SGSH gene transfer in mucopolysaccharidosis type IIIA mice using canine adenovirus vectors

Molecular Genetics and Metabolism

Volumn 100, Issue 2, 2010, Pages 168-175

  Lau, Adeline A ^a,b   Hopwood, John J ^a,b   Kremer, Eric J ^c,d   Hemsley, Kim M ^a,b  

^a Lysosomal Diseases Research Unit   (Australia)

^b UNIVERSITY OF ADELAIDE   (Australia)

^c INSTITUT DE GÉNÉTIQUE MOLÉCULAIRE DE MONTPELLIER   (France)

^d UNIV MONTPELLIER   (France)

Author keywords

Canine adenovirus; Gene therapy; Mucopolysaccharidosis; Sanfilippo syndrome

Indexed keywords

ADENOVIRUS VECTOR; HEPARAN SULFATE; N SULFOGLUCOSAMINE SULFOHYDROLASE; SULFATASE; UNCLASSIFIED DRUG;

ANIMAL EXPERIMENT; ANIMAL MODEL; ANIMAL TISSUE; ARTICLE; CANINE ADENOVIRUS; DOSE RESPONSE; GENE EXPRESSION; LYSOSOME STORAGE DISEASE; MOUSE; MUCOPOLYSACCHARIDOSIS; NERVE DEGENERATION; NEUROPATHOLOGY; NEWBORN; NONHUMAN; PRIORITY JOURNAL; SANFILIPPO SYNDROME TYPE A; THALAMUS;

ADENOVIRUSES, CANINE; ANIMALS; ANIMALS, NEWBORN; ANTIBODIES, VIRAL; ENZYME REPLACEMENT THERAPY; GENE TRANSFER TECHNIQUES; GENETIC VECTORS; HYDROLASES; MICE; MUCOPOLYSACCHARIDOSIS III;

ADENOVIRIDAE; CANINE ADENOVIRUS; CHICKEN ANEMIA VIRUS; MUS;

EID: 77951976097     PISSN: 10967192     EISSN: 10967206     Source Type: Journal    
DOI: 10.1016/j.ymgme.2010.02.006     Document Type: Article

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