Intracisternal enzyme replacement therapy in lysosomal storage diseases: Dispersal pathways, regional enzyme concentrations and the effect of posttreatment posture

Neuropathology and Applied Neurobiology

Volumn 39, Issue 6, 2013, Pages 681-692

  Jolly, R D ^a   Marshall, N R ^a   Marshall, J ^a   Hartman, A ^a   Hemsley, K M ^b   Winner, L K ^b  

^a MASSEY UNIVERSITY   (New Zealand)

^b WOMEN S AND CHILDREN S HOSPITAL   (Australia)

Author keywords

Cerebellomedullary cistern; Cerebrospinal fluid; Intracisternal enzyme replacement; Lysosomal storage disease; Mucopolysaccharidosis IIIA; Posture

Indexed keywords

CARBON; ENZYME; IOHEXOL; RECOMBINANT HUMAN SULFAMIDASE; UNCLASSIFIED DRUG;

ANIMAL EXPERIMENT; ANIMAL MODEL; ANIMAL TISSUE; ARTICLE; BODY POSTURE; CEREBROSPINAL FLUID FLOW; COMPUTER ASSISTED TOMOGRAPHY; CONTROLLED STUDY; DOG; ENZYME REPLACEMENT; GENE LOCUS; INTRACISTERNAL DRUG ADMINISTRATION; LYSOSOME STORAGE DISEASE; MALE; NONHUMAN; PRIORITY JOURNAL; SUBARACHNOID SPACE;

CEREBELLOMEDULLARY CISTERN; CEREBROSPINAL FLUID; INTRACISTERNAL ENZYME REPLACEMENT; LYSOSOMAL STORAGE DISEASE; MUCOPOLYSACCHARIDOSIS IIIA; POSTURE;

ANIMALS; BRAIN; CARBON; CISTERNA MAGNA; DOGS; ENZYME REPLACEMENT THERAPY; HYDROLASES; LYSOSOMAL STORAGE DISEASES; MALE; POSTURE;

EID: 84883652395     PISSN: 03051846     EISSN: 13652990     Source Type: Journal    
DOI: 10.1111/nan.12010     Document Type: Article

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