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Volumn 9, Issue 10, 2013, Pages 991-999

Advances in hematopoietic stem cell transplantation for primary immunodeficiency

Author keywords

extracorporeal photopheresis; graft versus host disease; mesenchymal stromal cells; newborn screening for severe combined immunodeficiency; primary immunodeficiency; reduced intensity conditioning; severe combined immunodeficiency; targeted busulfan; treosulfan

Indexed keywords

BUSULFAN; TREOSULFAN;

EID: 84886904259     PISSN: 1744666X     EISSN: 17448409     Source Type: Journal    
DOI: 10.1586/1744666X.2013.836061     Document Type: Review
Times cited : (21)

References (59)
  • 1
    • 0014433553 scopus 로고
    • Immunological reconstitution of sex-linked lymphopenic immunological deficiency
    • Gatti RA, Meuwissen HJ, Allen HD, Hong R, Good RA. Immunological reconstitution of sex-linked lymphopenic immunological deficiency. Lancet 2(7583), 1366-1369 (1968).
    • (1968) Lancet , vol.2 , Issue.7583 , pp. 1366-1369
    • Gatti, R.A.1    Meuwissen, H.J.2    Allen, H.D.3    Hong, R.4    Good, R.A.5
  • 2
    • 0014433499 scopus 로고
    • Bone-marrow transplantation in a patient with the Wiskott-Aldrich syndrome
    • Bach FH, Albertini RJ, Joo P, Anderson JL, Bortin MM. Bone-marrow transplantation in a patient with the Wiskott-Aldrich syndrome. Lancet 2(7583), 1364-1366 (1968).
    • (1968) Lancet , vol.2 , Issue.7583 , pp. 1364-1366
    • Bach, F.H.1    Albertini, R.J.2    Joo, P.3    Anderson, J.L.4    Bortin, M.M.5
  • 3
    • 77956395504 scopus 로고    scopus 로고
    • Transplantation of hematopoietic stem cells and long-term survival for primary immunodeficiencies in Europe: Entering a new century, do we do better?
    • Gennery AR, Slatter MA, Grandin L et al. Transplantation of hematopoietic stem cells and long-term survival for primary immunodeficiencies in Europe: entering a new century, do we do better? J. Allergy Clin. Immunol. 126, 602-610.e1-e11 (2010).
    • (2010) J. Allergy Clin. Immunol. , vol.126
    • Gennery, A.R.1    Slatter, M.A.2    Grandin, L.3
  • 4
    • 11244284216 scopus 로고    scopus 로고
    • Improved survival after unrelated bone marrow transplantation in children with primary immunodeficiency using a reduced-intensity conditioning regimen
    • Rao K, Amrolia PJ, Jones A et al. Improved survival after unrelated bone marrow transplantation in children with primary immunodeficiency using a reduced-intensity conditioning regimen. Blood 105, 979-985 (2005).
    • (2005) Blood , vol.105 , pp. 979-985
    • Rao, K.1    Amrolia, P.J.2    Jones, A.3
  • 6
    • 34648844153 scopus 로고    scopus 로고
    • Intensive postgrafting immune suppression combined with nonmyeloablative conditioning for transplantation of HLA-identical hematopoietic cell grafts: Results of a pilot study for treatment of primary immunodeficiency disorders
    • Burroughs LM, Storb R, Leisenring WM et al. Intensive postgrafting immune suppression combined with nonmyeloablative conditioning for transplantation of HLA-identical hematopoietic cell grafts: results of a pilot study for treatment of primary immunodeficiency disorders. Bone Marrow Transplant. 40, 633-642 (2007).
    • (2007) Bone Marrow Transplant. , vol.40 , pp. 633-642
    • Burroughs, L.M.1    Storb, R.2    Leisenring, W.M.3
  • 7
    • 69949094169 scopus 로고    scopus 로고
    • Haemopoietic stem-cell transplantation with antibody-based minimal-intensity conditioning: A phase 1/2 study
    • Straathof KC, Rao K, Eyrich M et al. Haemopoietic stem-cell transplantation with antibody-based minimal-intensity conditioning: a phase 1/2 study. Lancet 374, 912-920 (2009).
    • (2009) Lancet , vol.374 , pp. 912-920
    • Straathof, K.C.1    Rao, K.2    Eyrich, M.3
  • 8
    • 2442715230 scopus 로고    scopus 로고
    • Thyroid dysfunction after bone marrow transplantation for primary immunodeficiency without the use of total body irradiation in conditioning
    • Slatter MA, Gennery AR, Cheetham TD et al. Thyroid dysfunction after bone marrow transplantation for primary immunodeficiency without the use of total body irradiation in conditioning. Bone Marrow Transplant. 33, 949-953 (2004).
    • (2004) Bone Marrow Transplant. , vol.33 , pp. 949-953
    • Slatter, M.A.1    Gennery, A.R.2    Cheetham, T.D.3
  • 9
    • 80052087580 scopus 로고    scopus 로고
    • Therapeutic drug monitoring is essential for intravenous busulfan therapy in pediatric hematopoietic stem cell recipients
    • Malar R, Sjoö F, Rentsch K, Hassan M, Güngor T. Therapeutic drug monitoring is essential for intravenous busulfan therapy in pediatric hematopoietic stem cell recipients. Pediatr. Transplant. 15, 580-588 (2011).
    • (2011) Pediatr. Transplant. , vol.15 , pp. 580-588
    • Malar, R.1    Sjoö, F.2    Rentsch, K.3    Hassan, M.4    Güngor, T.5
  • 10
    • 84886910979 scopus 로고    scopus 로고
    • Excellent outcome after submyeloablative reduced-toxicity conditioning and hematopoietic stem cell transplantation in high-risk chronic granulomatous disease patients
    • In Press
    • Güngor T, Albert MH, Teira P et al. Excellent outcome after submyeloablative reduced-toxicity conditioning and hematopoietic stem cell transplantation in high-risk chronic granulomatous disease patients. Lancet (2013) (In Press).
    • (2013) Lancet
    • Güngor, T.1    Albert, M.H.2    Teira, P.3
  • 11
    • 0037114622 scopus 로고    scopus 로고
    • Treatment of chronic granulomatous disease with myeloablative conditioning and an unmodified hemopoietic allograft: A survey of the European experience 1985-2000
    • Seger RA, Gungor T, Belohradsky BH et al. Treatment of chronic granulomatous disease with myeloablative conditioning and an unmodified hemopoietic allograft: a survey of the European experience, 1985-2000. Blood 100, 4344-4350 (2002).
    • (2002) Blood , vol.100 , pp. 4344-4350
    • Seger, R.A.1    Gungor, T.2    Belohradsky, B.H.3
  • 12
    • 13944280315 scopus 로고    scopus 로고
    • Dose-escalated treosulphan in combination with cyclophosphamide as a new preparative regimen for allogeneic haematopoietic stem cell transplantation in patients with an increased risk for regimen-related complications
    • Beelen DW, Trenschel R, Casper J et al. Dose-escalated treosulphan in combination with cyclophosphamide as a new preparative regimen for allogeneic haematopoietic stem cell transplantation in patients with an increased risk for regimen-related complications. Bone Marrow Transplant. 35, 233-2341 (2005).
    • (2005) Bone Marrow Transplant. , vol.35 , pp. 233-2341
    • Beelen, D.W.1    Trenschel, R.2    Casper, J.3
  • 13
    • 84865988132 scopus 로고    scopus 로고
    • Allogeneic hematopoietic SCT in patients with AML following treosulfan/fludarabine conditioning
    • Casper J, Holowiecki J, Trenschel R et al. Allogeneic hematopoietic SCT in patients with AML following treosulfan/fludarabine conditioning. Bone Marrow Transplant. 47, 1171-1177 (2012).
    • (2012) Bone Marrow Transplant. , vol.47 , pp. 1171-1177
    • Casper, J.1    Holowiecki, J.2    Trenschel, R.3
  • 14
    • 47249112625 scopus 로고    scopus 로고
    • Treosulfan-containing regimens achieve high rates of engraftment associated with low transplant morbidity and mortality in children with non-malignant disease and significant co-morbidities
    • Greystoke B, Bonanomi S, Carr TF et al. Treosulfan-containing regimens achieve high rates of engraftment associated with low transplant morbidity and mortality in children with non-malignant disease and significant co-morbidities. Br. J. Haematol. 142, 257-262 (2008).
    • (2008) Br. J. Haematol. , vol.142 , pp. 257-262
    • Greystoke, B.1    Bonanomi, S.2    Carr, T.F.3
  • 15
    • 55949130876 scopus 로고    scopus 로고
    • Treosulphan as an alternative to busulphan for myeloablative conditioning in paediatric allogeneic transplantation
    • Cutting R, Mirelman A, Vora A. Treosulphan as an alternative to busulphan for myeloablative conditioning in paediatric allogeneic transplantation. Br. J. Haematol. 143, 748-745 (2008).
    • (2008) Br. J. Haematol. , vol.143 , pp. 748-745
    • Cutting, R.1    Mirelman, A.2    Vora, A.3
  • 16
    • 79956040256 scopus 로고    scopus 로고
    • Treosulfan-based conditioning regimens for hematopoietic stem cell transplantation in children with primary immunodeficiency: United Kingdom experience
    • Slatter M, Rao K, Amrolia P et al. Treosulfan-based conditioning regimens for hematopoietic stem cell transplantation in children with primary immunodeficiency: United Kingdom experience. Blood 117, 4367-4375 (2011).
    • (2011) Blood , vol.117 , pp. 4367-4375
    • Slatter, M.1    Rao, K.2    Amrolia, P.3
  • 17
    • 84856113386 scopus 로고    scopus 로고
    • Treosulfan-based preparative regimens for allo-HSCT in childhood hematological malignancies: A retrospective study on behalf of the EBMT pediatric diseases working party
    • Wachowiak J, Sykora KW, Cornish J et al Treosulfan-based preparative regimens for allo-HSCT in childhood hematological malignancies: a retrospective study on behalf of the EBMT pediatric diseases working party. Bone Marrow Transplant. 46, 1510-1518 (2011).
    • (2011) Bone Marrow Transplant. , vol.46 , pp. 1510-1518
    • Wachowiak, J.1    Sykora, K.W.2    Cornish, J.3
  • 18
    • 84876406371 scopus 로고    scopus 로고
    • Long-term follow-up of children conditioned with Treosulfan: German and Austrian experience
    • Beier R, Schulz A, Honig M et al Long-term follow-up of children conditioned with Treosulfan: German and Austrian experience. Bone Marrow Transplant. 48, 491-501 (2013).
    • (2013) Bone Marrow Transplant. , vol.48 , pp. 491-501
    • Beier, R.1    Schulz, A.2    Honig, M.3
  • 19
    • 84864075455 scopus 로고    scopus 로고
    • Allogeneic hematopoietic stem cell transplantation in thalassemia major: Results of a reduced-toxicity conditioning regimen based on the use of treosulfan
    • Bernardo ME, Piras E, Vacca A et al. Allogeneic hematopoietic stem cell transplantation in thalassemia major: results of a reduced-toxicity conditioning regimen based on the use of treosulfan. Blood 120, 473-476 (2012).
    • (2012) Blood , vol.120 , pp. 473-476
    • Bernardo, M.E.1    Piras, E.2    Vacca, A.3
  • 20
    • 10744221943 scopus 로고    scopus 로고
    • Defibrotide in the treatment of children with veno-occlusive disease (VOD): A retrospective multicentre study demonstrates therapeutic efficacy upon early intervention
    • Corbacioglu S, Greil J, Peters C et al Defibrotide in the treatment of children with veno-occlusive disease (VOD): a retrospective multicentre study demonstrates therapeutic efficacy upon early intervention. Bone Marrow Transplant. 33, 189-195 (2004).
    • (2004) Bone Marrow Transplant. , vol.33 , pp. 189-195
    • Corbacioglu, S.1    Greil, J.2    Peters, C.3
  • 21
    • 84859432625 scopus 로고    scopus 로고
    • Defibrotide for prophylaxis of hepatic veno-occlusive disease in paediatric haemopoietic stem-cell transplantation: An open-label, phase 3, randomised controlled trial
    • Corbacioglu S, Cesaro S, Faraci M et al Defibrotide for prophylaxis of hepatic veno-occlusive disease in paediatric haemopoietic stem-cell transplantation: an open-label, phase 3, randomised controlled trial. Lancet 379, 1301-1309 (2012).
    • (2012) Lancet , vol.379 , pp. 1301-1309
    • Corbacioglu, S.1    Cesaro, S.2    Faraci, M.3
  • 22
    • 84876417064 scopus 로고    scopus 로고
    • Haploidentical related-donor hematopoietic cell transplantation in children using megadoses of CliniMACs-selected CD34(+) cells and a fixed CD3(+) dose
    • Dvorak CC, Gilman AL, Horn B et al Haploidentical related-donor hematopoietic cell transplantation in children using megadoses of CliniMACs-selected CD34(+) cells and a fixed CD3(+) dose. Bone Marrow Transplant. 48, 508-513 (2013).
    • (2013) Bone Marrow Transplant. , vol.48 , pp. 508-513
    • Dvorak, C.C.1    Gilman, A.L.2    Horn, B.3
  • 23
    • 39149139612 scopus 로고    scopus 로고
    • Long-term immune reconstitution after anti-CD52-treated or anti-CD34-treated hematopoietic stem cell transplantation for severe T-lymphocyte immunodeficiency
    • Slatter MA, Brigham K, Dickinson AM et al. Long-term immune reconstitution after anti-CD52-treated or anti-CD34-treated hematopoietic stem cell transplantation for severe T-lymphocyte immunodeficiency. J. Allergy Clin. Immunol. 121, 361-367 (2008).
    • (2008) J. Allergy Clin. Immunol. , vol.121 , pp. 361-367
    • Slatter, M.A.1    Brigham, K.2    Dickinson, A.M.3
  • 24
    • 0035144015 scopus 로고    scopus 로고
    • Mesenchymal stem cells are capable of homing to the bone marrow of non-human primates following systemic infusion
    • Devine SM, Bartholomew AM, Mahmud N et al. Mesenchymal stem cells are capable of homing to the bone marrow of non-human primates following systemic infusion. Exp. Hematol. 29, 244-55 (2001).
    • (2001) Exp. Hematol. , vol.29 , pp. 244-255
    • Devine, S.M.1    Bartholomew, A.M.2    Mahmud, N.3
  • 25
    • 84878553354 scopus 로고    scopus 로고
    • Haploidentical hematopoietic stem cell transplantation can lead to viral clearance in severe combined immunodeficiency
    • Slatter M, Nademi Z, Patel S et al. Haploidentical hematopoietic stem cell transplantation can lead to viral clearance in severe combined immunodeficiency. J. Allergy Clin. Immunol. 131, 1705-1708.e1 (2013).
    • (2013) J. Allergy Clin. Immunol. , vol.131
    • Slatter, M.1    Nademi, Z.2    Patel, S.3
  • 26
    • 84865365080 scopus 로고    scopus 로고
    • Immune reconstitution and strategies for rebuilding the immune system after haploidentical stem cell transplantation
    • Oevermann L, Lang P, Feuchtinger T et al. Immune reconstitution and strategies for rebuilding the immune system after haploidentical stem cell transplantation. Ann. NY Acad. Sci. 1266, 161-170 (2012).
    • (2012) Ann. NY Acad. Sci. , vol.1266 , pp. 161-170
    • Oevermann, L.1    Lang, P.2    Feuchtinger, T.3
  • 27
    • 84858077731 scopus 로고    scopus 로고
    • IgG antibodies to ATG early after pediatric hematopoietic SCT increase the risk of acute GVHD
    • Jol-van der Zijde CM, Bredius RG, Jansen-Hoogendijk AM et al. IgG antibodies to ATG early after pediatric hematopoietic SCT increase the risk of acute GVHD. Bone Marrow Transplant. 47, 360-368 (2012).
    • (2012) Bone Marrow Transplant. , vol.47 , pp. 360-368
    • Jol-Van Der Zijde, C.M.1    Bredius, R.G.2    Jansen-Hoogendijk, A.M.3
  • 28
    • 84857030533 scopus 로고    scopus 로고
    • Omission of in vivo T-cell depletion promotes rapid expansion of naive CD4+ cord blood lymphocytes and restores adaptive immunity within 2 months after unrelated cord blood transplant
    • Chiesa R, Gilmour K, Qasim W et al. Omission of in vivo T-cell depletion promotes rapid expansion of naive CD4+ cord blood lymphocytes and restores adaptive immunity within 2 months after unrelated cord blood transplant. Br. J. Haematol. 156, 656-666 (2012).
    • (2012) Br. J. Haematol. , vol.156 , pp. 656-666
    • Chiesa, R.1    Gilmour, K.2    Qasim, W.3
  • 29
    • 31144431851 scopus 로고    scopus 로고
    • Effect of IL-18 and sIL2R on aGVHD occurrence after hematopoietic stem cell transplantation in some Iranian patients
    • Shaiegan M, Iravani M, Babaee G, Ghavamzadeh A. Effect of IL-18 and sIL2R on aGVHD occurrence after hematopoietic stem cell transplantation in some Iranian patients. Transpl. Immunol. 15, 223-227 (2006).
    • (2006) Transpl. Immunol. , vol.15 , pp. 223-227
    • Shaiegan, M.1    Iravani, M.2    Babaee, G.3    Ghavamzadeh, A.4
  • 30
    • 51649121552 scopus 로고    scopus 로고
    • Change in plasma tumor necrosis factor receptor 1 levels in the first week after myeloablative allogeneic transplantation correlates with severity and incidence of GVHD and survival
    • Choi SW, Kitko CL, Braun T et al. Change in plasma tumor necrosis factor receptor 1 levels in the first week after myeloablative allogeneic transplantation correlates with severity and incidence of GVHD and survival. Blood 112, 1539-1542 (2008).
    • (2008) Blood , vol.112 , pp. 1539-1542
    • Choi, S.W.1    Kitko, C.L.2    Braun, T.3
  • 31
    • 79953699970 scopus 로고    scopus 로고
    • Biomarkers of immune activation to screen for severe, acute GVHD
    • August KJ, Chiang KY, Bostick RM et al Biomarkers of immune activation to screen for severe, acute GVHD. Bone Marrow Transplant. 46, 601-604 (2011).
    • (2011) Bone Marrow Transplant. , vol.46 , pp. 601-604
    • August, K.J.1    Chiang, K.Y.2    Bostick, R.M.3
  • 32
    • 0038378818 scopus 로고    scopus 로고
    • Proinflammatory cytokines and their role in the development of major transplant-related complications in the early phase after allogeneic bone marrow transplantation
    • Schots R, Kaufman L, Van Riet I et al. Proinflammatory cytokines and their role in the development of major transplant-related complications in the early phase after allogeneic bone marrow transplantation. Leukemia 17, 1150-1156 (2003).
    • (2003) Leukemia , vol.17 , pp. 1150-1156
    • Schots, R.1    Kaufman, L.2    Van Riet, I.3
  • 33
    • 77952962428 scopus 로고    scopus 로고
    • Elafin is a biomarker of graft-versus-host disease of the skin
    • Paczesny S, Braun TM, Levine JE et al. Elafin is a biomarker of graft-versus-host disease of the skin. Sci. Transl. Med. 2, 13ra2 (2010).
    • (2010) Sci. Transl. Med. , vol.2
    • Paczesny, S.1    Braun, T.M.2    Levine, J.E.3
  • 34
    • 84055177580 scopus 로고    scopus 로고
    • Regenerating islet-derived 3-alpha is a biomarker of gastrointestinal graft-versus-host disease
    • Ferrara JL, Harris AC, Greenson JK et al. Regenerating islet-derived 3-alpha is a biomarker of gastrointestinal graft-versus-host disease. Blood 118, 6702-6708 (2011).
    • (2011) Blood , vol.118 , pp. 6702-6708
    • Ferrara, J.L.1    Harris, A.C.2    Greenson, J.K.3
  • 35
    • 84863371821 scopus 로고    scopus 로고
    • Plasma biomarkers of lower gastrointestinal and liver acute GVHD
    • Harris AC, Ferrara JL, Braun TM et al. Plasma biomarkers of lower gastrointestinal and liver acute GVHD. Blood 119, 2960-2963 (2012).
    • (2012) Blood , vol.119 , pp. 2960-2963
    • Harris, A.C.1    Ferrara, J.L.2    Braun, T.M.3
  • 36
    • 84886857809 scopus 로고    scopus 로고
    • Low Paneth cell numbers at onset of gastrointestinal GVHD identify patients at high risk for non-relapse mortality
    • Epub ahead of print
    • Levine JE, Huber E, Hammer ST et al. Low Paneth cell numbers at onset of gastrointestinal GVHD identify patients at high risk for non-relapse mortality. Blood (2013) (Epub ahead of print).
    • (2013) Blood
    • Levine, J.E.1    Huber, E.2    Hammer, S.T.3
  • 37
    • 84860345135 scopus 로고    scopus 로고
    • Acute graft-versus-host disease biomarkers measured during therapy can predict treatment outcomes: A Blood and Marrow Transplant Clinical Trials Network study
    • Levine JE, Logan BR, Wu J et al. Acute graft-versus-host disease biomarkers measured during therapy can predict treatment outcomes: a Blood and Marrow Transplant Clinical Trials Network study. Blood 119, 3854-3860 (2012).
    • (2012) Blood , vol.119 , pp. 3854-3860
    • Levine, J.E.1    Logan, B.R.2    Wu, J.3
  • 38
    • 2342482526 scopus 로고    scopus 로고
    • Treatment of severe acute graft-versus-host disease with third party haploidentical mesenchymal stem cells
    • Le Blanc K, Rasmusson I, Sundberg B et al Treatment of severe acute graft-versus-host disease with third party haploidentical mesenchymal stem cells. Lancet 363, 1439-1441 (2004).
    • (2004) Lancet , vol.363 , pp. 1439-1441
    • Le Blanc, K.1    Rasmusson, I.2    Sundberg, B.3
  • 39
    • 33744913533 scopus 로고    scopus 로고
    • Mesenchymal stem cells for treatment of therapy-resistant graft-versus-host disease
    • Ringden O, Uzunel M, Rasmusson I et al. Mesenchymal stem cells for treatment of therapy-resistant graft-versus-host disease. Transplantation 81, 1390-1397 (2006).
    • (2006) Transplantation , vol.81 , pp. 1390-1397
    • Ringden, O.1    Uzunel, M.2    Rasmusson, I.3
  • 40
    • 43049103438 scopus 로고    scopus 로고
    • Mesenchymal stem cells for treatment of steroid-resistant, severe, acute graft-versus-host disease: A Phase II study
    • Le Blanc K, Frassoni F, Ball L et al. Mesenchymal stem cells for treatment of steroid-resistant, severe, acute graft-versus-host disease: a Phase II study. Lancet 371, 1579-1586 (2008).
    • (2008) Lancet , vol.371 , pp. 1579-1586
    • Le Blanc, K.1    Frassoni, F.2    Ball, L.3
  • 41
    • 78650208987 scopus 로고    scopus 로고
    • Mesenchymal stem cell as salvage treatment for refractory chronic GVHD
    • Weng JY, Du X, Geng SX et al. Mesenchymal stem cell as salvage treatment for refractory chronic GVHD. Bone Marrow Transplant. 45, 1732-1740 (2010).
    • (2010) Bone Marrow Transplant. , vol.45 , pp. 1732-1740
    • Weng, J.Y.1    Du, X.2    Geng, S.X.3
  • 42
    • 77955509074 scopus 로고    scopus 로고
    • Platelet-lysate-expanded mesenchymal stromal cells as a salvage therapy for severe resistant graft-versus-host disease in a pediatric population
    • Lucchini G, Introna M, Dander E et al. Platelet-lysate-expanded mesenchymal stromal cells as a salvage therapy for severe resistant graft-versus-host disease in a pediatric population. Biol. Blood Marrow Transplant. 16, 1293-1301 (2010).
    • (2010) Biol. Blood Marrow Transplant. , vol.16 , pp. 1293-1301
    • Lucchini, G.1    Introna, M.2    Dander, E.3
  • 43
    • 77952584405 scopus 로고    scopus 로고
    • Co transplantation of mesenchymal stem cells might prevent death from graft-versus-host disease (GVHD) with-out abrogating graft-versus-tumor effects after HLA-mismatched allogeneic transplantation following nonmyeloablative conditioning
    • Baron F, Lechanteur C, Willems E et al. Co transplantation of mesenchymal stem cells might prevent death from graft-versus-host disease (GVHD) with-out abrogating graft-versus-tumor effects after HLA-mismatched allogeneic transplantation following nonmyeloablative conditioning. Biol. Blood Marrow Transplant. 16, 838-847 (2010).
    • (2010) Biol. Blood Marrow Transplant. , vol.16 , pp. 838-847
    • Baron, F.1    Lechanteur, C.2    Willems, E.3
  • 44
    • 79952624644 scopus 로고    scopus 로고
    • Efficacy and safety of ex vivo cultured adult human mesenchymal stem cells (prochymal) in pediatric patients with severe refractory acute graft-versus-host disease in a compassionate use study
    • Prasad VK, Lucas KG, Kleiner GI et al. (2011) Efficacy and safety of ex vivo cultured adult human mesenchymal stem cells (prochymal) in pediatric patients with severe refractory acute graft-versus-host disease in a compassionate use study. Biol Blood Marrow Transplant. 17, 534-541 (2011).
    • (2011) Biol Blood Marrow Transplant , vol.17 , pp. 534-541
    • Prasad, V.K.1    Lucas, K.G.2    Kleiner, G.I.3
  • 45
    • 0242559948 scopus 로고    scopus 로고
    • Photopheresis in paediatric patients with drug-resistant chronic graft-versus-host disease
    • Dall'Amico R, Rossetti F, Zulian F et al. Photopheresis in paediatric patients with drug-resistant chronic graft-versus-host disease. Br. J. Haematol. 97, 848-854 (1997).
    • (1997) Br. J. Haematol. , vol.97 , pp. 848-854
    • Dall'Amico, R.1    Rossetti, F.2    Zulian, F.3
  • 46
    • 0032212219 scopus 로고    scopus 로고
    • Successful use of extracorporeal photochemotherapy in the treatment of severe acute and chronic graft-versus-host disease
    • Greinix HT, Volc-Platzer B, Rabitsch W et al. Successful use of extracorporeal photochemotherapy in the treatment of severe acute and chronic graft-versus-host disease. Blood 92, 3098-3104 (1998).
    • (1998) Blood , vol.92 , pp. 3098-3104
    • Greinix, H.T.1    Volc-Platzer, B.2    Rabitsch, W.3
  • 47
    • 84881590532 scopus 로고    scopus 로고
    • Extracorporeal photopheresis: A useful therapy for patients with steroids refractory acute graft versus host disease but not for the prevention of the chronic form
    • doi: 10.1111/bjd.12332, Epub ahead of print
    • Rubegni P, Feci L, Poggiali S et al. Extracorporeal photopheresis: a useful therapy for patients with steroids refractory acute graft versus host disease but not for the prevention of the chronic form. Br. J. Dermatol. doi: 10.1111/bjd.12332 (2013) (Epub ahead of print).
    • (2013) Br. J. Dermatol
    • Rubegni, P.1    Feci, L.2    Poggiali, S.3
  • 48
    • 84855729962 scopus 로고    scopus 로고
    • Outcome of children requiring intensive care following haematopoietic SCT for primary immunodeficiency and other non-malignant disorders
    • Cole TS, Johnstone IC, Pearce MS et al. Outcome of children requiring intensive care following haematopoietic SCT for primary immunodeficiency and other non-malignant disorders. Bone Marrow Transplant. 47, 40-45 (2012).
    • (2012) Bone Marrow Transplant. , vol.47 , pp. 40-45
    • Cole, T.S.1    Johnstone, I.C.2    Pearce, M.S.3
  • 49
    • 79953082197 scopus 로고    scopus 로고
    • Neonatal diagnosis of severe combined immunodeficiency leads to significantly improved survival outcome: The case for newborn screening
    • Brown L, Xu-Bayford J, Allwood Z et al. Neonatal diagnosis of severe combined immunodeficiency leads to significantly improved survival outcome: the case for newborn screening. Blood 117, 3243-3246 (2011).
    • (2011) Blood , vol.117 , pp. 3243-3246
    • Brown, L.1    Xu-Bayford, J.2    Allwood, Z.3
  • 50
    • 84857757608 scopus 로고    scopus 로고
    • The long quest for neonatal screening for severe combined immunodeficiency
    • Buckley RH. The long quest for neonatal screening for severe combined immunodeficiency. J. Allergy Clin. Immunol. 129, 597-604 (2012).
    • (2012) J. Allergy Clin. Immunol. , vol.129 , pp. 597-604
    • Buckley, R.H.1
  • 51
    • 84882791221 scopus 로고    scopus 로고
    • Newborn screening for severe combined immunodeficiency and T-cell lymphopenia in California: Results of the first 2 years
    • Kwan A, Church JA, Cowan MJ et al. Newborn screening for severe combined immunodeficiency and T-cell lymphopenia in California: Results of the first 2 years. J. Allergy Clin. Immunol. 132, 140-150.e7 (2013).
    • (2013) J. Allergy Clin. Immunol. , vol.132
    • Kwan, A.1    Church, J.A.2    Cowan, M.J.3
  • 52
    • 84878616948 scopus 로고    scopus 로고
    • Tandem mass spectrometry, but not T-cell receptor excision circle analysis, identifies newborns with late-onset adenosine deaminase deficiency
    • la Marca G, Canessa C, Giocaliere E et al. Tandem mass spectrometry, but not T-cell receptor excision circle analysis, identifies newborns with late-onset adenosine deaminase deficiency. J. Allergy Clin. Immunol. 131, 1604-1610 (2013).
    • (2013) J. Allergy Clin. Immunol. , vol.131 , pp. 1604-1610
    • La Marca, G.1    Canessa, C.2    Giocaliere, E.3
  • 53
    • 0035089907 scopus 로고    scopus 로고
    • Diagnosis of severe combined immunodeficiency
    • Gennery AR, Cant AJ. Diagnosis of severe combined immunodeficiency. J. Clin. Pathol. 54, 191-195 (2001).
    • (2001) J. Clin. Pathol. , vol.54 , pp. 191-195
    • Gennery, A.R.1    Cant, A.J.2
  • 54
    • 84876932180 scopus 로고    scopus 로고
    • Unresolved issues in hematopoietic stem cell transplantation for severe combined immunodeficiency: Need for safer conditioning and reduced late effects
    • Horn B, Cowan MJ. Unresolved issues in hematopoietic stem cell transplantation for severe combined immunodeficiency: need for safer conditioning and reduced late effects. J. Allergy Clin. Immunol. 131, 1306-1311 (2013).
    • (2013) J. Allergy Clin. Immunol. , vol.131 , pp. 1306-1311
    • Horn, B.1    Cowan, M.J.2
  • 55
    • 36448992228 scopus 로고    scopus 로고
    • Efficient transplantation via antibody-based clearance of hematopoietic stem cell niches
    • Czechowicz A, Kraft D, Weissman IL, Bhattacharya D. Efficient transplantation via antibody-based clearance of hematopoietic stem cell niches. Science 318, 1296-1299 (2007).
    • (2007) Science , vol.318 , pp. 1296-1299
    • Czechowicz, A.1    Kraft, D.2    Weissman, I.L.3    Bhattacharya, D.4
  • 56
    • 84875699025 scopus 로고    scopus 로고
    • B-cell reconstitution for SCID: Should a conditioning regimen be used in SCID treatment?
    • Haddad E, Leroy S, Buckley RH. B-cell reconstitution for SCID: should a conditioning regimen be used in SCID treatment? J. Allergy Clin. Immunol. 131, 994-1000 (2013).
    • (2013) J. Allergy Clin. Immunol. , vol.131 , pp. 994-1000
    • Haddad, E.1    Leroy, S.2    Buckley, R.H.3
  • 57
    • 84887501471 scopus 로고    scopus 로고
    • Safety and clinical efficacy of rapidly-generated trivirus-directed T cells as treatment for Adenovirus, EBV and CMV infections after allogeneic hematopoietic stem cell transplant
    • Epub ahead of print
    • Gerdemann U, Katari UL, Papadopoulou A et al. Safety and clinical efficacy of rapidly-generated trivirus-directed T cells as treatment for Adenovirus, EBV and CMV infections after allogeneic hematopoietic stem cell transplant. Mol. Ther. (2013) (Epub ahead of print).
    • (2013) Mol. Ther.
    • Gerdemann, U.1    Katari, U.L.2    Papadopoulou, A.3
  • 58
    • 78549241330 scopus 로고    scopus 로고
    • Adoptive transfer of pp65-specific T cells for the treatment of chemorefractory cytomegalovirus disease or reactivation after haploidentical and matched unrelated stem cell transplantation
    • Feuchtinger T, Opherk K, Bethge WA et al. Adoptive transfer of pp65-specific T cells for the treatment of chemorefractory cytomegalovirus disease or reactivation after haploidentical and matched unrelated stem cell transplantation. Blood 116, 4360-4367 (2010).
    • (2010) Blood , vol.116 , pp. 4360-4367
    • Feuchtinger, T.1    Opherk, K.2    Bethge, W.A.3
  • 59
    • 84876451718 scopus 로고    scopus 로고
    • Health related quality of life and emotional health in children with chronic granulomatous disease: A comparison of those managed conservatively with those that have undergone haematopoietic stem cell transplant
    • Cole T, McKendrick F, Titman P et al. Health related quality of life and emotional health in children with chronic granulomatous disease: a comparison of those managed conservatively with those that have undergone haematopoietic stem cell transplant. J. Clin. Immunol. 33, 8-13 (2013).
    • (2013) J. Clin. Immunol. , vol.33 , pp. 8-13
    • Cole, T.1    McKendrick, F.2    Titman, P.3


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