILD; GENE ORDER; GENETIC VECTORS; GRANULOCYTES; HUMANS; IMMUNOHISTOCHEMISTRY; INDUCED PLURIPOTENT STEM CELLS; LENTIVIRUS; MALE; MEMBRANE POTENTIAL, MITOCHONDRIAL; MYELOPOIESIS; NEUTROPENIA; NEUTROPHILS; TRANSDUCTION, GENETIC;

EID: 84892579544     PISSN: 03906078     EISSN: 15928721     Source Type: Journal    
DOI: 10.3324/haematol.2013.083873     Document Type: Article

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