Specific elimination of mutant mitochondrial genomes in patient-derived cells by mitoTALENs

Nature Medicine

Volumn 19, Issue 9, 2013, Pages 1111-1113

  Bacman, Sandra R ^a   Williams, Siôn L ^a   Pinto, Milena ^a   Peralta, Susana ^a   Moraes, Carlos T ^a  

^a UNIVERSITY OF MIAMI MILLER SCHOOL OF MEDICINE   (United States)

Author keywords

[No Author keywords available]

Indexed keywords

MITOCHONDRIAL DNA;

ARTICLE; DELETION MUTANT; DISORDERS OF MITOCHONDRIAL FUNCTIONS; DYSTONIA; GENE EXPRESSION; HAPLOTYPE; HETEROPLASMY; HUMAN; IN VIVO STUDY; MITOCHONDRIAL DNA DEPLETION; MITOCHONDRIAL GENOME; MUTATION; NONHUMAN; OPTIC NERVE DISEASE; OSTEOSARCOMA; OSTEOSARCOMA CELL; POINT MUTATION; PRIORITY JOURNAL;

AMINO ACID SEQUENCE; CELL LINE, TUMOR; DEOXYRIBONUCLEASES, TYPE II SITE-SPECIFIC; DNA, MITOCHONDRIAL; GENOME, MITOCHONDRIAL; HUMANS; MITOCHONDRIA; MITOCHONDRIAL DISEASES; MOLECULAR SEQUENCE DATA; MUTATION; OSTEOSARCOMA;

EID: 84883778302     PISSN: 10788956     EISSN: 1546170X     Source Type: Journal    
DOI: 10.1038/nm.3261     Document Type: Article

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